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SavePharmacokinetics and protein binding of cholesterol-conjugated heteroduplex oligonucleotide
Yoshioka, Yukitake; Yamamoto, Syunsuke; Kusamori, Kosuke; Nakayama, Miyu; Fujita, Hisashi; Goto, Akihiko; Iwasaki, Shinji; Nagata, Tetsuya; Itakura, Shoko; Kusuhara, Hiroyuki; Yokota, Takanori; Hirabayashi, Hideki
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SaveHeteroduplex oligonucleotide technology boosts oligonucleotide splice switching activity of morpholino oligomers in a Duchenne muscular dystrophy mouse model
Hasegawa, Juri; Nagata, Tetsuya; Ihara, Kensuke; Tanihata, Jun; Ebihara, Satoe; Yoshida-Tanaka, Kie; Yanagidaira, Mitsugu; Ohara, Masahiro; Sasaki, Asuka; Nakayama, Miyu; Yamamoto, Syunsuke; Ishii, Takashi; Iwata-Hara, Rintaro; Naito, Mitsuru; Miyata, Kanjiro; Sakaue, Fumika; Yokota, Takanori
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