Haydar Frangoul - Publications, H-index & Citations

Back

Haydar Frangoul

Sarah Cannon Research Institute

42H-index

266Paper Count

7.5KCitation Count

Published Papers 41

Publication Date

Incidence of Human Leukocyte Antigen (HLA) Class I Antibodies and Impact on Platelet Engraftment, Transfusions and Bleeding in Recipients of Gene Therapy for Sickle Cell Disease and Transfusion Dependent Beta Thalassemia

Transplantation and Cellular Therapy

IF4.4

2026-08-15

PREAI

Haydar Frangoul; Meghann McManus; Clinton Carroll; Sallyanne Fossey; Mathew Rowe; Addison Roelandts; Eileen McCartney; Shelby Aide; Amanda Stults; Sam Forbes; Christy Riggins; Kala Morgan; Rayea Tilman; Morgan Duckworth; Natalie Davis; Katie Bruce; Minoo Battiwala; Jennifer Domm; Misty Evans

Save

Prime Editing for p47phox-Deficient Chronic Granulomatous Disease

NEW ENGLAND JOURNAL OF MEDICINE

IF78.5

2025-12-01

PREAI

Gori, Jennifer L.; Haddad, Elie; Frangoul, Haydar; Kohn, Donald B.; Morris, Emma C.; Martin, Bradley N.; Deary, Briana A.; Nickerson, McKinley; Scholz, Rebecca L.; Fernandez, Isabel; Leveille, Karine; De Ravin, Suk See; Kang, Elizabeth M.; Pierzynski, Marie; Estwick, Tyra; Littel, Patricia; Kuhns, Douglas B.; Long Priel, Debra A.; Teira, Pierre; Turvey, Stuart; Arnold, Jordyn; Evans, Misty D.; McManus, Meghann; Carpenter, Ben; Waterman, David P.; Anzalone, Andrew V.; Petrusich, Alexandria; Osuna, Christa E.; O'Malley, Tiernan T.; Stewart-Ornstein, Jacob; Heath, Jack M.; Nehilla, Barrett J.; Asmal, Mohammed; Malech, Harry L.

Save

Improvements in Health-Related Quality of Life in Patients with Transfusion-Dependent β-Thalassemia After Exagamglogene Autotemcel

Blood Advances

IF7.1

2025-08-28

OAAI

Josu de la Fuente; Haydar Frangoul; Peter Lang; Donna Wall; Roland Meisel; Selim Corbacioglu; Amanda M. Li; Ami J. Shah; Ben Carpenter; Janet L. Kwiatkowski; Markus Y. Mapara; Robert I. Liem; Joachim Rupprecht; Kevin H.M. Kuo; Hayley Merkeley; Mattia Algeri; Wally Smith; Puja Kohli; Nanxin Li; Jaime Rubin; Siyu Zhang; William Hobbs; Franco Locatelli

Save

Improvements in Health-Related Quality of Life in Patients with Severe Sickle Cell Disease After Exagamglogene Autotemcel

Blood Advances

IF7.1

2025-08-28

OAAI

Akshay Sharma; Franco Locatelli; Monica Bhatia; Lyndsay Molinari; Markus Y. Mapara; Robert I. Liem; Laurence Dedeken; Donna Wall; Michael J. Eckrich; Kevin H. M. Kuo; Wally Smith; Suzan Imren; Puja Kohli; Nanxin Li; Tina Liu; Jaime Rubin; William Hobbs; Stephan A. Grupp; Haydar Frangoul

Save

Gene Therapy for HbSC Disease and other Compound Heterozygous Sickle Hemoglobinopathies: A Time for Inclusion

Blood

IF23.1

2025-08-22

PREAI

Andrew Wilks; Martin H. Steinberg; Haydar Frangoul

Save

Safety and Feasibility of Fertility Preservation and Fertility Outcomes in Patients with Sickle Cell Disease and Transfusion Dependent Beta Thalassemia Undergoing Gene Therapy

Transplantation and Cellular Therapy

IF4.4

2025-08-06

PREAI

Sarah Hmaidan; Kristin Van Heertum; Shreya Bhatia; Jennifer Domm; Meghann McManus; Clinton Carroll; Amanda Stults; Katie Bruce; Misty Evans; Haydar Frangoul

