Not logged in Ocular Safety and Toxicology of Subretinal Gene Therapy With rAAV.hPDE6A in Nonhuman Primates Seitz, Immanuel P.; Wozar, Fabian; Ochakovski, Guy Alex; Reichel, Felix F.; Korte, Sven; Korbmacher, Birgit; Wilhelm, Barbara; Suesskind, Daniela; Bartz-Schmidt, Karl-Ulrich; Fischer, M. Dominik; Peters, Tobias Share Save
Safety of Human USH1C Transgene Expression Following Subretinal Injection in Wild-Type Pigs Kiraly, Peter; Klein, Joshua; Seitz, Immanuel P.; Reichel, Felix F.; Peters, Tobias; Ardan, Taras; Juhasova, Jana; Juhas, Stefan; Ellederova, Zdenka; Nemesh, Yaroslav; Nyshchuk, Ruslan; Klymiuk, Nikolai; Nagel-Wolfrum, Kerstin; Winslow, Ashley R.; Wolfrum, Uwe; Motlik, Jan; Fischer, M. Dominik Share Save
Optimizing Subretinal Bleb Formation for Visual Streak Involvement in a Porcine Model for Retinal Gene Therapy Seitz, Immanuel P.; Peters, Tobias; Reichel, Felix; Baehr, Andrea; Auch, Hanna; Motlik, Jan; Ardan, Taras; Juhasova, Jana; Nemesh, Yaroslav; Juhas, Stefan; Klymiuk, Nikolai; Fischer, Manuel Dominik Share Save
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Development of retinal atrophy after subretinal gene therapy with voretigene neparvovec Reichel, Felix Friedrich; Seitz, Immanuel; Wozar, Fabian; Dimopoulos, Spyridon; Jung, Ronja; Kempf, Melanie; Kohl, Susanne; Kortum, Friederike Charlotte; Ott, Saskia; Pohl, Lisa; Stingl, Krunoslav; Bartz-Schmidt, Karl Ulrich; Stingl, Katarina; Fischer, M. Dominik Share Save
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Three-year results of phase I retinal gene therapy trial for CNGA3-mutated achromatopsia: results of a non randomised controlled trial Reichel, Felix Friedrich; Michalakis, Stylianos; Wilhelm, Barbara; Zobor, Ditta; Muehlfriedel, Regine; Kohl, Susanne; Weisschuh, Nicole; Sothilingam, Vithiyanjali; Kuehlewein, Laura; Kahle, Nadine; Seitz, Immanuel; Paquet-Durand, Francois; Tsang, Stephen H.; Martus, Peter; Peters, Tobias; Seeliger, Mathias; Bartz-Schmidt, Karl Ulrich; Ueffing, Marius; Zrenner, Eberhard; Biel, Martin; Wissinger, Bernd; Fischer, Dominik Share Save
Humoral Immune Response After Intravitreal But Not After Subretinal AAV8 in Primates and Patients Reichel, Felix F.; Peters, Tobias; Wilhelm, Barbara; Biel, Martin; Ueffing, Marius; Wissinger, Bernd; Bartz-Schmidt, Karl U.; Klein, Reinhild; Michalakis, Stylianos; Fischer, M. Dominik Share Save
AAV8 Can Induce Innate and Adaptive Immune Response in the Primate Eye Reichel, Felix F.; Dauletbekov, Daniyar L.; Klein, Reinhild; Peters, Tobias; Ochakoyski, G. Alex; Seitz, Immanuel P.; Wilhelm, Barbara; Ueffing, Marius; Biel, Martin; Wissinger, Bernd; Michalakis, Stylianos; Bartz-Schmidt, Karl Ulrich; Fischer, M. Dominik Share Save
Superior Retinal Gene Transfer and Biodistribution Profile of Subretinal Versus Intravitreal Delivery of AAV8 in Nonhuman Primates Seitz, Immanuel P.; Michalakis, Stylianos; Wilhelm, Barbara; Reichel, Felix E.; Ochakovski, G. Alex; Zrenner, Eberhart; Ueffing, Marius; Biel, Martin; Wissinger, Bernd; Bartz-Schmidt, Karl U.; Peters, Tobias; Fischer, M. Dominik Share Save