Not logged in Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency Booth, Claire; Masiuk, Katelyn; Vazouras, Konstantinos; Fernandes, Augustine; Xu-Bayford, Jinhua; Campo Fernandez, Beatriz; Roy, Sohini; Curio-Penny, Beatrice; Arnold, Jordyn; Terrazas, Dayna; Reid, Jack; Gilmour, Kimberly C.; Adams, Stuart; Alvarez Mediavilla, Elena; Mhaldien, Lana; O'Toole, Grainne; Ahmed, Rima; Garabedian, Elizabeth; Malech, Harry; De Ravin, Suk See; Moore, Theodore B.; De Oliveira, Satiro; Pellin, Danilo; Lin, Tsai-Yu; Dang, Thao Thi; Cornetta, Kenneth; Hershfield, Michael S.; Hara, Havinder; Thrasher, Adrian J.; Gaspar, H. Bobby; Kohn, Donald B. Share Save
Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy Eichler, Florian; Duncan, Christine N.; Musolino, Patricia L.; Lund, Troy C.; Gupta, Ashish O.; De Oliveira, Satiro; Thrasher, Adrian J.; Aubourg, Patrick; Kuehl, Joern-Sven; Loes, Daniel J.; Amartino, Hernan; Smith, Nicholas; Fernandes, Juliana Folloni; Sevin, Caroline; Sankar, Raman; Hussain, Shaun A.; Gissen, Paul; Dalle, Jean-Hugues; Platzbecker, Uwe; Downey, Gerald F.; McNeil, Elizabeth; Demopoulos, Laura; Dietz, Andrew C.; Thakar, Himal L.; Orchard, Paul J.; Williams, David A. Share Save
Antiviral cellular therapy for enhancing T-cell reconstitution before or after hematopoietic stem cell transplantation (ACES): a two-arm, open label phase II interventional trial of pediatric patients with risk factor assessment Keller, Michael D.; Hanley, Patrick J.; Chi, Yueh-Yun; Aguayo-Hiraldo, Paibel; Dvorak, Christopher C.; Verneris, Michael R.; Kohn, Donald B.; Pai, Sung-Yun; Saldana, Blachy J. Davila; Hanisch, Benjamin; Quigg, Troy C.; Adams, Roberta H.; Dahlberg, Ann; Chandrakasan, Shanmuganathan; Hasan, Hasibul; Malvar, Jemily; Jensen-Wachspress, Mariah A.; Lazarski, Christopher A.; Sani, Gelina; Idso, John M.; Lang, Haili; Chansky, Pamela; McCann, Chase D.; Tanna, Jay; Abraham, Allistair A.; Webb, Jennifer L.; Shibli, Abeer; Keating, Amy K.; Satwani, Prakash; Muranski, Pawel; Hall, Erin; Eckrich, Michael J.; Shereck, Evan; Miller, Holly; Mamcarz, Ewelina; Agarwal, Rajni; De Oliveira, Satiro N.; Vander Lugt, Mark T.; Ebens, Christen L.; Aquino, Victor M.; Bednarski, Jeffrey J.; Chu, Julia; Parikh, Suhag; Whangbo, Jennifer; Lionakis, Michail; Zambidis, Elias T.; Gourdine, Elizabeth; Bollard, Catherine M.; Pulsipher, Michael A. Share Save
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Mediport use as an acceptable standard for CAR T cell infusion Eylon, Maya; Prabhu, Snehit; John, Samuel; King, Maxwell J. M.; Bhatt, Dhruv; Curran, Kevin J.; Erickson, Courtney; Karras, Nicole A.; Phillips, Christine L.; Satwani, Prakash; Hermiston, Michelle; Southworth, Erica; Baumeister, Susanne H. C.; Talano, Julie-An; MacMillan, Margaret L.; Rossoff, Jenna; Bonifant, Challice L.; Myers, Gary Doug; Rouce, Rayne H.; Toner, Keri; Driscoll, Timothy A.; Katsanis, Emmanuel; Salzberg, Dana B.; Schiff, Deborah; De Oliveira, Satiro N.; Capitini, Christian M.; Pacenta, Holly L.; Pfeiffer, Thomas; Shah, Niketa C.; Huynh, Van; Skiles, Jodi L.; Fraint, Ellen; McNerney, Kevin O.; Quigg, Troy C.; Krueger, Joerg; Ligon, John A.; Fabrizio, Vanessa A.; Baggott, Christina; Laetsch, Theodore W.; Schultz, Liora M. Share Save
