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SaveFlavones provide resistance to DUX4-induced toxicity via an mTor-independent mechanism
Cohen, Justin; Huang, Shushu; Koczwara, Katherine E.; Woods, Kristen T.; Ho, Vincent; Woodman, Keryn G.; Arbiser, Jack L.; Daman, Katelyn; Lek, Monkol; Emerson Jr, Charles P.; Desimone, Alec M.
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SaveDeath after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy
Lek, Angela; Wong, Brenda; Keeler, Allison; Blackwood, Meghan; Ma, Kaiyue; Huang, Shushu; Sylvia, Katelyn; Batista, A. Rita; Artinian, Rebecca; Kokoski, Danielle; Parajuli, Shestruma; Putra, Juan; Carreon, C. Katte; Lidov, Hart; Woodman, Keryn; Pajusalu, Sander; Spinazzola, Janelle M.; Gallagher, Thomas; Larovere, Joan; Balderson, Diane; Black, Lauren; Sutton, Keith; Horgan, Richard; Lek, Monkol; Flotte, Terence
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SaveApplying genome-wide CRISPR-Cas9 screens for therapeutic discovery in facioscapulohumeral muscular dystrophy
Lek, Angela; Zhang, Yuanfan; Woodman, Keryn G.; Huang, Shushu; DeSimone, Alec M.; Cohen, Justin; Ho, Vincent; Conner, James; Mead, Lillian; Kodani, Andrew; Pakula, Anna; Sanjana, Neville; King, Oliver D.; Jones, Peter L.; Wagner, Kathryn R.; Lek, Monkol; Kunkel, Louis M.
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SaveExpression profiling in exercised mdx suggests a role for extracellular proteins in the dystrophic muscle immune response
Coles, Chantal A.; Gordon, Lavinia; Hunt, Liam C.; Webster, Tracie; Piers, Adam T.; Kintakas, Christopher; Woodman, Keryn; Touslon, Su L.; Smythe, Gayle M.; White, Jason D.; Lamande, Shireen R.
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