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SaveCarbohydrate sulfotransferase 14 gene deletion induces dermatan sulfate deficiency and affects collagen structure and bowel contraction
Ono, Fumiko; Takahashi, Yuki; Shimada, Shin; Mizumoto, Shuji; Miyata, Shinji; Nitahara-Kasahara, Yuko; Yamada, Shuhei; Okada, Takashi; Kosho, Tomoki; Yoshizawa, Takahiro
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SaveAdeno-Associated Virus Self-Assembled with Tannic Acid and Phenylboronic Acid Polymers to Evade Neutralizing Antibodies and Reduce Adverse Events
Honda, Y; Nagao, S; Kinoh, H; Liu, XY; Matsudaira, N; Dirisala, A; Nitta-Matsutomo, S; Nomoto, T; Hayashita-Kinoh, H; Miura, Y; Okada, T; Nishiyama, N
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SaveIdentifying Viral Vector Characteristics by Nanopore Sensing
Tsutsui, Makusu; Wada, Mikako; Arima, Akihide; Tsunekawa, Yuji; Sasaki, Takako; Sakamoto, Kenji; Yokota, Kazumichi; Baba, Yoshinobu; Kawai, Tomoji; Okada, Takashi
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SaveApplications and Limitations of Equilibrium Density Gradient Analytical Ultracentrifugation for the Quantitative Characterization of Adeno-Associated Virus Vectors
Hirohata, Kiichi; Yamaguchi, Yuki; Maruno, Takahiro; Shibuya, Risa; Torisu, Tetsuo; Onishi, Takayuki; Chono, Hideto; Mineno, Junichi; Yuzhe, Yuan; Higashiyama, Kiyoko; Masumi-Koizumi, Kyoko; Uchida, Kazuhisa; Yamamoto, Takenori; Uchida, Eriko; Okada, Takashi; Uchiyama, Susumu
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SaveDevelopment of a novel purification method for AAV vectors using tangential flow filtration
Miyaoka, Rimi; Tsunekawa, Yuji; Kurosawa, Yae; Sasaki, Takako; Onodera, Azusa; Sakamoto, Kenji; Kakiuchi, Yuko; Wada, Mikako; Nitahara-Kasahara, Yuko; Hayashita-Kinoh, Hiromi; Okada, Takashi
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SaveLONRF2 is a protein quality control ubiquitin ligase whose deficiency causes late-onset neurological deficits
Li, Dan; Johmura, Yoshikazu; Morimoto, Satoru; Doi, Miyuki; Nakanishi, Keiko; Ozawa, Manabu; Tsunekawa, Yuji; Inoue-Yamauchi, Akane; Naruse, Hiroya; Matsukawa, Takashi; Takeshita, Yukio; Suzuki, Naoki; Aoki, Masashi; Nishiyama, Ayumi; Zeng, Xin; Konishi, Chieko; Suzuki, Narumi; Nishiyama, Atsuya; Harris, Alexander Stephen; Morita, Mariko; Yamaguchi, Kiyoshi; Furukawa, Yoichi; Nakai, Kenta; Tsuji, Shoji; Yamazaki, Satoshi; Yamanashi, Yuji; Shimada, Shoichi; Okada, Takashi; Okano, Hideyuki; Toda, Tatsushi; Nakanishi, Makoto
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SaveImmunomodulatory amnion-derived mesenchymal stromal cells preserve muscle function in a mouse model of Duchenne muscular dystrophy
Nitahara-Kasahara, Yuko; Nakayama, Soya; Kimura, Koichi; Yamaguchi, Sho; Kakiuchi, Yuko; Nito, Chikako; Hayashi, Masahiro; Nakaishi, Tomoyuki; Ueda, Yasuyoshi; Okada, Takashi
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SaveDrinking hydrogen water improves photoreceptor structure and function in retinal degeneration 6 mice
Igarashi, Tsutomu; Ohsawa, Ikuroh; Kobayashi, Maika; Miyazaki, Kai; Igarashi, Toru; Kameya, Shuhei; Shiozawa, Asaka Lee; Ikeda, Yasuhiro; Miyagawa, Yoshitaka; Sakai, Mashito; Okada, Takashi; Sakane, Iwao; Takahashi, Hiroshi
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SaveCDP-ribitol prodrug treatment ameliorates ISPD-deficient muscular dystrophy mouse model
Tokuoka, Hideki; Imae, Rieko; Nakashima, Hitomi; Manya, Hiroshi; Masuda, Chiaki; Hoshino, Shunsuke; Kobayashi, Kazuhiro; Lefeber, Dirk J.; Matsumoto, Riki; Okada, Takashi; Endo, Tamao; Kanagawa, Motoi; Toda, Tatsushi
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SaveA new mouse model of Ehlers-Danlos syndrome generated using CRISPR/Cas9-mediated genomic editing
Nitahara-Kasahara, Yuko; Mizumoto, Shuji; Inoue, Yukiko U.; Saka, Shota; Posadas-Herrera, Guillermo; Nakamura-Takahashi, Aki; Takahashi, Yuki; Hashimoto, Ayana; Konishi, Kohei; Miyata, Shinji; Masuda, Chiaki; Matsumoto, Emi; Maruoka, Yasunobu; Yoshizawa, Takahiro; Tanase, Toshiki; Inoue, Takayoshi; Yamada, Shuhei; Nomura, Yoshihiro; Takeda, Shin'ichi; Watanabe, Atsushi; Kosho, Tomoki; Okada, Takashi
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