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R. Jude Samulski

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99H-index
418Paper Count
3.7WCitation Count
Published Papers 163
Publication Date
Cardiotropic AAV gene therapy for heart failure: a phase 1 trial
err2025-10-21
err0
errOAAI
errTimothy D. Henry; Eugene S. Chung; Monica Alvisi; Ferzin Sethna; David R. Murray; Jay H. Traverse; Lothar Roessig; Luke Roberts; Swarna Reddy; Youjun Chen; Tugba Guven Ozkan; Stacy Webb; Monika Mittal; Leigh Ervin; Hesham Sadek; Sheila Mikhail; Kobra Haghighi; Canwen Jiang; R. Jude Samulski; Evangelia G. Kranias; Anna P. Tretiakova; Roger J. Hajjar
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New hope for older SMA patients with next-generation self-complementary AAV gene therapy
err2025-09-22
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PREAI
errHiroyuki Nakai; Erika L. Finanger; Richard Jude Samulski
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AAV vector transduction restriction and attenuated toxicity in hESCs via a rationally designed inverted terminal repeat
err2025-01-24
err0
errOAAI
errSong, Liujiang; Hasegawa, Tomoko; Brown, Nolan J.; Bower, Jacquelyn J.; Samulski, Richard J.; Hirsch, Matthew L.
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AAV vectors: The Rubik's cube of human gene therapy
err2022-12-01
err139
errOAAI
errPupo, Amaury; Fernandez, Audry; Low, Siew Hui; Francois, Achille; Suarez-Amaran, Lester; Samulski, Richard Jude
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Thermostability and in vivo performance of AAV9 in a film matrix
err2022-11-21
err5
errOAAI
errDoan, Trang Nguyen Kieu; Le, Matthew D.; Bajrovic, Irnela; Celentano, Lorne; Krause, Charles; Balyan, Haley Grooms; Svancarek, Abbie; Mote, Angela; Tretiakova, Anna; Samulski, R. Jude; Croyle, Maria A.
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Customized blood-brain barrier shuttle peptide to increase AAV9 vector crossing the BBB and augment transduction in the brain
err2022-02-01
err9
errOAAI
errZhang, Xintao; Chai, Zheng; Dobbins, Amanda Lee; Itano, Michelle S.; Askew, Charles; Miao, Zhe; Niu, Hongqian; Samulski, R. Jude; Li, Chengwen
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Flies in the ointment: AAV vector preparations and tumor risk
err2021-09-01
err7
errOAAI
errZhang, Junping; Yu, Xiangping; Herzog, Roland W.; Samulski, R. Jude; Xiao, Weidong
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Satellite Subgenomic Particles Are Key Regulators of Adeno-Associated Virus Life Cycle
err2021-06-21
err10
errOAAI
errZhang, Junping; Yu, Xiangping; Guo, Ping; Firrman, Jenni; Pouchnik, Derek; Diao, Yong; Samulski, Richard Jude; Xiao, Weidong
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D matters in recombinant AAV DNA packaging
err2021-06-01
err5
errOAAI
errZhang, Junping; Guo, Ping; Xu, Yinxia; Mulcrone, Patrick L.; Samulski, R. Jude; Xiao, Weidong
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Mavis Agbandje-McKenna's lifelong commitment to teaching and research
err2021-05-01
err1
errOAAI
errByrne, Barry J.; McCall, Angela L.; Davidson, Beverly L.; Samulski, R. Jude
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Intrastromal Gene Therapy Prevents and Reverses Advanced Corneal Clouding in a Canine Model of Mucopolysaccharidosis I
err2020-06-01
err29
errOAAI
errMiyadera, Keiko; Conatser, Laura; Llanga, Telmo A.; Carlin, Kendall; O'Donnell, Patricia; Bagel, Jessica; Song, Liujiang; Kurtzberg, Joanne; Samulski, R. Jude; Gilger, Brian; Hirsch, Matthew L.
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MV Capsid-Promoter Interactions Determine CNS Cell-Selective Gene Expression In Vivo
err2020-05-01
err47
errOAAI
errPowell, Sara K.; Samulski, R. Jude; McCown, Thomas J.
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Efficient Capsid Antigen Presentation From Adeno-Associated Virus Empty Virions In Vivo (vol 9, 844, 2018)
err2020-02-04
err0
errOAAI
errPei, Xiaolei; Earley, Lauriel Freya; He, Yi; Chen, Xiaojing; Hall, Nikita Elexa; Samulski, Richard Jude; Li, Chengwen
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Chimeric Capsid Proteins Impact Transduction Efficiency of Haploid Adeno-Associated Virus Vectors
err2019-12-09
err17
errOAAI
errChai, Zheng; Zhang, Xintao; Dobbins, Amanda Lee; Frost, Ellie Azure; Samulski, R. Jude; Li, Chengwen
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Adeno-Associated Virus (AAV) Versus Immune Response
err2019-01-25
err100
errOAAI
errRabinowitz, Joseph; Chan, Ying Kai; Samulski, Richard Jude
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Sub-2 Å Ewald curvature corrected structure of an AAV2 capsid variant
err2018-09-07
err77
errOAAI
errTan, Yong Zi; Aiyer, Sriram; Mietzsch, Mario; Hull, Joshua A.; McKenna, Robert; Grieger, Joshua; Samulski, R. Jude; Baker, Timothy S.; Agbandje-McKenna, Mavis; Lyumkis, Dmitry
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Blood-brain barrier shuttle peptides enhance AAV transduction in the brain after systemic administration
err2018-09-01
err62
errOAAI
errZhang, Xintao; He, Ting; Chai, Zheng; Samulski, R. Jude; Li, Chengwen
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Atomic structure of a rationally engineered gene delivery vector, AAV2.5
err2018-09-01
err25
errOAAI
errBurg, Matthew; Rosebrough, Claire; Drouin, Lauren M.; Bennett, Antonette; Mietzsch, Mario; Chipman, Paul; McKenna, Robert; Sousa, Duncan; Potter, Mark; Byrne, Barry; Samulski, R. Jude; Agbandje-McKenna, Mavis
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