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Post-Transplantation Cyclophosphamide Is Associated with an Increase in Non-Cytomegalovirus Herpesvirus Infections in Patients with Acute Leukemia and Myelodysplastic Syndrome Singh, Anurag; Dandoy, Christopher E.; Chen, Min; Kim, Soyoung; Mulroney, Carolyn M.; Kharfan-Dabaja, Mohamed A.; Ganguly, Siddhartha; Maziarz, Richard T.; Kanakry, Christopher G.; Kanakry, Jennifer A.; Patel, Sagar S.; Hill, Joshua A.; De Oliveir, Satiro; Taplitz, Randy; Hematti, Peiman; Lazarus, Hillard M.; Abid, Muhammad Bilal; Goldsmith, Scott R.; Romee, Rizwan; Komanduri, Krishna, V; Badawy, Sherif M.; Friend, Brian D.; Beitinjaneh, Amer; Politikos, Ioannis; Perales, Miguel-Angel; Riches, Marcie Share Save
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency Kohn, D. B.; Booth, C.; Shaw, K. L.; Xu-Bayford, J.; Garabedian, E.; Trevisan, V.; Carbonaro-Sarracino, D. A.; Soni, K.; Terrazas, D.; Snell, K.; Ikeda, A.; Leon-Rico, D.; Moore, T. B.; Buckland, K. F.; Shah, A. J.; Gilmour, K. C.; De Oliveira, S.; Rivat, C.; Crooks, G. M.; Izotova, N.; Tse, J.; Adams, S.; Shupien, S.; Ricketts, H.; Davila, A.; Uzowuru, C.; Icreverzi, A.; Barman, P.; Fernandez, B. Campo; Hollis, R. P.; Coronel, M.; Yu, A.; Chun, K. M.; Casas, C. E.; Zhang, R.; Arduini, S.; Lynn, F.; Kudari, M.; Spezzi, A.; Zahn, M.; Heimke, R.; Labik, I.; Parrott, R.; Buckley, R. H.; Reeves, L.; Cornetta, K.; Sokolic, R.; Hershfield, M.; Schmidt, M.; Candotti, F.; Malech, H. L.; Thrasher, A. J.; Gaspar, H. B. Share Save
Acoustofluidic sonoporation for gene delivery to human hematopoietic stem and progenitor cells Belling, Jason N.; Heidenreich, Liv K.; Tian, Zhenhua; Mendoza, Alexandra M.; Chiou, Tzu-Ting; Gong, Yao; Chen, Natalie Y.; Young, Thomas D.; Wattanatorn, Natcha; Park, Jae Hyeon; Scarabelli, Leonardo; Chiang, Naihao; Takahashi, Jack; Young, Stephen G.; Stieg, Adam Z.; De Oliveira, Satiro; Huang, Tony Jun; Weiss, Paul S.; Jonas, Steven J. Share Save
Development of Hematopoietic Stem Cell-Engineered Invariant Natural Killer T Cell Therapy for Cancer Zhu, Yanni; Smith, Drake J.; Zhou, Yang; Li, Yan-Ruide; Yu, Jiaji; Lee, Derek; Wang, Yu-Chen; Di Biase, Stefano; Wang, Xi; Hardoy, Christian; Ku, Josh; Tsao, Tasha; Lin, Levina J.; Pham, Alexander T.; Moon, Heesung; McLaughlin, Jami; Cheng, Donghui; Hollis, Roger P.; Campo-Fernandez, Beatriz; Urbinati, Fabrizia; Wei, Liu; Pang, Larry; Rezek, Valerie; Berent-Maoz, Beata; Macabali, Mignonette H.; Gjertson, David; Wang, Xiaoyan; Galic, Zoran; Kitchen, Scott G.; An, Dong Sung; Hu-Lieskovan, Siwen; Kaplan-Lefko, Paula J.; De Oliveira, Satiro N.; Seet, Christopher S.; Larson, Sarah M.; Forman, Stephen J.; Heath, James R.; Zack, Jerome A.; Crooks, Gay M.; Radu, Caius G.; Ribas, Antoni; Kohn, Donald B.; Witte, Owen N.; Yang, Lili Share Save
