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SaveCreating New Cis-Regulatory Elements of HBD to Reactivate Delta-Globin
Chen, Lini; Liu, Diandian; Hong, Weicong; Xu, Luhong; Cheng, Lin; Luo, Ying; Xu, Hui; Liang, Junbin; Fang, Jianpei; Li, Xinyu
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SaveUpdated Safety and Efficacy Results of RM-001, Autologous HBG1/2 Promoter-Modified CD34+Hematopoietic Stem and Progenitor Cells, in Treating Transfusion-Dependent β-Thalassemia
Liu, Rongrong; Wang, Li; Xu, Hui; Fang, Jianpei; Liu, Sixi; Yin, Xiaolin; Liang, Junbin; Li, Xinyu; Li, Yue; Yang, Gaohui; Li, Yaoyun; Zhou, Yali; Shi, Lei; Lai, Yongrong; Huang, Junjiu; Zhang, Xinhua
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SaveFirst-in-Human Study of Autologous HBA2-Edited CD34+Hematopoietic Stem and Progenitor Cells in Alpha-Thalassemia with Constant Spring Mutation
Wang, Li; Xu, Hui; Liang, Junbin; Li, Yaoyun; Cheng, Lin; Luo, Ying; Huang, Liancheng; Shi, Lei; Zeng, Lihong; Luo, Rongrong; Xiao, Bin; Liu, Meiping; Huang, Liping; Xiao, Zhendong; Zhang, Xinhua; Huang, Junjiu
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