Save

Best Practices in Gene Therapy for Sickle Cell Disease and Transfusion-dependent β-Thalassemia

Transplantation and Cellular Therapy

IF4.4

2025-06-01

PREAI

Haydar Frangoul; Amanda Stults; Katie Bruce; Jennifer Domm; Clinton Carroll; Shelby Aide; Morgan Duckworth; Misty Evans; Meghann McManus

Save

Impact of Different Definitions of Vaso-Occlusion on Efficacy Assessments in Sickle Cell Disease Clinical Trials

ADVANCES IN THERAPY

IF4

2025-03-01

OAAI

Frangoul, Haydar; Locatelli, Franco; Eckrich, Michael J.; Imren, Suzan; Li, Nanxin; Xuan, Fengjuan; Grupp, Stephan A.

Save

Reni-Cel, an Investigational AsCas12a Gene-Edited Cell Medicine, Led to Successful Engraftment, Increased Hemoglobin, and Reduced Transfusion Dependence in Patients with Transfusion-Dependent Beta-Thalassemia Treated in the Edithal Trial

BLOOD

IF23.1

2024-11-05

PREAI

Frangoul, Haydar; Hanna, Rabi; Walters, Mark C.; Chang, Kai-Hsin; Jaskolka, Michael; Kim, Keunpyo; Mei, Baisong; Afonja, Olubunmi; Thompson, Alexis

Save

Impact of Race and Ethnicity on Outcomes After Umbilical Cord Blood Transplantation

TRANSPLANTATION AND CELLULAR THERAPY

IF4.4

2024-10-01

PREAI

Ballen, Karen; Wang, Tao; He, Naya; Knight, Jennifer M.; Hong, Sanghee; Frangoul, Haydar; Verdonck, Leo F.; Steinberg, Amir; Diaz, Miguel A.; Lemaistre, C. Fred; Badawy, Sherif M.; Pu, Jeffrey J.; Hashem, Hasan; Savani, Bipin; Sharma, Akshay; Lazarus, Hillard M.; Abid, Muhammad Bilal; Tay, Jason; Rangarajan, Hemalatha G.; Kindwall-Keller, Tamila; Freytes, Cesar O.; Beitinjaneh, Amer; Winestone, Lena E.; Gergis, Usama; Farhadfar, Nosha; Bhatt, Neel S.; Schears, Raquel M.; Gomez-Almaguer, David; Aljurf, Mahmoud; Agrawal, Vaibhav; Kuwatsuka, Yachiyo; Seo, Sachiko; Marks, David I.; Lehmann, Leslie; Wood, William A.; Hashmi, Shahrukh; Saber, Wael

Save

Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia

NEW ENGLAND JOURNAL OF MEDICINE

IF78.5

2024-05-09

PREAI

Locatelli, F.; Lang, P.; Wall, D.; Meisel, R.; Corbacioglu, S.; Li, A. M.; de la Fuente, J.; Shah, A. J.; Carpenter, B.; Kwiatkowski, J. L.; Mapara, M.; Liem, R. I.; Cappellini, M. D.; Algeri, M.; Kattamis, A.; Sheth, S.; Grupp, S.; Handgretinger, R.; Kohli, P.; Shi, D.; Ross, L.; Bobruff, Y.; Simard, C.; Zhang, L.; Morrow, P. K.; Hobbs, W. E.; Frangoul, H.

Save

Exagamglogene Autotemcel for Severe Sickle Cell Disease

NEW ENGLAND JOURNAL OF MEDICINE

IF78.5

2024-05-09

PREAI

Frangoul, H.; Locatelli, F.; Sharma, A.; Bhatia, M.; Mapara, M.; Molinari, L.; Wall, D.; Liem, R. I.; Telfer, P.; Shah, A. J.; Cavazzana, M.; Corbacioglu, S.; Rondelli, D.; Meisel, R.; Dedeken, L.; Lobitz, S.; de Montalembert, M.; Steinberg, M. H.; Walters, M. C.; Eckrich, M. J.; Imren, S.; Bower, L.; Simard, C.; Zhou, W.; Xuan, F.; Morrow, P. K.; Hobbs, W. E.; Grupp, S. A.