Impact of cytogenetic abnormalities on outcomes of adult Philadelphia-negative acute lymphoblastic leukemia after allogeneic hematopoietic stem cell transplantation: a study by the Acute Leukemia Working Committee of the Center for International Blood and Marrow Transplant Research Lazaryan, Aleksandr; Dolan, Michelle; Zhang, Mei-Jie; Wang, Hai-Lin; Kharfan-Dabaja, Mohamed A.; Marks, David, I; Bejanyan, Nelli; Copelan, Edward; Majhail, Navneet S.; Waller, Edmund K.; Chao, Nelson; Prestidge, Tim; Nishihori, Taiga; Kebriaei, Partow; Inamoto, Yoshihiro; Hamilton, Betty; Hashmi, Shahrukh K.; Kamble, Rammurti T.; Bacher, Ulrike; Hildebrandt, Gerhard C.; Stiff, Patrick J.; McGuirk, Joseph; Aldoss, Ibrahim; Beitinjaneh, Amer M.; Muffly, Lori; Vij, Ravi; Olsson, Richard F.; Byrne, Michael; Schultz, Kirk R.; Aljurf, Mahmoud; Seftel, Matthew; Savoie, Mary Lynn; Savani, Bipin N.; Verdonck, Leo F.; Cairo, Mitchell S.; Hossain, Nasheed; Bhatt, Vijaya Raj; Frangoul, Haydar A.; Abdel-Azim, Hisham; Al Malki, Monzr; Munker, Reinhold; Rizzieri, David; Khera, Nandita; Nakamura, Ryotaro; Ringden, Olle; van der Poel, Marjolein; Murthy, Hemant S.; Liu, Hongtao; Mori, Shahram; De Oliveira, Satiro; Bolanos-Meade, Javier; Elsawy, Mahmoud; Barba, Pere; Nathan, Sunita; George, Biju; Pawarode, Attaphol; Grunwald, Michael; Agrawal, Vaibhav; Wang, Youjin; Assal, Amer; Caro, Paul Castillo; Kuwatsuka, Yachiyo; Seo, Sachiko; Ustun, Celalettin; Politikos, Ioannis; Lazarus, Hillard M.; Saber, Wael; Sandmaier, Brenda M.; De Lima, Marcos; Litzow, Mark; Bachanova, Veronika; Weisdorf, Daniel Share Save
Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome Kuo, Caroline Y.; Long, Joseph D.; Campo-Fernandez, Beatriz; de Oliveira, Satiro; Cooper, Aaron R.; Romero, Zulema; Hoban, Megan D.; Joglekar, Alok, V; Lill, Georgia R.; Kaufman, Michael L.; Fitz-Gibbon, Sorel; Wang, Xiaoyan; Hollis, Roger P.; Kohn, Donald B. Share Save
Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy Eichler, Florian; Duncan, Christine; Musolino, Patricia L.; Orchard, Paul J.; De Oliveira, Satiro; Thrasher, Adrian J.; Armant, Myriam; Dansereau, Colleen; Lund, Troy C.; Miller, Weston P.; Raymond, Gerald V.; Sankar, Raman; Shah, Ami J.; Sevin, Caroline; Gaspar, H. Bobby; Gissen, Paul; Amartino, Hernan; Bratkovic, Drago; Smith, Nicholas J. C.; Paker, Asif M.; Shamir, Esther; O'Meara, Tara; Davidson, David; Aubourg, Patrick; Williams, David A. Share Save
