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SaveA precise and efficient adenine base editor
Tu, Tianxiang; Song, Zongming; Liu, Xiaoyu; Wang, Shengxing; He, Xiaoxue; Xi, Haitao; Wang, Jiahua; Yan, Tong; Chen, Haoran; Zhang, Zhenwu; Lv, Xiujuan; Lv, Jineng; Huang, Xiu-Feng; Zhao, Junzhao; Lin, Chao-Po; Gao, Caixia; Zhang, Jinwei; Gu, Feng
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SaveDepletion of miR-96 Delays, But Does Not Arrest, Photoreceptor Development in Mice
Xiang, Lue; Zhang, Juan; Rao, Feng-Qin; Yang, Qiao-Li; Zeng, Hui-Yi; Huang, Sheng-Hai; Xie, Zhen-Xiang; Lv, Ji-Neng; Lin, Dan; Chen, Xue-Jiao; Wu, Kun-Chao; Lu, Fan; Huang, Xiu-Feng; Chen, Qi
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SaveHuman cell based directed evolution of adenine base editors with improved efficiency
Fu, Junhao; Li, Qing; Liu, Xiaoyu; Tu, Tianxiang; Lv, Xiujuan; Yin, Xidi; Lv, Jineng; Song, Zongming; Qu, Jia; Zhang, Jinwei; Li, Jinsong; Gu, Feng
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SaveEngineered FnCas12a with enhanced activity through directional evolution in human cells
Liu, Xiexie; Liu, Xiaoyu; Zhou, Chenchen; Lv, Jineng; He, Xiubin; Liu, Yuanyuan; Xie, Haihua; Wang, Bang; Lv, Xiujuan; Tang, Lianchao; Li, Mingchun; Liu, Changbao; Zhao, Junzhao; Liu, Yong; Song, Zongming; Gu, Feng
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SaveNonhuman Primate Model of Oculocutaneous Albinismwith TYR and OCA2 Mutations
Wu, Kun-Chao; Lv, Ji-Neng; Yang, Hui; Yang, Feng-Mei; Lin, Rui; Lin, Qiang; Shen, Ren-Juan; Wang, Jun-Bin; Duan, Wen-Hua; Hu, Min; Zhang, Jun; He, Zhan-Long; Jin, Zi-Bing
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SaveGene Correction Reverses Ciliopathy and Photoreceptor Loss in iPSC-Derived Retinal Organoids from Retinitis Pigmentosa Patients (vol 10, pg 1267, 2018)
Deng, Wen-Li; Gao, Mei-Ling; Lei, Xin-Lan; Lv, Ji-Neng; Zhao, Huan; He, Kai-Wen; Xia, Xi-Xi; Li, Ling-Yun; Chen, Yu-Chen; Li, Yan-Ping; Pan, Deng; Xue, Tian; Jin, Zi-Bing
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SaveGene Correction Reverses Ciliopathy and Photoreceptor Loss in iPSC-Derived Retinal Organoids from Retinitis Pigmentosa Patients
Deng, Wen-Li; Gao, Mei-Ling; Lei, Xin-Lan; Lv, Ji-Neng; Zhao, Huan; He, Kai-Wen; Xia, Xi-Xi; Li, Ling-Yun; Chen, Yu-Chen; Li, Yan-Ping; Pan, Deng; Xue, Tian; Jin, Zi-Bing
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SavemiR-183/96 plays a pivotal regulatory role in mouse photoreceptor maturation and maintenance
Xiang, Lue; Chen, Xue-Jiao; Wu, Kun-Chao; Zhang, Chang-Jun; Zhou, Gao-Hui; Lv, Ji-Neng; Sun, Lan-Fang; Cheng, Fei-Fei; Cai, Xue-Bi; Jin, Zi-Bing
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SaveTargeted RP9 ablation and mutagenesis in mouse photoreceptor cells by CRISPR-Cas9
Lv, Ji-Neng; Zhou, Gao-Hui; Chen, Xuejiao; Chen, Hui; Wu, Kun-Chao; Xiang, Lue; Lei, Xin-Lan; Zhang, Xiao; Wu, Rong-Han; Jin, Zi-Bing
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SaveSLC7A14 linked to autosomal recessive retinitis pigmentosa
Jin, Zi-Bing; Huang, Xiu-Feng; Lv, Ji-Neng; Xiang, Lue; Li, Dong-Qing; Chen, Jiangfei; Huang, Changjiang; Wu, Jinyu; Lu, Fan; Qu, Jia
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SaveAAV-Mediated Lysophosphatidylcholine Acyltransferase 1 (Lpcat1) Gene Replacement Therapy Rescues Retinal Degeneration in rd11 Mice
Dai, Xufeng; Han, Juanjuan; Qi, Yan; Zhang, Hua; Xiang, Lue; Lv, Jineng; Li, Jie; Deng, Wen-Tao; Chang, Bo; Hauswirth, William W.; Pang, Ji-jing
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SaveLECT2 protects mice against bacterial sepsis by activating macrophages via the CD209a receptor
Lu, Xin-Jiang; Chen, Jiong; Yu, Chao-Hui; Shi, Yu-Hong; He, Yu-Qing; Zhang, Rui-Cheng; Huang, Zuo-An; Lv, Ji-Neng; Zhang, Shun; Xu, Lei
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