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Long-term efficacy and safety in the 60-month, Phase 3 ILLUMINATE-B trial of lumasiran in infants and young children with primary hyperoxaluria type 1 Frishberg, Yaacov; Hayes, Wesley; Ben-Shalom, Efrat; Shasha-Lavsky, Hadas; Sas, David; Michael, Mini; Sellier-Leclerc, Anne-Laure; Hogan, Julien; Willey, Richard; Gansner, John; Kaspar, Cristin; Magen, Daniella Share Save
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Lumasiran for Advanced Primary Hyperoxaluria Type 1: Phase 3 ILLUMINATE-C Trial Michael, Mini; Groothoff, Jaap W.; Shasha-Lavsky, Hadas; Lieske, John C.; Frishberg, Yaacov; Simkova, Eva; Sellier-Leclerc, Anne-Laure; Devresse, Arnaud; Guebre-Egziabher, Fitsum; Bakkaloglu, Sevcan A.; Mourani, Chebl; Saqan, Rola; Singer, Richard; Willey, Richard; Habtemariam, Bahru; Gansner, John M.; Bhan, Ishir; McGregor, Tracy; Magen, Daniella Share Save
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Phase 3 trial of lumasiran for primary hyperoxaluria type 1: A new RNAi therapeutic in infants and young children Sas, David J.; Magen, Daniella; Hayes, Wesley; Shasha-Lavsky, Hadas; Michael, Mini; Schulte, Indra; Sellier-Leclerc, Anne-Laure; Lu, Jiandong; Seddighzadeh, Ali; Habtemariam, Bahru; McGregor, Tracy L.; Fujita, Kenji P.; Frishberg, Yaacov Share Save
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Developing Consensus-Based Outcome Domains for Trials in Children and Adolescents with CKD: An International Delphi Survey Logeman, Charlotte; Guha, Chandana; Howell, Martin; Hanson, Camilla S.; Craig, Jonathan C.; Samuel, Susan; Zappitelli, Michael; Matsuda-Abedini, Mina; Dart, Allison; Furth, Susan; Eddy, Allison; Groothoff, Jaap; Yap, Hui-Kim; Bockenhauer, Detlef; Sinha, Aditi; Alexander, Stephen, I; Goldstein, Stuart L.; Gipson, Debbie S.; Michael, Mini; Walker, Amanda; Kausman, Joshua; Gaillard, Segolene; Bacchetta, Justine; Rheault, Michelle N.; Warady, Bradley A.; Neu, Alicia; Christian, Martin; McTaggart, Steven; Liu, Isaac; Teo, Sharon; Sautenet, Benedicte; Gutman, Talia; Carter, Simon; Teixeira-Pinto, Armando; Tong, Allison Share Save
Renal Survival in Children with Glomerulonephritis with Crescents: A Pediatric Nephrology Research Consortium Cohort Study Maliakkal, Joseph G.; Hicks, M. John; Michael, Mini; Selewski, David T.; Twombley, Katherine; Rheault, Michelle N.; Seamon, Meredith; Misurac, Jason M.; Tran, Cheryl L.; Reyes, Loretta; Flynn, Joseph T.; Onder, Ali M.; Constantinescu, Alexandru R.; Singh, Vaishali; Pan, Cynthia; Omoloja, Abiodun; Wu, Qiang; Smoyer, William E.; Hidalgo, Guillermo; Wenderfer, Scott E. Share Save
Identifying Important Outcomes for Young People With CKD and Their Caregivers: A Nominal Group Technique Study Hanson, Camilla S.; Gutman, Talia; Craig, Jonathan C.; Bernays, Sarah; Raman, Gayathri; Zhang, Yifan; James, Laura J.; Ralph, Angelique F.; Ju, Angela; Manera, Karine E.; Teixeira-Pinto, Armando; Viecelli, Andrea K.; Alexander, Stephen, I; Blydt-Hansen, Tom D.; Dionne, Janis; McTaggart, Steven; Michael, Mini; Walker, Amanda; Carter, Simon; Wenderfer, Scott E.; Winkelmayer, Wolfgang C.; Bockenhauer, Detlef; Dart, Allison; Eddy, Allison A.; Furth, Susan L.; Gipson, Debbie S.; Goldstein, Stuart L.; Groothoff, Jaap; Samuel, Susan; Sinha, Aditi; Webb, Nicholas J. A.; Yap, Hui-Kim; Zappitelli, Michael; Currier, Helen; Tong, Allison Share Save
Child and Parental Perspectives on Communication and Decision Making in Pediatric CKD: A Focus Group Study Gutman, Talia; Hanson, Camilla S.; Bernays, Sarah; Craig, Jonathan C.; Sinha, Aditi; Dart, Allison; Eddy, Allison A.; Gipson, Debbie S.; Bockenhauer, Detlef; Yap, Hui-Kim; Groothoff, Jaap; Zappitelli, Michael; Webb, Nicholas J. A.; Alexander, Stephen, I; Goldstein, Stuart L.; Furth, Susan; Samuel, Susan; Blydt-Hansen, Tom; Dionne, Janis; Michael, Mini; Wenderfer, Scott E.; Winkelmayer, Wolfgang C.; Currier, Helen; McTaggart, Steven; Walker, Amanda; Ralph, Angelique F.; Ju, Angela; James, Laura J.; Carter, Simon; Tong, Allison Share Save
Deficiency of complement factor H-related proteins and autoantibody-positive hemolytic uremic syndrome in an infant with combined partial deficiencies and autoantibodies to complement factor H and ADAMTS13 (vol 11, sfy010, 2018) Michael, Mini; Turner, Nancy; Elenberg, Ewa; Shaffer, Linda G.; Teruya, Jun; Arar, Mazen; Hui, Shiu-Ki; Smith, Richard J.; Moake, Joel Share Save
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Whole-exome sequencing in the molecular diagnosis of individuals with congenital anomalies of the kidney and urinary tract and identification of a new causative gene Bekheirnia, Mir Reza; Bekheirnia, Nasim; Bainbridge, Matthew N.; Gu, Shen; Akdemir, Zeynep Hande Coban; Gambin, Tomek; Janzen, Nicolette K.; Jhangiani, Shalini N.; Muzny, Donna M.; Michael, Mini; Brewer, Eileen D.; Elenberg, Ewa; Kale, Arundhati S.; Riley, Alyssa A.; Swartz, Sarah J.; Scott, Daryl A.; Yang, Yaping; Srivaths, Poyyapakkam R.; Wenderfer, Scott E.; Bodurtha, Joann; Applegate, Carolyn D.; Velinov, Milen; Myers, Angela; Borovik, Lior; Craigen, William J.; Hanchard, Neil A.; Rosenfeld, Jill A.; Lewis, Richard Alan; Gonzales, Edmond T.; Gibbs, Richard A.; Belmont, John W.; Roth, David R.; Eng, Christine; Braun, Michael C.; Lupski, James R.; Lamb, Dolores J. Share Save
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