Not logged inMolecular features of a Huntington's disease knock-in minipig
Kolesnikova, Anastasiia; Sathasivam, Kirupa; Tusi, Solaleh Khoramian; Landles, Christian; Osborne, Georgina F.; Kovalenko, Marina; Gillis, Tammy; Kamenna, Eva; Sekac, David; Nguyen, Duong The; Valekova, Ivona; Juhas, Stefan; Juhasova, Jana; Levinska, Bozena; Baxa, Monika; Motlik, Jan; Klima, Jiri; Howland, David; Wheeler, Vanessa C.; Bates, Gillian P.; Ellederova, Zdenka
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SaveSubretinal Injection Volume Correlates to Persistent Outer Retinal Thinning in the Pig Eye
Seitz, Immanuel P.; Nyshchuk, Ruslan; Ellederova, Zdenka; Ardan, Taras; Juhasova, Jana; Nemesh, Yaroslav; Juhas, Stefan; Drutovic, Saskia; Susskind, Daniela; Schnichels, Sven; Motlik, Jan; Klymiuk, Nikolai; Wolfrum, Uwe; DeMott, Kathryn Post; Klein, Jennifer J.; Winslow, Ashley; Fischer, M. Dominik
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SaveDelivery of Human iPSC-Derived RPE Cells in Healthy Minipig Retina Results in Interaction Between Photoreceptors and Transplanted Cells
Brymová, AM; Rodriguez-Jimenez, FJ; Konrad, A; Nemesh, Y; Thottappali, MA; Artero-Castro, A; Nyshchuk, R; Kolesnikova, A; Müller, B; Studenovska, H; Juhasova, J; Juhas, S; Valekova, I; Lukovic, D; Aleman, C; Ardan, T; Drutovic, S; Motlik, J; Ellederova, Z; Stranák, Z; Veith, M; Lytvynchuk, L; Sharma, R; Bharti, K; Petrovski, G; Jendelova, P; Stieger, K; Erceg, S
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SaveSafety of Human USH1C Transgene Expression Following Subretinal Injection in Wild-Type Pigs
Kiraly, Peter; Klein, Joshua; Seitz, Immanuel P.; Reichel, Felix F.; Peters, Tobias; Ardan, Taras; Juhasova, Jana; Juhas, Stefan; Ellederova, Zdenka; Nemesh, Yaroslav; Nyshchuk, Ruslan; Klymiuk, Nikolai; Nagel-Wolfrum, Kerstin; Winslow, Ashley R.; Wolfrum, Uwe; Motlik, Jan; Fischer, M. Dominik
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SaveHuman iPSC-derived RPE cells implantation into minipig eye - Six weeks follow-up study
Ardan, T; Erceg, S; Brymová, A; Studenovska, H; Mueller, B; Stieger, K; Petrovski, G; Lytvynchuk, L; Stranák, Z; Veith, M; Juhás, S; Juhasova, J; Nemesh, Y; Ellederová, Z; Motlik, J
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SaveCircHTT(2,3,4,5,6) - co-evolving with the HTT CAG-repeat tract - modulates Huntington's disease phenotypes
Morandell, Jasmin; Monziani, Alan; Lazioli, Martina; Donzel, Deborah; Doring, Jessica; Pegorar, Claudio Oss; D'Anzi, Angela; Pellegrini, Miguel; Mattiello, Andrea; Bortolotti, Dalia; Bergonzoni, Guendalina; Tripathi, Takshashila; Mattis, Virginia B.; Kovalenko, Marina; Rosati, Jessica; Dieterich, Christoph; Dassi, Erik; Wheeler, Vanessa C.; Ellederova, Zdenka; Wilusz, Jeremy E.; Viero, Gabriella; Biagioli, Marta
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SaveHuman iPSC-derived RPE cells implantation into minipig eye: Two weeks follow-up study
Ardan, Taras; Erceg, Slaven; Artero-Castro, Ana; Studenovska, Hana; Mueller, Brigitte; Stieger, Knut; Lytvynchuk, Lyubomyr; Stranak, Zbynek; Ellederova, Zdenka; Juhas, Stefan; Motlik, Jan; Petrovski, Goran
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SaveIn vitro and in vivo evaluation of genetically corrected RPE cells for autologous cell therapy of hereditary retinal dystrophies
Rodriguez-Jimenez, F. J.; Brymova, A.; Mueller, B.; Stieger, K.; Jendelova, P.; Ardan, T.; Studenovska, H.; Lytvynchuk, L.; Stranak, Z.; Ellederova, Z.; Juhas, J.; Motlik, J.; Petrovski, G.; Erceg, Lukovic D.
