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Tppp3 is a novel molecule for retinal ganglion cell identification and optic nerve regeneration Rao, Mishal; Luo, Ziming; Liu, Chia-Chun; Chen, Chi-Yu; Wang, Shining; Nahmou, Michael; Tanasa, Bogdan; Virmani, Aman; Byrne, Leah; Goldberg, Jeffrey L.; Sahel, Jose-Alain; Chang, Kun-Che Share Save
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Modeling PRPF31 retinitis pigmentosa using retinal pigment epithelium and organoids combined with gene augmentation rescue Rodrigues, Amelie; Slembrouck-Brec, Amelie; Nanteau, Celine; Terray, Angelique; Tymoshenko, Yelyzaveta; Zagar, Yvrick; Reichman, Sacha; Xi, Zhouhuan; Sahel, Jose-Alain; Fouquet, Stephane; Orieux, Gael; Nandrot, Emeline F.; Byrne, Leah C.; Audo, Isabelle; Roger, Jerome E.; Goureau, Olivier Share Save
Machine learning sequence prioritization for cell type-specific enhancer design Lawler, Alyssa J.; Ramamurthy, Easwaran; Brown, Ashley R.; Shin, Naomi; Kim, Yeonju; Toong, Noelle; Kaplow, Irene M.; Wirthlin, Morgan; Zhang, Xiaoyu; Phan, BaDoi N.; Fox, Grant A.; Wade, Kirsten; He, Jing; Ozturk, Bilge Esin; Byrne, Leah C.; Stauffer, William R.; Fish, Kenneth N.; Pfenning, Andreas R. Share Save
Targeting ON-bipolar cells by AAV gene therapy stably reverses LRIT3-congenital stationary night blindness Miyadera, Keiko; Santana, Evelyn; Roszak, Karolina; Iffrig, Sommer; Visel, Meike; Iwabe, Simone; Boyd, Ryan F.; Bartoe, Joshua T.; Sato, Yu; Gray, Alexa; Ripolles-Garcia, Ana; Dufour, Valerie L.; Byrne, Leah C.; Flannery, John G.; Beltran, William A.; Aguirre, Gustavo D. Share Save
Transcriptional and anatomical diversity of medium spiny neurons in the primate striatum He, Jing; Kleyman, Michael; Chen, Jianjiao; Alikaya, Aydin; Rothenhoefer, Kathryn M.; Ozturk, Bilge Esin; Wirthlin, Morgan; Bostan, Andreea C.; Fish, Kenneth; Byrne, Leah C.; Pfenning, Andreas R.; Stauffer, William R. Share Save
scAAVengr, a transcriptome-based pipeline for quantitative ranking of engineered AAVs with single-cell resolution Ozturk, Bilge E.; Johnson, Molly E.; Kleyman, Michael; Turunc, Serhan; He, Jing; Jabalameli, Sara; Xi, Zhouhuan; Visel, Meike; Dufour, Valerie L.; Iwabe, Simone; Marinho, Luis Felipe L. Pompeo; Aguirre, Gustavo D.; Sahel, Jose-Alain; Schaffer, David, V; Pfenning, Andreas R.; Flannery, John G.; Beltran, William A.; Stauffer, William R.; Byrne, Leah C. Share Save
Parallel functional testing identifies enhancers active in early postnatal mouse brain Lambert, Jason T.; Su-Feher, Linda; Cichewicz, Karol; Warren, Tracy L.; Zdilar, Iva; Wang, Yurong; Lim, Kenneth J.; Haigh, Jessica L.; Morse, Sarah J.; Canales, Cesar P.; Stradleigh, Tyler W.; Palacios, Erika Castillo; Haghani, Viktoria; Moss, Spencer D.; Parolini, Hannah; Quintero, Diana; Shrestha, Diwash; Vogt, Daniel; Byrne, Leah C.; Nord, Alex S. Share Save
Pharmacological clearance of misfolded rhodopsin for the treatment ofRHO-associated retinitis pigmentosa Liu, Xujie; Feng, Bing; Vats, Abhishek; Tang, Hong; Seibel, William; Swaroop, Manju; Tawa, Gregory; Zheng, Wei; Byrne, Leah; Schurdak, Mark; Chen, Yuanyuan Share Save
In vivo directed evolution of adeno-associated virus in the primate retina Byrne, Leah C.; Day, Timothy P.; Visel, Meike; Strazzeri, Jennifer A.; Fortuny, Cecile; Dalkara, Deniz; Merigan, William H.; Schaffer, David, V; Flannery, John G. Share Save
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