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Frank W.G. Leebeek

Erasmus University Medical Center

72H-index
598Paper Count
2.0WCitation Count
Published Papers 339
Publication Date
Risk of thrombosis and bleeding following CAR T-cell therapy: Insights from the Dutch “Follow that CAR!” registry
err2026-07-28
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errAmica K. Ko; Pim G. N. J. Mutsaers; Lukas M. van Kleij; Amária Vledder; Elise R. A. Pennings; Anne M. Spanjaart; Janneke W. de Boer; Kylie Keijzer; Astrid M. P. Demandt; Jaap A. van Doesum; Suzanne van Dorp; Margot Jak; Maria T. Kuipers; Tom van Meerten; Marjolein W. M. van der Poel; Joost S. P. Vermaat; Frank W. G. Leebeek; Marie J. Kersten; Mandy N. Lauw
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Historical, current and future treatments for von Willebrand disease
err2026-01-01
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errCasari, Caterina; Leebeek, Frank W. G.; Peyvandi, Flora
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Allele-selective Disruption of Pathogenic VWF Variants in Type 2 Von Willebrand Disease using CRISPR/Cas9
err2025-12-22
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errIsabel Bär; Stijn A. Groten; Alastair Barraclough; Petra E. Bürgisser; Calvin van Kwawegen; Peter J. Lenting; Iris van Moort; Jeroen C.J. Eikenboom; Frank W.G. Leebeek; Jan Voorberg; Maartje van den Biggelaar; Ruben Bierings
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Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B
err2025-12-01
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PREAI
errPipe, Steven W.; Miesbach, Wolfgang; Recht, Michael; Leebeek, Frank W. G.; Key, Nigel S.; Castaman, Giancarlo; Lattimore, Susan; Coppens, Michiel; Le Quellec, Sandra; Mahajan, Vaibhav; Gill, Sean; Drelich, Douglass; Monahan, Paul E.
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Correction: Rewriting the script: gene therapy and genome editing for von Willebrand Disease
err2025-11-07
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errAlastair Barraclough†; Isabel Bär†; Tirsa van Duijl; Karin Fijnvandraat; Jeroen C. J. Eikenboom; Frank W. G. Leebeek; Ruben Bierings; Jan Voorberg; Despoina Trasanidou†
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A comprehensive care pathway of gene therapy for hemophilia based on current guideline documents and Summary of Product Characteristics (SMPCs); Communication from the ISTH SSC Working Group on Gene Therapy
err2025-10-27
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PREAI
errCaroline M.A. Mussert; Wolfgang Miesbach; Pratima Chowdary; David Lillicrap; Johnny Mahlangu; Flora Peyvandi; Steven W. Pipe; Alok Srivastava; Jan Voorberg; Glenn F. Pierce; Radoslaw Kaczmarek; Paul Batty; Ilaria Cutica; Amit Nathwani; Frank W.G. Leebeek
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Large deletions in the F8 gene predict immune tolerance induction failure in people with severe hemophilia A
err2025-10-10
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errIlja Oomen; Amal Abdi; Linda Broer; Ricardo M. Camelo; Fábia M.R.A. Callado; Luany E.M. Carvalho; Ilenia L. Calcaterra; Manuel Carcao; Giancarlo Castaman; Jeroen C.J. Eikenboom; Kathelijn Fischer; Vivian K.B. Franco; Judy Geissler; Taco W. Kuijpers; Frank W.G. Leebeek; David Lillicrap; Cláudia S. Lorenzato; Maria Elisa Mancuso; Davide Matino; Matteo N.D. Di Minno; Aomei Mo; Alex B. Mohseny; Sietse Q. Nagelkerke; Johannes Oldenburg; Suely Meireles Rezende; Georges-Etienne Rivard; Natalia Rydz; Saskia E.M. Schols; Michael W.T. Tanck; Jan Voorberg; Karin Fijnvandraat; Samantha C. Gouw
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Sex differences in outcomes of vitamin K antagonist treatment in patients with a mechanical heart valve: a Dutch population-based cohort study
err2025-10-08
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errEva K. Kempers; Chantal Visser; Jaap Seelig; Qingui Chen; Henk J. Adriaansen; Maarten J. Beinema; Arina J. ten Cate-Hoek; Laura M. Faber; Charlotte E.A. Dronkers; Melchior C. Nierman; Roger K. Schindhelm; Nynke M. Wiersma; Alexander D.M. Stork; Frederikus A. Klok; Frank W.G. Leebeek; Ron Pisters; Suzanne C. Cannegieter; Raffaele De Caterina; Martin E.W. Hemels; Hugo ten Cate; Maryam Kavousi; Marieke J.H.A. Kruip
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Rewriting the script: gene therapy and genome editing for von Willebrand Disease
err2025-09-23
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errAlastair Barraclough†; Isabel Bär†; Tirsa van Duijl; Karin Fijnvandraat; Jeroen C. J. Eikenboom; Frank W. G. Leebeek; Ruben Bierings; Jan Voorberg; Despoina Trasanidou†
