Not logged in International neuroblastoma risk group consortium: a model of networking for rare cancers Susan L Cohn, MD; Wendy B London, PhD; Gudrun Schleiermacher, MD, PhD; Lucas Moreno, MD, PhD; Inge M Ambros, PhD; Peter F Ambros, PhD; Rochelle Bagatell, MD; Maja Beck Popovic, MD; Klaus Hermann Beiske, MD, PhD; Frank Berthold, MD; Suzi Birz, MScMI; Hervé J Brisse, MD; Garrett M Brodeur, MD; Penelope R Brock, MD; Susan Burchill, PhD; Angelika Eggert, MD; Sara M Federico, MD; Matthias Fischer, PhD; Brian T Furner, MS; Barbara Hero, MD; David Machin, PhD; Takehiko Kamijo, MD; Katherine K Matthay, MD; Akira Nakagawara, MD, PhD; Arlene Naranjo, PhD; Ulrike Pötschger, PhD; Dominique Valteau-Couanet, MD; Michael T Watkins, PhD; Meredith S Irwin, MD; Samuel L Volchenboum, MD, PhD; Julie R Park, MD; Andrew D J Pearson, MD; null Share Save
Update on Surveillance for Wilms Tumor and Hepatoblastoma in Beckwith-Wiedemann Syndrome and Other Predisposition Syndromes Kalish, Jennifer M.; Becktell, Kerri D.; Bougeard, Gaelle; Brodeur, Garrett M.; Diller, Lisa R.; Doria, Andrea S.; Hansford, Jordan R.; Klein, Steven D.; Kohlmann, Wendy K.; Kratz, Christian P.; Macfarland, Suzanne P.; Pajtler, Kristian W.; Rednam, Surya P.; Schienda, Jaclyn; States, Lisa J.; Villani, Anita; Weksberg, Rosanna; Zelley, Kristin; Tomlinson, Gail E.; Brzezinski, Jack J. Share Save
Establishment of the consortium for childhood cancer predisposition and the childhood cancer predisposition study Porter, Christopher C.; Brodeur, Garrett M.; Diller, Lisa; Edgerton, Chloe; Kamihara, Junne; Kohlmann, Wendy; MacFarland, Suzanne P.; Maese, Luke; Malkin, David; Nichols, Kim E.; Perrino, Melissa R.; Plon, Sharon E.; Rednam, Surya; Villani, Anita Share Save
Identification of TP53 germline variants in pediatric patients undergoing tumor testing: strategy and prevalence Luo, Minjie; Wong, Derek; Zelley, Kristin; Wu, Jinhua; Schubert, Jeffery; Denenberg, Elizabeth H.; Fanning, Elizabeth A.; Chen, Jiani; Gallo, Daniel; Golenberg, Netta; Patel, Maha; Conlin, Laura K.; Maxwell, Kara N.; Wertheim, Gerald B.; Surrey, Lea F.; Zhong, Yiming; Brodeur, Garrett M.; MacFarland, Suzanne P.; Li, Marilyn M. Share Save
Establishment of the Consortium for Childhood Cancer Predisposition and the Childhood Cancer Predisposition Study Villani, Anita; Brodeur, Garrett M.; Diller, Lisa R.; Edgerton, Chloe; Kamihara, Junne; Kohlmann, Wendy; MacFarland, Suzanne P.; Maese, Luke; Malkin, David; Nichols, Kim E.; Perrino, Melissa R.; Plon, Sharon E.; Rednam, Surya; Porter, Christopher C. Share Save
Adult-Onset Cancer Predisposition Syndromes in Children and Adolescents-To Test or not to Test? Kratz, Christian P.; Lupo, Philip J.; Zelley, Kristin; Schienda, Jaclyn; Nichols, Kim E.; Stewart, Douglas R.; Malkin, David; Brodeur, Garrett M.; Maxwell, Kara; Plon, Sharon E.; Walsh, Michael F. Share Save
Genomic profiling of pediatric hematologic malignancies and diagnosis of cancer predisposition syndromes: tumor- only versus paired tumor-normal sequencing Newman, Haley; Clark, Mary Egan; Wong, Derek; Wu, Jinhua; Brodeur, Garrett M.; Hunger, Stephen P.; Tasian, Sarah K.; Olson, Timothy; Warren, Julia T.; Teachey, David T.; Bona, Kira; Schubert, Jeffrey; Golenberg, Netta; Patel, Maha; Denenberg, Elizabeth H.; Fanning, Elizabeth A.; Chen, Jiani; Luke, Tamara; Charles, Sarah; Gallo, Daniel; Cao, Kajia; Fu, Weixuan; Fan, Zhiqian; Surrey, Lea F.; Wertheim, Gerald; Luo, Minjie; MacFarland, Suzanne P.; Li, Marilyn M.; Zhong, Yiming Share Save
