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Quantitative relationship between tominersen concentrations in cerebrospinal fluid and biomarker changes in Huntington's disease patients Yamamoto, Yumi; Silber Baumann, Hanna E.; Bjornsson, Marcus; Grimsey, Paul; Hawellek, David J.; Anderson, Karen; Leavitt, Blair R.; Landwehrmeyer, Bernhard G.; Tabrizi, Sarah; Mccolgan, Peter; Wild, Edward J.; Sanwald Ducray, Patricia Share Save
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Huntington's disease phenocopy syndromes revisited: a clinical comparison and next-generation sequencing exploration Koriath, Carolin Anna Maria; Guntoro, Fernando; Norsworthy, Penelope; Dolzhenko, Egor; Eberle, Michael; Moss, Davina J. Hensman; Flower, Michael; Hummerich, Holger; Rosser, Anne Elizabeth; Tabrizi, Sarah J.; Mead, Simon; Wild, Edward J. Share Save
Increased frequency of repeat expansion mutations across different populations Ibanez, Kristina; Jadhav, Bharati; Zanovello, Matteo; Gagliardi, Delia; Clarkson, Christopher; Facchini, Stefano; Garg, Paras; Martin-Trujillo, Alejandro; Gies, Scott J.; Deforie, Valentina Galassi; Dalmia, Anupriya; Moss, Davina J. Hensman; Vandrovcova, Jana; Rocca, Clarissa; Moutsianas, Loukas; Marini-Bettolo, Chiara; Walker, Helen; Turner, Chris; Shoai, Maryam; Long, Jeffrey D.; Fratta, Pietro; Langbehn, Douglas R.; Tabrizi, Sarah J.; Caulfield, Mark J.; Cortese, Andrea; Escott-Price, Valentina; Hardy, John; Houlden, Henry; Sharp, Andrew J.; Tucci, Arianna Share Save
Long-Term Health Outcomes of Huntington Disease and the Impact of Future Disease-Modifying Treatments-A Decision-Modeling Analysis Guzauskas, Gregory F.; Tabrizi, Sarah J.; Long, Jeffrey D.; Arnesen, Astri; Hamilton, Jamie L.; Claassen, Daniel O.; Munetsi, Lorraine R.; Malik, Shahid; Rodriguez-Santana, Idaira; Ali, Talaha M.; Zhang, Frank Share Save
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Huntington disease alters the actionable information in plasma extracellular vesicles Neueder, Andreas; Nitzschner, Philipp; Wagner, Ronja; Hummel, Julia; Hoschek, Franziska; Wagner, Maximilian; Abdelmoez, Alshaimaa; von Einem, Bjoern; Landwehrmeyer, G. Bernhard; Tabrizi, Sarah J.; Orth, Michael Share Save
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Tominersen in Adults with Manifest Huntington's Disease McColgan, Peter; Thobhani, Alpa; Boak, Lauren; Schobel, Scott A.; Nicotra, Alessia; Palermo, Giuseppe; Trundell, Dylan; Zhou, Julian; Schlegel, Valerie; Ducray, Patricia Sanwald; Hawellek, David J.; Dorn, Jonas; Simillion, Cedric; Lindemann, Michael; Wheelock, Vicki; Durr, Alexandra; Anderson, Karen E.; Long, Jeffrey D.; Wild, Edward J.; Landwehrmeyer, G. Bernhard; Leavitt, Blair R.; Tabrizi, Sarah J.; Doody, Rachelle Share Save
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