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A novel cause of type 1 Von Willebrand Disease: impaired exocytosis of Weibel-Palade bodies due to biallelic MADD variants
errBlood
IF23.1
err2025-07-17
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PREAI
errSophie Hordijk; Stijn A. Groten; Petra E. Bürgisser; Sebastiaan N. J. Laan; Georg Christoph Korenke; Tomáš Honzík; Diane Beysen; Frank W. G. Leebeek; Paul A. Skehel; Maartje van den Biggelaar; Tom Carter; Ruben Bierings
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von Willebrand disease-specific defects and proteomic signatures in endothelial colony–forming cells
err2025-05-06
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errSebastiaan N.J. Laan; Stijn Groten; Richard J. Dirven; Petra E. Bürgisser; Frank W.G. Leebeek; Iris van Moort; Maartje van den Biggelaar; Ruben Bierings; Jeroen Eikenboom
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Completion of phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 years
err2025-04-08
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errAnnette von Drygalski; Esteban Gomez; Adam Giermasz; Giancarlo Castaman; Nigel S. Key; Susan U. Lattimore; Frank W. G. Leebeek; Wolfgang A. Miesbach; Michael Recht; Paul E. Monahan; Sandra Le Quellec; Steven W. Pipe
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The severe von Willebrand disease variant p.M771V leads to impaired anterograde trafficking of von Willebrand factor in patient-derived and base-edited endothelial colony-forming cells
err2025-02-01
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PREAI
errBar, Isabel; Barraclough, Alastair; Burgisser, Petra E.; van Kwawegen, Calvin; Fijnvandraat, Karin; Eikenboom, Jeroen C. J.; Leebeek, Frank W. G.; Voorberg, Jan; Bierings, Ruben
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Sexuality and bleeding in von Willebrand disease
err2025-02-01
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errvan Kwawegen, Calvin B.; Pastoor, Hester; Eikenboom, Jeroen; Fijnvandraat, Karin; Ypma, Paula; Heubel-Moenen, Floor C. J. I.; van Galen, Karin P. M.; Mauser-Bunschoten, Evelien P.; Meijer, Karina; Schols, Saskia E. M.; Cnossen, Marjon H.; van der Bom, Johanna G.; de Meris, Joke; Atiq, Ferdows; Kruip, Marieke J. H. A.; Leebeek, Frank W. G.
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Replacement therapy in pregnant women with von Willebrand disease during delivery: Factor levels and pharmacokinetics
err2025-01-03
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errAl Arashi, Wala; Cloesmeijer, Michael E.; Leebeek, Frank W. G.; Duvekot, Johannes J.; Kruip, Marieke J. H. A.; Mathot, Ron A. A.; Cnossen, Marjon H.
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Type of D-dimer assay determines the diagnostic yield of computed tomography in patients suspected for pulmonary embolism
err2025-01-01
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errAssmann, Jorn L. J. C.; Gammeren, Adriaan J. van; Sprenger, Reinier A.; de Wit, Saskia; Ceelie, Huib; Leebeek, Frank W. G.; Schellings, Mark W. M.
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Adeno-associated virus-based gene therapy for hemophilia- addressing the gaps
err2025-01-01
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errMiesbach, Wolfgang; Batty, Paul; Chowdary, Pratima; Fong, Sylvia; Kaczmarek, Radoslaw; Leebeek, Frank W. G.; Long, Brian; Mahlangu, Johnny; Makris, Mike; Pierce, Glenn F.; Pipe, Steven W.; Srivastava, Alok; Voorberg, Jan; Peyvandi, Flora
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Genetic variants, thrombocytopenia, and clinical phenotype of type 2B von Willebrand disease: a median 16-year follow-up study
err2024-12-01
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errvan Kwawegen, Calvin B.; Atiq, Ferdows; Endenburg, Dara; Fijnvandraat, Karin; van Galen, Karin P. M.; Cnossen, Marjon H.; Schols, Saskia E. M.; Kruip, Marieke J. H. A.; van Heerde, Waander L.; de Meris, Joke; van der Bom, Johanna G.; Eikenboom, Jeroen; Meijer, Karina; Leebeek, Frank W. G.
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Patient-reported data on the severity of Von Willebrand disease
err2024-10-15
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errvan Kwawegen, Calvin B.; Fijnvandraat, Karin; Kruip, Marieke J. H. A.; de Meris, Joke; Schols, Saskia E. M.; Meijer, Karina; van der Bom, Johanna G.; Cnossen, Marjon H.; van Galen, Karin P. M.; Atiq, Ferdows; Eikenboom, Jeroen; Leebeek, Frank W. G.
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