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Changes in sputum viscoelastic properties and airway inflammation in primary ciliary dyskinesia are comparable to cystic fibrosis on elexacaftor/tezacaftor/ivacaftor therapy Nussstein, Hannah; Urbantat, Ruth M.; Fentker, Kerstin; Loewe, Aditi; Duerr, Julia; Haji, Mohamed; Doellinger, Felix; Stahl, Mirjam; Graeber, Simon Y.; Gradzielski, Michael; Rohmel, Jobst; Mertins, Philipp; Schaupp, Laura; Mall, Marcus A. Share Save
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Reduction of systemic inflammation by elexacaftor/tezacaftor/ ivacaftor correlates with lung function improvement in cystic fibrosis Halle, Olga; Graeber, Simon Y.; Kontsendorn, Julia; Kessemeier, Claudia; Falke, Jan-Niklas; Schwabe, Jannik; Schuetz, Katharina; Pallenberg, Sophia T.; Dalferth, Rebecca; Grychtol, Ruth; Ringshausen, Felix C.; Stahl, Mirjam; Thee, Stephanie; Roehmel, Jobst F.; Syunyaeva, Zulfiya; Duerr, Julia; Chung, Jaehi; Hirtz, Stephanie; Uselmann, Tatjana; Kuehbandner, Iris; Rueckes-Nilges, Claudia; Bagheri-Pothoff, Azadeh; Barth, Sandra; Schaub, Bianca; Brinkmann, Folke; Weber, Stefanie; van Koningsbruggen-Rietschel, Silke; Abdo, Mustafa; Weckmann, Markus; Widder, Stefanie; Hansen, Gesine; Tuemmler, Burkhard; Sommerburg, Olaf; Naehrlich, Lutz; Mall, Marcus A.; Dittrich, Anna-Maria Share Save
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The established chest MRI score for cystic fibrosis can be applied to contrast agent-free matrix pencil decomposition functional MRI: a multireader analysis Steinke, Eva; Bauman, Grzegorz; Steffen, Ingo G.; Schobert, Isabel T.; Thee, Stephanie; Syunyaeva, Zulfiya; Roehmel, Jobst; Posch, Helena; Fahlenkamp, Ute L.; Scale, Carolin; Veldhoen, Simon; Bieri, Oliver; Wielpuetz, Mark O.; Mall, Marcus A.; Stahl, Mirjam; Doellinger, Felix Share Save
Long-Term Impact of Lumacaftor/Ivacaftor Treatment on Cystic Fibrosis Disease Progression in Children 2-5 Years of Age Homozygous for F508del-CFTR A Phase 2, Open-Label Clinical Trial Stahl, Mirjam; Roehmel, Jobst; Eichinger, Monika; Doellinger, Felix; Naehrlich, Lutz; Kopp, Matthias, V; Dittrich, Anna-Maria; Sommerburg, Olaf; Ray, Partha; Maniktala, Anita; Xu, Tu; Conner, Sarah; Joshi, Aniket; Mascia, Molly; Wielpueurotz, Mark O.; Mall, Marcus A. Share Save
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The international registry for primary ciliary dyskinesia reveals regional variation of genotypes and significant genotype-phenotype correlations Raidt, Johanna; Riepenhausen, Sarah; Amirav, Israel; Athanazio, Rodrigo A.; Aviram, Micha; Balinotti, Juan E.; Bar-On, Ophir; Bode, Sebastian Fn; Boon, Mieke; Borrelli, Melissa; Carr, Siobhan B.; Crowley, Suzanne; Dehlink, Eleonora; Diepenhorst, Sandra; Durdik, Peter; Dworniczak, Bernd; Emiralioglu, Nagehan; Erdem, Ela; Fonnesu, Rossella; Gracci, Serena; Grosse-Onnebrink, Joerg; Gwozdziewicz, Karolina; Haarman, Eric G.; Hansen, Christine R.; Hogg, Claire; Holgersen, Mathias G.; Julian, Varghese; Kerem, Eitan; Korner, Robert W.; Kotz, Karsten; Kouis, Panayiotis; Loebinger, Michael R.; Lorent, Natalie; Lucas, Jane S.; Maj, Debora; Mall, Marcus A.; Marthin, June K.; Martinu, Vendula; Mazurek, Henryk; Mitchison, Hannah M.; Noethe-Menchen, Tabea; Olbrich, Heike; Ozcelik, Ugur; Pennekamp, Petra; Pifferi, Massimo; Pogorzelski, Andrzej; Ringshausen, Felix C.; Roehmel, Jobst F.; Rovira-Amigo, Sandra; Rumman, Nisreen; Schlegtendal, Anne; Shoemark, Amelia; Kennelly, Synne Sperstad; Staar, Ben; Sutharsan, Sivagurunathan; Thomas, Simon; Ullmann, Nicola; Von Hardenberg, Sandra; Walker, Woolf; Wetzke, Martin; Witt, Michal; Yiallouros, Panayiotis; Zietkiewicz, Ewa; Nielsen, Kim G.; Omran, Heymut Share Save