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency Shaw, Kit L.; Garabedian, Elizabeth; Mishra, Suparna; Barman, Provaboti; Davila, Alejandra; Carbonaro, Denise; Shupien, Sally; Silvin, Christopher; Geiger, Sabine; Nowicki, Barbara; Smogorzewska, E. Monika; Brown, Berkley; Wang, Xiaoyan; de Oliveira, Satiro; Choi, Yeong; Ikeda, Alan; Terrazas, Dayna; Fu, Pei-Yu; Yu, Allen; Fernandez, Beatriz Campo; Cooper, Aaron R.; Engel, Barbara; Podsakoff, Greg; Balamurugan, Arumugam; Anderson, Stacie; Muul, Linda; Jagadeesh, G. Jayashree; Kapoor, Neena; Tse, John; Moore, Theodore B.; Purdy, Ken; Rishi, Radha; Mohan, Kathey; Skoda-Smith, Suzanne; Buchbinder, David; Abraham, Roshini S.; Scharenberg, Andrew; Yang, Otto O.; Cornetta, Kenneth; Gjertson, David; Hershfield, Michael; Sokolic, Rob; Candotti, Fabio; Kohn, Donald B. Share Save
Pre-clinical development of gene modification of haematopoietic stem cells with chimeric antigen receptors for cancer immunotherapy Larson, Sarah M.; Truscott, Laurel C.; Chiou, Tzu-Ting; Patel, Amie; Kao, Roy; Tu, Andy; Tyagi, Tulika; Lu, Xiang; Elashoff, David; De Oliveira, Satiro N. Share Save
Phase II Clinical Trial of Gene Therapy for Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA-SCID) Using γ-Retroviral Vector Shaw, Kit L.; Garabedian, Elizabeth; Sokolic, Rob; Barman, Provaboti; Davila, Alejandra; Silvin, Christopher; de Oliveira, Satiro; Shah, Ami J.; Terrazas, Dayna; Carbonaro, Denise; Geiger, Sabine; Mishra, Suparna; Cooper, Aaron; Smogorzewska, Monika; Jagadeesh, Jayashree; Hershfield, Michael S.; Wayne, Alan; Crooks, Gay M.; Moore, Theodore; Candotti, Fabio; Kohn, Donald B. Share Save
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A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency Hacein-Bey-Abina, S.; Pai, S. -Y.; Gaspar, H. B.; Armant, M.; Berry, C. C.; Blanche, S.; Bleesing, J.; Blondeau, J.; de Boer, H.; Buckland, K. F.; Caccavelli, L.; Cros, G.; De Oliveira, S.; Fernandez, K. S.; Guo, D.; Harris, C. E.; Hopkins, G.; Lehmann, L. E.; Lim, A.; London, W. B.; van der Loo, J. C. M.; Malani, N.; Male, F.; Malik, P.; Marinovic, M. A.; McNicol, A. -M.; Moshous, D.; Neven, B.; Oleastro, M.; Picard, C.; Ritz, J.; Rivat, C.; Schambach, A.; Shaw, K. L.; Sherman, E. A.; Silberstein, L. E.; Six, E.; Touzot, F.; Tsytsykova, A.; Xu-Bayford, J.; Baum, C.; Bushman, F. D.; Fischer, A.; Kohn, D. B.; Filipovich, A. H.; Notarangelo, L. D.; Cavazzana, M.; Williams, D. A.; Thrasher, A. J. Share Save
Human Lymphoid Development in the Absence of Common γ-Chain Receptor Signaling Kohn, Lisa A.; Seet, Christopher S.; Scholes, Jessica; Codrea, Felicia; Chan, Rebecca; Zaidi-Merchant, Sania; Zhu, Yuhua; De Oliveira, Satiro; Kapoor, Neena; Shah, Ami; Abdel-Azim, Hisham; Kohn, Donald B.; Crooks, Gay M. Share Save
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