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CK1δ/ε-mediated TDP-43 phosphorylation contributes to early motor neuron disease toxicity in amyotrophic lateral sclerosis Ko, Vivian I.; Ong, Kailee; Kwon, Deborah Y.; Li, Xueying; Pietrasiewicz, Alicia; Harvey, James S.; Lulla, Mukesh; Bhat, Guruharsha; Cleveland, Don W.; Ravits, John M. Share Save
Frontotemporal dementia-like disease progression elicited by seeded aggregation and spread of FUS Vazquez-Sanchez, Sonia; Tilkin, Britt; Gasset-Rosa, Fatima; Zhang, Sitao; Piol, Diana; McAlonis-Downes, Melissa; Artates, Jonathan; Govea-Perez, Noe; Verresen, Yana; Guo, Lin; Cleveland, Don W.; Shorter, James; Da Cruz, Sandrine Share Save
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A phage nucleus-associated RNA-binding protein is required for jumbo phage infection Enustun, Eray; Armbruster, Emily G.; Lee, Jina; Zhang, Sitao; Yee, Brian A.; Malukhina, Kseniya; Gu, Yajie; Deep, Amar; Naritomi, Jack T.; Liang, Qishan; Aigner, Stefan; Adler, Benjamin A.; Cress, Brady F.; Doudna, Jennifer A.; Chaikeeratisak, Vorrapon; Cleveland, Don W.; Ghassemian, Majid; Bintu, Bogdan; Yeo, Gene W.; Pogliano, Joe; Corbett, Kevin D. Share Save
Cryptic splicing of stathmin-2 and UNC13A mRNAs is a pathological hallmark of TDP-43-associated Alzheimer's disease Quadros, Ana Rita Agra Almeida; Li, Zhaozhi; Wang, Xue; Ndayambaje, I. Sandra; Aryal, Sandeep; Ramesh, Nandini; Nolan, Matthew; Jayakumar, Rojashree; Han, Yi; Stillman, Hannah; Aguilar, Corey; Wheeler, Hayden J.; Connors, Theresa; Lopez-Erauskin, Jone; Baughn, Michael W.; Melamed, Ze'ev; Beccari, Melinda S.; Martinez, Laura Olmedo; Canori, Michael; Lee, Chao-Zong; Moran, Laura; Draper, Isabelle; Kopin, Alan S.; Oakley, Derek H.; Dickson, Dennis W.; Cleveland, Don W.; Hyman, Bradley T.; Das, Sudeshna; Ertekin-Taner, Niluefer; Lagier-Tourenne, Clotilde Share Save
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GOLGA8 increases bulk antisense oligonucleotide uptake and activity in mammalian cells McMahon, Moira A.; Rahdar, Meghdad; Mukhopadhyay, Swagatam; Bui, Huynh-Hoa; Hart, Christopher; Damle, Sagar; Courtney, Margo; Baughn, Michael W.; Cleveland, Don W.; Bennett, Frank Share Save
Comprehensive evaluation of human-derived anti-poly-GA antibodies in cellular and animal models of C9orf72 disease Jambeau, Melanie; Meyer, Kevin D.; Hruska-Plochan, Marian; Tabet, Ricardos; Lee, Chao-Zong; Ray-Soni, Ananya; Aguilar, Corey; Savage, Kitty; Mishra, Nibha; Cavegn, Nicole; Borter, Petra; Lin, Chun-Chia; Jansen-West, Karen R.; Jiang, Jie; Freyermuth, Fernande; Lia, Nan; De Rossi, Pierre; Perez-Berlanga, Manuela; Jiang, Xin; Daughrity, Lilian M.; Pereira, Joao; Narayanan, Sarav; Gu, Yuanzheng; Dhokai, Shekhar; Dalkilic-Liddle, Isin; Maniecka, Zuzanna; Weber, Julien; Workman, Michael; McAlonis-Downes, Melissa; Berezovski, Eugene; Zhang, Yong-Jie; Berry, James; Wainger, Brian J.; Kankel, Mark W.; Rushe, Mia; Hock, Christoph; Nitsch, Roger M.; Cleveland, Don W.; Petrucelli, Leonard; Gendron, Tania F.; Montrasio, Fabio; Grimm, Jan; Polymenidou, Magdalini; lagier-Tourenne, Clotilde Share Save