B-cell acute lymphoblastic leukemia and juvenile xanthogranuloma in a patient with ETV6 thrombocytopenia and leukemia predisposition syndrome: novel clinical presentation and perspective Newman, Haley; MacFarland, Suzanne P.; Brodeur, Garrett M.; Olson, Timothy; Bhojwani, Deepa; Stokke, Jamie; Kovach, Alexandra E.; Clark, Mary Egan; Luo, Minjie; Li, Marilyn; Shah, Amish; Hunger, Stephen P. Share Save
DICER1 RNase IIIb domain mutations trigger widespread miRNA dysregulation and MAPK activation in pediatric thyroid cancer Ricarte-Filho, Julio C.; Casado-Medrano, Victoria; Reichenberger, Erin; Spangler, Zachary; Scheerer, Michele; Isaza, Amber; Baran, Julia; Patel, Tasleema; MacFarland, Suzanne P.; Brodeur, Garrett M.; Stewart, Douglas R.; Baloch, Zubair; Bauer, Andrew J.; Wasserman, Jonathan D.; Franco, Aime T. Share Save
Structural Optimization and Enhanced Prodrug-Mediated Delivery Overcomes Camptothecin Resistance in High-Risk Solid Tumors Nguyen, Ferro; Guan, Peng; Guerrero, David T.; Kona, Venkatadri; Naraparaju, Koumudi; Perry, Lauren M.; Soberman, Danielle; Pressly, Benjamin B.; Alferiev, Ivan S.; Chorny, Michael; Brodeur, Garrett M. Share Save
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RET receptor expression and interaction with TRK receptors in neuroblastomas Tetri, Laura H.; Kolla, Venkatadri; Golden, Rebecca L.; Iyer, Radhika; Croucher, Jamie L.; Choi, Jee-Hye; Macfarland, Suzanne P.; Naraparaju, Koumudi; Guan, Peng; Nguyen, Ferro; Gaonkar, Krutika S.; Raman, Pichai; Brodeur, Garrett M. Share Save
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Earlier Colorectal Cancer Screening May Be Necessary In Patients With Li-Fraumeni Syndrome MacFarland, Suzanne P.; Zelley, Kristin; Long, Jessica M.; McKenna, Danielle; Mamula, Petar; Domchek, Susan M.; Nathanson, Katherine L.; Brodeur, Garrett M.; Rustgi, Anil K.; Katona, Bryson W.; Maxwell, Kara N. Share Save
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Nanocarriers with a camptothecin-mitocan co-drug suppress tumor growth and extend survival in models of chemosensitive and chemoresistant neuroblastoma Guerrero, David; Alferiev, Ivan S.; Nguyen, Ferro; Guan, Peng; Kolla, Venkatadri; Soberman, Danielle; Fishbein, Ilia; Levy, Robert J.; Brodeur, Garrett M.; Chorny, Michael Share Save
STARTRK-NG: A phase 1/1b study of entrectinib in children and adolescents with advanced solid tumors and primary CNS tumors, with or without TRK, ROS1, or ALK fusions Desai, Ami V.; Brodeur, Garrett M.; Foster, Jennifer; Shusterman, Suzanne; Sabnis, Amit J.; Macy, Magaret; Wetmore, Cynthia; Basu, Ellen; Hornby, Zachary; Esquibel, Vanessa; Maneval, Edna Chow; Multani, Pratik S.; Fox, Elizabeth Share Save
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Entrectinib is a potent inhibitor of Trk-driven neuroblastomas in a xenograft mouse model Iyer, Radhika; Wehrmann, Lea; Golden, Rebecca L.; Naraparaju, Koumudi; Croucher, Jamie L.; MacFarland, Suzanne P.; Guan, Peng; Kolla, Venkatadri; Wei, Ge; Cam, Nicholas; Li, Gang; Hornby, Zachary; Brodeur, Garrett M. Share Save