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SaveMINIPIG MODELS OF HUNTINGTON'S DISEASE AT PIGMOD CENTER
Vochozkova, Petra Runa; Auch, Hannah; Nemesh, Kateryna; Nyguen, The Duong; Sekac, David; Kamenna, Eva; Baxa, Monika; Klima, Jiri; Ardan, Taras; Juhas, Stefan; Levinska, Bozena; Juhasova, Jana; Keller, Jiri; Klempir, Jiri; Motlik, Jan; Klymiuk, Nikolai; Ellederova, Zdenka
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SaveSubretinal Implantation of Human Primary RPE Cells Cultured on Nanofibrous Membranes in Minipigs
Lytvynchuk, Lyubomyr; Ebbert, Annabelle; Studenovska, Hana; Nagymihaly, Richard; Josifovska, Natasha; Rais, David; Popelka, Stepan; Tichotova, Lucie; Nemesh, Yaroslav; Cizkova, Jana; Juhasova, Jana; Juhas, Stefan; Jendelova, Pavla; Franekova, Janka; Kozak, Igor; Erceg, Slaven; Stranak, Zbynek; Mueller, Brigitte; Ellederova, Zdenka; Motlik, Jan; Stieger, Knut; Ardan, Taras; Petrovski, Goran
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SaveEarly disruption of photoreceptor cell architecture and loss of vision in a humanized pig model of usher syndromes
Grotz, Sophia; Schaefer, Jessica; Wunderlich, Kirsten A.; Ellederova, Zdenka; Auch, Hannah; Baehr, Andrea; Runa-Vochozkova, Petra; Fadl, Janet; Arnold, Vanessa; Ardan, Taras; Veith, Miroslav; Santamaria, Gianluca; Dhom, Georg; Hitzl, Wolfgang; Kessler, Barbara; Eckardt, Christian; Klein, Joshua; Brymova, Anna; Linnert, Joshua; Kurome, Mayuko; Zakharchenko, Valeri; Fischer, Andrea; Blutke, Andreas; Doering, Anna; Suchankova, Stepanka; Popelar, Jiri; Rodriguez-Bocanegra, Eduardo; Dlugaiczyk, Julia; Straka, Hans; May-Simera, Helen; Wang, Weiwei; Laugwitz, Karl-Ludwig; Vandenberghe, Luk H.; Wolf, Eckhard; Nagel-Wolfrum, Kerstin; Peters, Tobias; Motlik, Jan; Fischer, M. Dominik; Wolfrum, Uwe; Klymiuk, Nikolai
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SaveAdvantages of nanofibrous membranes for culturing of primary RPE cells compared to commercial scaffolds
Tichotova, Lucie; Studenovska, Hana; Petrovski, Goran; Popelka, Stepan; Nemesh, Yaroslav; Sedlackova, Miroslava; Drutovic, Saskia; Rohiwal, Sonali; Jendelova, Pavla; Erceg, Slaven; Brymova, Anna; Artero-Castro, Ana; Lytvynchuk, Lyubomyr; Stranak, Zbynek; Ellederova, Zdenka; Motlik, Jan; Ardan, Taras
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SaveCIRCHTT, A CIRCULAR RNA FROM THE HUNTINGTON'S DISEASE GENE LOCUS: FUNCTIONAL CHARACTERIZATION AND POSSIBLE IMPLICATIONS FOR DISEASE MODULATION
Doring, Jessica; Ferrari, Simone; Monziani, Alan; Pegorar, Claudio Oss; Tripathi, Takshashila; Di Leva, Francesca; Kerschbamer, Emanuela; Mattis, Virginia B.; Dieterich, Christoph; Dassi, Erik; Wheeler, Vanessa C.; Hansikova, Hana; Ellederova, Zdenka; Wilusz, Jeremy E.; Biagioli, Marta
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SaveWidespread and sustained target engagement in Huntington's disease minipigs upon intrastriatal microRNA-based gene therapy
Valles, Astrid; Evers, Melvin M.; Stam, Anouk; Sogorb-Gonzalez, Marina; Brouwers, Cynthia; Vendrell-Tornero, Carlos; Acar-Broekmans, Seyda; Paerels, Lieke; Klima, Jiri; Bohuslavova, Bozena; Pintauro, Roberta; Fodale, Valentina; Bresciani, Alberto; Liscak, Roman; Urgosik, Dusan; Starek, Zdenek; Crha, Michal; Blits, Bas; Petry, Harald; Ellederova, Zdenka; Motlik, Jan; van Deventer, Sander; Konstantinova, Pavlina
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SavePolyethylenimine based magnetic nanoparticles mediated non-viral CRISPR/Cas9 system for genome editing
Rohiwal, S. S.; Dvorakova, N.; Klima, J.; Vaskovicova, M.; Senigl, F.; Slouf, M.; Pavlova, E.; Stepanek, P.; Babuka, D.; Benes, H.; Ellederova, Z.; Stieger, K.
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