Not logged inDeath after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy
Lek, Angela; Wong, Brenda; Keeler, Allison; Blackwood, Meghan; Ma, Kaiyue; Huang, Shushu; Sylvia, Katelyn; Batista, A. Rita; Artinian, Rebecca; Kokoski, Danielle; Parajuli, Shestruma; Putra, Juan; Carreon, C. Katte; Lidov, Hart; Woodman, Keryn; Pajusalu, Sander; Spinazzola, Janelle M.; Gallagher, Thomas; Larovere, Joan; Balderson, Diane; Black, Lauren; Sutton, Keith; Horgan, Richard; Lek, Monkol; Flotte, Terence
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SaveNovel Combinatorial MicroRNA-Binding Sites in AAV Vectors Synergistically Diminish Antigen Presentation and Transgene Immunity for Efficient and Stable Transduction
Muhuri, Manish; Zhan, Wei; Maeda, Yukiko; Li, Jia; Lotun, Anoushka; Chen, Jennifer; Sylvia, Katelyn; Dasgupta, Ishani; Arjomandnejad, Motahareh; Nixon, Thomas; Keeler, Allison M.; Manokaran, Sangeetha; He, Ran; Su, Qin; Tai, Phillip W. L.; Gao, Guangping
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SaveA Network of High-Mobility Group Box Transcription Factors Programs Innate Interleukin-17 Production
Malhotra, Nidhi; Narayan, Kavitha; Cho, Ok Hyun; Sylvia, Katelyn E.; Yin, Catherine; Melichar, Heather; Rashighi, Mehdi; Lefebvre, Veronique; Harris, John E.; Berg, Leslie J.; Kang, Joonsoo
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SaveThe Tec Kinase ITK Regulates Thymic Expansion, Emigration, and Maturation of γδ NKT Cells
Yin, Catherine C.; Cho, Ok Hyun; Sylvia, Katelyn E.; Narayan, Kavitha; Prince, Amanda L.; Evans, John W.; Kang, Joonsoo; Berg, Leslie J.
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SaveIntrathymic programming of effector fates in three molecularly distinct γδ T cell subtypes
Narayan, Kavitha; Sylvia, Katelyn E.; Malhotra, Nidhi; Yin, Catherine C.; Martens, Gregory; Vallerskog, Therese; Kornfeld, Hardy; Xiong, Na; Cohen, Nadia R.; Brenner, Michael B.; Berg, Leslie J.; Kang, Joonsoo
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