A reference human induced pluripotent stem cell line for collaborative studies Pantazis, Caroline B.; Yang, Andrian; Lara, Erika; McDonough, Justin A.; Blauwendraat, Cornelis; Peng, Lirong; Oguro, Hideyuki; Kanaujiya, Jitendra; Zou, Jizhong; Sebesta, David; Pratt, Gretchen; Cross, Erin; Blockwick, Jeffrey; Buxton, Philip; Kinner-Bibeau, Lauren; Medura, Constance; Tompkins, Christopher; Hughes, Stephen; Santiana, Marianita; Faghri, Faraz; Nalls, Mike A.; Vitale, Daniel; Ballard, Shannon; Qi, Yue A.; Ramos, Daniel M.; Anderson, Kailyn M.; Stadler, Julia; Narayan, Priyanka; Papademetriou, Jason; Reilly, Luke; Nelson, Matthew P.; Aggarwal, Sanya; Rosen, Leah U.; Kirwan, Peter; Pisupati, Venkat; Coon, Steven L.; Scholz, Sonja W.; Priebe, Theresa; Ottl, Miriam; Dong, Jian; Meijer, Marieke; Janssen, Lara J. M.; Lourenco, Vanessa S.; van der Kant, Rik; Crusius, Dennis; Paquet, Dominik; Raulin, Ana-Caroline; Bu, Guojun; Held, Aaron; Wainger, Brian J.; Gabriele, Rebecca M. C.; Casey, Jackie M.; Wray, Selina; Abu-Bonsrah, Dad; Parish, Clare L.; Beccari, Melinda S.; Cleveland, Don W.; Li, Emmy; Rose, Indigo V. L.; Kampmann, Martin; Aristoy, Carles Calatayud; Verstreken, Patrik; Heinrich, Laurin; Chen, Max Y.; Schule, Birgitt; Dou, Dan; Holzbaur, Erika L. F.; Zanellati, Maria Clara; Basundra, Richa; Deshmukh, Mohanish; Cohen, Sarah; Khanna, Richa; Raman, Malavika; Nevin, Zachary S.; Matia, Madeline; Van Lent, Jonas; Timmerman, Vincent; Conklin, Bruce R.; Chase, Katherine Johnson; Zhang, Ke; Funes, Salome; Bosco, Daryl A.; Erlebach, Lena; Welzer, Marc; Kronenberg-Versteeg, Deborah; Lyu, Guochang; Arenas, Ernest; Coccia, Elena; Sarrafha, Lily; Ahfeldt, Tim; Marioni, John C.; Skarnes, William C.; Cookson, Mark R.; Ward, Michael E.; Merkle, Florian T. Share Save
Heat-shock chaperone HSPB1 regulates cytoplasmic TDP-43 phase separation and liquid-to-gel transition Lu, Shan; Hu, Jiaojiao; Arogundade, Olubankole Aladesuyi; Goginashvili, Alexander; Vazquez-Sanchez, Sonia; Diedrich, Jolene K.; Gu, Jinge; Blum, Jacob; Oung, Spencer; Ye, Qiaozhen; Yu, Haiyang; Ravits, John; Liu, Cong; Yates, John R., III; Cleveland, Don W. Share Save
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Wild-type FUS corrects ALS-like disease induced by cytoplasmic mutant FUS through autoregulation Sanjuan-Ruiz, Inmaculada; Govea-Perez, Noe; McAlonis-Downes, Melissa; Dieterle, Stephane; Megat, Salim; Dirrig-Grosch, Sylvie; Picchiarelli, Gina; Piol, Diana; Zhu, Qiang; Myers, Brian; Lee, Chao-Zong; Cleveland, Don W.; Lagier-Tourenne, Clotilde; Da Cruz, Sandrine; Dupuis, Luc Share Save
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Immune evasion in HPV-head and neck precancer-cancer transition is driven by an aneuploid switch involving chromosome 9p loss William Jr, William N.; Zhao, Xin; Bianchi, Joy J.; Lin, Heather Y.; Cheng, Pan; Lee, J. Jack; Carter, Hannah; Alexandrov, Ludmil B.; Abraham, Jim P.; Spetzler, David B.; Dubinett, Steven M.; Cleveland, Don W.; Cavenee, Webster; Davoli, Teresa; Lippman, Scott M. Share Save
Novel STMN2 Variant Linked to Amyotrophic Lateral Sclerosis Risk and Clinical Phenotype Theunissen, Frances; Anderton, Ryan S.; Mastaglia, Frank L.; Flynn, Loren L.; Winter, Samantha J.; James, Ian; Bedlack, Richard; Hodgetts, Stuart; Fletcher, Sue; Wilton, Steve D.; Laing, Nigel G.; MacShane, Mandi; Needham, Merrilee; Saunders, Ann; Mackay-Sim, Alan; Melamed, Ze'ev; Ravits, John; Cleveland, Don W.; Akkari, P. Anthony Share Save
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