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Interim results from a first in human phase 1 clinical trial of in utero enzyme replacement therapy for lysosomal disorders Mackenzie, Tippi C.; Lianoglou, Billie; Canepa, Emma; Herzeg, Akos; Borgas, Beltran; Cohen, Jennifer L.; Bali, Deeksha; Young, Sarah; Gonzalez-Vele, Juan; Munar, Dane; Gelb, Michael H.; Herbs, Zackary (Ari) M.; Chakraborty, Pranesh; Kishnani, Priya; Harmatz, Paul Share Save
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Synthesis and Detection of BODIPY-, Biotin-, and 19F- Labeled Single-Entity Dendritic Heparan Sulfate Mimetics Spijkers-Shaw, Sam; Devlin, Rory; Shields, Nicholas J.; Feng, Xiang; Peck, Tessa; Lenihan-Geels, Georgia; Davis, Connor; Young, Sarah L.; La Flamme, Anne C.; Zubkova, Olga V. Share Save
Measurement of glycosaminoglycans in the amniotic fluid of fetuses with mucopolysaccharidoses treated in a phase I clinical trial by in utero enzyme replacement therapy Young, Sarah; Lianoglou, Billie R.; Herzeg, Akos; Borges, Beltran; Chakraborty, Pranesh; Bali, Deeksha; Gonzalez, Juan M.; Canepa, Emma; Kishnani, Priya; Cohen, Jennifer L.; Harmatz, Paul; MacKenzie, Tippi C. Share Save
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In utero enzyme replacement therapy in a fetus with infantile-onset Pompe disease Cohen, Jennifer L.; Chakraborty, Pranesh; Fung-Kee-Fung, Karen; Schwa, Marisa E.; Bali, Deeksha; Young, Sarah; Gelb, Michael H.; Khaledi, Hamid; McIntosh, Nathan; DiBattista, Alicia; Kelly, Deidre; Smallshaw, Stacey; Lianoglou, Billie; Harmatz, Paul; Kishnani, Priya S.; MacKenzie, Tippi C. Share Save
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Oncolytic virus-derived type I interferon restricts CAR T cell therapy Evgin, Laura; Huff, Amanda L.; Wongthida, Phonphimon; Thompson, Jill; Kottke, Tim; Tonne, Jason; Schuelke, Matthew; Ayasoufi, Katayoun; Driscoll, Christopher B.; Shim, Kevin G.; Reynolds, Pierce; Monie, Dileep D.; Johnson, Aaron J.; Coffey, Matt; Young, Sarah L.; Archer, Gary; Sampson, John; Pulido, Jose; Perez, Luis Sanchez; Vile, Richard Share Save
The Delta-Subunit Selective GABAA Receptor Modulator, DS2, Improves Stroke Recovery via an Anti-inflammatory Mechanism Neumann, Silke; Boothman-Burrell, Lily; Gowing, Emma; Jacobsen, Thomas A.; Ahring, Philip K.; Young, Sarah L.; Sandager-Nielsen, Karin; Clarkson, Andrew Share Save
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