Elexacaftor/tezacaftor/ivacaftor improves nasal nitric oxide in patients with cystic fibrosis Pioch, Charlotte O.; Ziegahn, Niklas; Allomba, Christine; Busack, Leonie M.; Schnorr, Alexandra N.; Tosolini, Apolline; Fuhlrott, Bent R.; Zagkla, Styliani; Othmer, Till; Syunyaeva, Zulfiya; Graeber, Simon Y.; Yoosefi, Mehrak; Thee, Stephanie; Steinke, Eva; Roehmel, Jobst; Mall, Marcus A.; Stahl, Mirjam Share Save
Contrast agent-free functional magnetic resonance imaging with matrix pencil decomposition to quantify abnormalities in lung perfusion and ventilation in patients with cystic fibrosis Doellinger, Felix; Bauman, Grzegorz; Roehmel, Jobst; Stahl, Mirjam; Posch, Helena; Steffen, Ingo G.; Pusterla, Orso; Bieri, Oliver; Wielpuetz, Mark O.; Mall, Marcus A. Share Save
Pharmacological Improvement of Cystic Fibrosis Transmembrane Conductance Regulator Function Rescues Airway Epithelial Homeostasis and Host Defense in Children with Cystic Fibrosis Loske, Jennifer; Voeller, Mirjam; Lukassen, Soeren; Stahl, Mirjam; Thuermann, Loreen; Seegebarth, Anke; Roehmel, Jobst; Wisniewski, Sebastian; Messingschlager, Marey; Lorenz, Stephan; Klages, Sven; Eils, Roland; Lehmann, Irina; Mall, Marcus A.; Graeber, Simon Y.; Trump, Saskia Share Save
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Magnetic Resonance Imaging of Pulmonary and Paranasal Sinus Abnormalities in Children with Primary Ciliary Dyskinesia Compared to Children with Cystic Fibrosis Wucherpfennig, Lena; Wuennemann, Felix; Eichinger, Monika; Schmitt, Niclas; Seitz, Angelika; Baumann, Ingo; Roehmel, Jobst F.; Stahl, Mirjam; Haemmerling, Susanne; Chung, Jaehi; Schenk, Jens-Peter; Alrajab, Abdulsattar; Kauczor, Hans-Ulrich; Mall, Marcus A.; Wielpuetz, Mark O.; Sommerburg, Olaf Share Save
Association between upper and lower respiratory disease in primary ciliary dyskinesia Lam, Yin Ting; Papon, Jean-Francois; Alexandru, Mihaela; Anagiotos, Andreas; Armengot, Miguel; Boon, Mieke; Burgess, Andrea; Calmes, Doriane; Crowley, Suzanne; Dheyauldeen, Sinan Ahmed D.; Emiralioglu, Nagehan; Eralp, Ela Erdem; Van Gogh, Christine; Haarman, Eric G.; Harris, Amanda; Hayn, Isolde; Hool, Sara-Lynn; Karadag, Bulent; Kempeneers, Celine; Kim, Sookyung; Latzin, Philipp; Lorent, Natalie; Ozcelik, Ugur; Reula, Ana; Roehmel, Jobst; Yiallouros, Panayiotis; Goutaki, Myrofora Share Save
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Immune-epithelial cell cross-talk enhances antiviral responsiveness to SARS-CoV-2 in children Magalhaes, Vladimir G.; Lukassen, Soeren; Drechsler, Maike; Loske, Jennifer; Burkart, Sandy S.; Wuest, Sandra; Jacobsen, Eva-Maria; Roehmel, Jobst; Mall, Marcus A.; Debatin, Klaus-Michael; Eils, Roland; Autenrieth, Stella; Janda, Ales; Lehmann, Irina; Binder, Marco Share Save
Effects of Lumacaftor/Ivacaftor on Cystic Fibrosis Disease Progression in Children 2 through 5 Years of Age Homozygous for F508del-CFTR: A Phase 2 Placebo-controlled Clinical Trial Stahl, Mirjam; Roehmel, Jobst; Eichinger, Monika; Doellinger, Felix; Naehrlich, Lutz; Kopp, Matthias V.; Dittrich, Anna-Maria; Lee, Christopher; Sommerburg, Olaf; Tian, Simon; Xu, Tu; Wu, Pan; Joshi, Aniket; Ray, Partha; Duncan, Margaret E.; Wielputz, Mark O.; Mall, Marcus A. Share Save