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SaveAOC 1044 induces exon 44 skipping and restores dystrophin protein in preclinical models of Duchenne muscular dystrophy
Etxaniz, Usue; Marks, Isaac; Albin, Tyler; Diaz, Matthew; Bhardwaj, Raghav; Anderson, Aaron; Tyaglo, Olecya; Hoang, Tiffany; Missinato, Maria Azzurra; Svensson, Kristoffer; Badillo, Ben; Kovach, Philip R.; Leung, Laura; Cochran, Michael; Kwon, Hae Won; Ahad Shah, Md Nur; Maruyama, Rika; Yokota, Toshifumi; Doppalapudi, Venkata R.; Darimont, Beatrice; Younis, Husam S.; Flanagan, W. Michael; Levin, Arthur A.; Huang, Hanhua; Karamanlidis, Georgios
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SaveStructure-Activity Relationship of Antibody-Oligonucleotide Conjugates: Evaluating Bioconjugation Strategies for Antibody-Phosphorodiamidate Morpholino Oligomer Conjugates for Drug Development
Cochran, Michael; Marks, Isaac; Albin, Tyler; Arias, Danny; Kovach, Philip; Darimont, Beatrice; Huang, Hanhua; Etxaniz, Usue; Kwon, Hae Won; Shi, Yunyu; Diaz, Matthew; Tyaglo, Olecya; Levin, Arthur; Doppalapudi, Venkata Ramana
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SaveEngineering Protein Nanoparticles Functionalized with an Immunodominant Coxiella burnetii Antigen to Generate a Q Fever Vaccine
Ramirez, Aaron; Felgner, Jiin; Jain, Aarti; Jan, Sharon; Albin, Tyler J.; Badten, Alexander J.; Gregory, Anthony E.; Nakajima, Rie; Jasinskas, Algimantas; Felgner, Philip L.; Burkhardt, Amanda M.; Davies, D. Huw; Wang, Szu-Wen
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SaveMagnitude and breadth of antibody cross-reactivity induced by recombinant influenza hemagglutinin trimer vaccine is enhanced by combination adjuvants
Hernandez-Davies, Jenny E.; Dollinger, Emmanuel P.; Pone, Egest J.; Felgner, Jiin; Liang, Li; Strohmeier, Shirin; Jan, Sharon; Albin, Tyler J.; Jain, Aarti; Nakajima, Rie; Jasinskas, Algimantas; Krammer, Florian; Esser-Kahn, Aaron; Felgner, Philip L.; Nie, Qing; Davies, D. Huw
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SaveSubunit Vaccines Using TLR Triagonist Combination Adjuvants Provide Protection Against Coxiella burnetii While Minimizing Reactogenic Responses
Fratzke, Alycia P.; Jan, Sharon; Felgner, Jiin; Liang, Li; Nakajima, Rie; Jasinskas, Algis; Manna, Saikat; Nihesh, Fnu N.; Maiti, Sampa; Albin, Tyler J.; Esser-Kahn, Aaron P.; Davies, D. Huw; Samuel, James E.; Felgner, Philip L.; Gregory, Anthony E.
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SaveTuning Subunit Vaccines with Novel TLR Triagonist Adjuvants to Generate Protective Immune Responses against Coxiella burnetii
Gilkes, Adrienne P.; Albin, Tyler J.; Manna, Saikat; Supnet, Medalyn; Ruiz, Sara; Tom, Janine; Badten, Alexander J.; Jain, Aarti; Nakajima, Rie; Felgner, Jiin; Davies, D. Huw; Stetkevich, Samuel A.; Zlotnik, Albert; Pearlman, Eric; Nalca, Aysegul; Felgner, Philip L.; Esser-Kahn, Aaron P.; Burkhardt, Amanda M.
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SaveLinked Toll-Like Receptor Triagonists Stimulate Distinct, Combination-Dependent Innate Immune Responses
Albin, Tyler J.; Tom, Janine K.; Manna, Saikat; Gilkes, Adrienne P.; Stetkevich, Samuel A.; Katz, Benjamin B.; Supnet, Medalyn; Felgner, Jiin; Jain, Aarti; Nakajima, Rie; Jasinskas, Algis; Zlotnik, Albert; Pearlman, Eric; Davies, D. Huw; Felgner, Phillip L.; Burkhardt, Amanda M.; Esser-Kahn, Aaron P.
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