Not logged in Share Save
IL10 gene mutations do not impair Tr1 differentiation in vivo and can be functionally corrected by precise gene editing Strubbe, Steven; Boss, Allison; Wang, Bing; Mantilla, Michelle Mercedes; Freeborn, Robert Arthur; Guevara Becerra, Martha; Gharahdaghi, Nima; Uhlig, Holm H.; Porteus, Matthew Hebden; Arkwright, Peter D.; Roncarolo, Maria-Grazia; Bacchetta, Rosa Share Save
Distinct type I and II interferon responses direct cortical and medullary thymic epithelial cell development Mohammed, Abdulvasey; Wang, Wenqing; Arreola, Martin; Solomon, Benjamin D.; Slepicka, Priscila F.; Hubka, Kelsea M.; Nguyen, Hanh Dan; Zheng, Zihao; Chavez, Michael G.; Yeh, Christine Y.; Kim, Doo Kyung; Ma, Michael R.; Martin, Elisabeth; Li, Li; Pasca, Anca M.; Winn, Virginia D.; Gifford, Casey A.; Kedlian, Veronika R.; Park, Jong-Eun; Khatri, Purvesh; Hollander, Georg A.; Roncarolo, Maria Grazia; Sebastiano, Vittorio; Teichmann, Sarah A.; Weinacht, Katja G. Share Save
Share Save
In utero hematopoietic stem cell transplantation for Fanconi anemia Swartzrock, Leah; Dib, Carla; Denis, Morgane; Willner, Hana; Ho, Katie; Haslett, Ethan; Han, Jian; Pan, Wenjing; Byrne-Steele, Miranda; Brown, Brittany; Krampf, Mark R.; Girsen, Anna; Blumenfeld, Yair J.; El-Sayed, Yasser Y.; Roncarolo, Maria G.; MacKenzie, Tippi C.; Czechowicz, Agnieszka D. Share Save
Transcriptional and epigenetic characterization of a new in vitro platform to model the formation of human pharyngeal endoderm Cipriano, Andrea; Colantoni, Alessio; Calicchio, Alessandro; Fiorentino, Jonathan; Gomes, Danielle; Moqri, Mahdi; Parker, Alexander; Rasouli, Sajede; Caldwell, Matthew; Briganti, Francesca; Roncarolo, Maria Grazia; Baldini, Antonio; Weinacht, Katja G.; Tartaglia, Gian Gaetano; Sebastiano, Vittorio Share Save
AML/T cell interactomics uncover correlates of patient outcomes and the key role of ICAM1 in T cell killing of AML Sayitoglu, Ece Canan; Luca, Bogdan A.; Boss, Allison Paige; Thomas, Benjamin Craig; Freeborn, Robert Arthur; Uyeda, Molly Javier; Chen, Pauline Ping; Nakauchi, Yusuke; Waichler, Colin; Lacayo, Norman; Bacchetta, Rosa; Majeti, Ravindra; Gentles, Andrew J.; Cepika, Alma-Martina; Roncarolo, Maria Grazia Share Save
IL-10-Engineered Human CD4+ Tr1 Cells Eliminate Myeloid Leukemia in an HLA Class I-Dependent Mechanism (Vol.25, 2254, 2017) Locafaro, Grazia; Andolfi, Grazia; Russo, Fabio; Cesana, Luca; Spinelli, Antonello; Camisa, Barbara; Ciceri, Fabio; Lombardo, Angelo; Bondanza, Attilio; Roncarolo, Maria Grazia; Gregori, Silvia Share Save
Share Save
Identification of unstable regulatory and autoreactive effector T cells that are expanded in patients with FOXP3 mutations Borna, Simon; Lee, Esmond; Nideffer, Jason; Ramachandran, Akshaya; Wang, Bing; Baker, Jeanette; Mavers, Melissa; Lakshmanan, Uma; Narula, Mansi; Garrett, Amy Kang-Hee; Schulze, Janika; Olek, Sven; Marois, Louis; Gernez, Yael; Bhatia, Monica; Chong, Hey Jin; Walter, Jolan; Kitcharoensakkul, Maleewan; Lang, Abigail; Cooper, Megan A.; Bertaina, Alice; Roncarolo, Maria Grazia; Meffre, Eric; Bacchetta, Rosa Share Save