Save

Autologous gene therapy for hemoglobinopathies: From bench to patient's bedside

MOLECULAR THERAPY

IF12

2024-05-01

OAAI

Locatelli, Franco; Cavazzana, Marina; Frangoul, Haydar; de la Fuente, Josu; Algeri, Mattia; Meisel, Roland

Save

Defining curative endpoints for transfusion-dependent β-thalassemia in the era of gene therapy and gene editing

AMERICAN JOURNAL OF HEMATOLOGY

IF9.9

2023-12-15

OAAI

Corbacioglu, Selim; Frangoul, Haydar; Locatelli, Franco; Hobbs, William; Walters, Mark

Save

Defining curative endpoints for sickle cell disease in the era of gene therapy and gene editing

AMERICAN JOURNAL OF HEMATOLOGY

IF9.9

2023-11-27

PREAI

Locatelli, Franco; Corbacioglu, Selim; Hobbs, William; Frangoul, Haydar; Walters, Mark C.

Save

An integrated therapeutic approach to sickle cell disease management beyond infancy

AMERICAN JOURNAL OF HEMATOLOGY

IF9.9

2023-05-12

PREAI

Ribeil, Jean-Antoine; Pollock, Galia; Frangoul, Haydar; Steinberg, Martin H.

Save

Gene editing for sickle cell disease and transfusion dependent thalassemias- A cure within reach

SEMINARS IN HEMATOLOGY

IF4.1

2023-01-01

PREAI

Eckrich, Michael J.; Frangoul, Haydar

Save

Clinical Characteristics and Outcomes of COVID-19 in Pediatric and Early Adolescent and Young Adult Hematopoietic Stem Cell Transplant Recipients: A Cohort Study

TRANSPLANTATION AND CELLULAR THERAPY

IF4.4

2022-10-01

OAAI

Bhatt, Neel S.; Sharma, Akshay; St Martin, Andrew; Abid, Muhammad Bilal; Brown, Valerie, I; Diaz Perez, Miguel Angel; Frangoul, Haydar; Gadalla, Shahinaz M.; Herr, Megan M.; Krem, Maxwell M.; Lazarus, Hillard M.; Martens, Michael J.; Mehta, Parinda A.; Nishihori, Taiga; Prestidge, Tim; Pulsipher, Michael A.; Rangarajan, Hemalatha G.; Williams, Kirsten M.; Winestone, Lena E.; Yin, Dwight E.; Riches, Marcie L.; Dandoy, Christopher E.; Auletta, Jeffery J.

Save

Safety, Tolerability, and Population Pharmacokinetics of Intravenous and Oral Isavuconazonium Sulfate in Pediatric Patients

ANTIMICROBIAL AGENTS AND CHEMOTHERAPY

IF4.5

2021-07-16

OAAI

Arrieta, Antonio C.; Neely, Michael; Day, J. Christopher; Rheingold, Susan R.; Sue, Paul K.; Muller, William J.; Danziger-Isakov, Lara A.; Chu, Julie; Yildirim, Inci; McComsey, Grace A.; Frangoul, Haydar A.; Chen, Tempe K.; Statler, Victoria A.; Steinbach, William J.; Yin, Dwight E.; Hamed, Kamal; Jones, Mark E.; Lademacher, Christopher; Desai, Amit; Micklus, Kelley; Phillips, Desiree Leiva; Kovanda, Laura L.; Walsh, Thomas J.

Save

CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia

NEW ENGLAND JOURNAL OF MEDICINE

IF78.5

2021-01-21

1.1K

OAAI

Frangoul, H.; Altshuler, D.; Cappellini, M. D.; Chen, Y-S; Domm, J.; Eustace, B. K.; Foell, J.; de la Fuente, J.; Grupp, S.; Handgretinger, R.; Ho, T. W.; Kattamis, A.; Kernytsky, A.; Lekstrom-Himes, J.; Li, A. M.; Locatelli, F.; Mapara, M. Y.; de Montalembert, M.; Rondelli, D.; Sharma, A.; Sheth, S.; Soni, S.; Steinberg, M. H.; Wall, D.; Yen, A.; Corbacioglu, S.

Save

Research Directions