SATB1ss Chromatin Loops Regulate Megakaryocyte/Erythroid Progenitor Expansion by Facilitating HSP70 and GATA1 Induction Wilkes, Mark C.; Chae, Hee-Don; Scanlon, Vanessa; Cepika, Alma-Martina; Wentworth, Ethan P.; Saxena, Mallika; Eskin, Ascia; Chen, Zugen; Glader, Bert; Roncarolo, Maria Grazia; Nelson, Stanley F.; Sakamoto, Kathleen M. Share Save
Share Save
Sequential Stem Cell-Kidney Transplantation in Schimke Immuno-osseous Dysplasia Bertaina, Alice; Grimm, Paul C.; Weinberg, Kenneth; Parkman, Robertson; Kristovich, Karen M.; Barbarito, Giulia; Lippner, Elizabeth; Dhamdhere, Girija; Ramachandran, Vasavi; Spatz, Jordan M.; Fathallah-Shaykh, Sahar; Atkinson, T. Prescott; Al-Uzri, Amira; Aubert, Geraldine; van der Elst, Kim; Green, Sean G.; Agarwal, Rajni; Slepicka, Priscila F.; Shah, Ami J.; Roncarolo, Maria G.; Gallo, Amy; Concepcion, Waldo; Lewis, David B. Share Save
Share Save
Pre-clinical development and molecular characterization of an engineered type 1 regulatory T-cell product suitable for immunotherapy Liu, Jeffrey Mao-Hwa; Chen, Ping; Uyeda, Molly Javier; Cieniewicz, Brandon; Sayitoglu, Ece Canan; Thomas, Benjamin Craig; Sato, Yohei; Bacchetta, Rosa; Cepika, Alma-Martina; Roncarolo, Maria Grazia Share Save
Alloantigen-specific type 1 regulatory T cells suppress through CTLA-4 and PD-1 pathways and persist long-term in patients Chen, Pauline P.; Cepika, Alma-Martina; Agarwal-Hashmi, Rajni; Saini, Gopin; Uyeda, Molly J.; Louis, David M.; Cieniewicz, Brandon; Narula, Mansi; Hernandez, Laura C. Amaya; Harre, Nicholas; Xu, Liwen; Thomas, Benjamin Craig; Ji, Xuhuai; Shiraz, Parveen; Tate, Keri M.; Margittai, Dana; Bhatia, Neehar; Meyer, Everett; Bertaina, Alice; Davis, Mark M.; Bacchetta, Rosa; Roncarolo, Maria Grazia Share Save
Share Save
BHLHE40 Regulates IL-10 and IFN-γ Production in T Cells but Does Not Interfere With Human Type 1 Regulatory T Cell Differentiation Uyeda, Molly Javier; Freeborn, Robert A. A.; Cieniewicz, Brandon; Romano, Rosa; Chen, Ping (Pauline); Liu, Jeffrey Mao-Hwa; Thomas, Benjamin; Lee, Esmond; Cepika, Alma-Martina; Bacchetta, Rosa; Roncarolo, Maria Grazia Share Save
Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease Lattanzi, Annalisa; Camarena, Joab; Lahiri, Premanjali; Segal, Helen; Srifa, Waracharee; Vakulskas, Christopher A.; Frock, Richard L.; Kenrick, Josefin; Lee, Ciaran; Talbott, Narae; Skowronski, Jason; Cromer, M. Kyle; Charlesworth, Carsten T.; Bak, Rasmus O.; Mantri, Sruthi; Bao, Gang; DiGiusto, David; Tisdale, John; Wright, J. Fraser; Bhatia, Neehar; Roncarolo, Maria Grazia; Dever, Daniel P.; Porteus, Matthew H. Share Save
Share Save