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Severe inflammation and lineage skewing are associated with poor engraftment of engineered hematopoietic stem cells in patients with sickle cell disease Sobrino, Steicy; Joseph, Laure; Magrin, Elisa; Chalumeau, Anne; Hebert, Nicolas; Corsia, Alice; Denis, Adeline; Roudaut, Cecile; Aussel, Clotilde; Leblanc, Olivia; Brusson, Megane; Felix, Tristan; Diana, Jean-Sebastien; Petrichenko, Angelina; El Etri, Jana; Godard, Auria; Tibi, Eden; Manceau, Sandra; Treluyer, Jean Marc; Mavilio, Fulvio; Bushman, Frederic D.; Marcais, Ambroise; Castelle, Martin; Neven, Benedicte; Hermine, Olivier; Renolleau, Sylvain; Magnani, Alessandra; Asnafi, Vahid; El Nemer, Wassim; Bartolucci, Pablo; Six, Emmanuelle; Semeraro, Michaela; Miccio, Annarita Share Save
Dupilumab in atopic-dermatitis-like eczema associated with inborn errors of immunity: A nationwide study Guillemin, Claire; Bellon, Nathalia; Jachiet, Marie; Barbarot, Sebastien; Bourrat, Emmanuelle; Chiaverini, Christine; Cougoul, Pierre; Ebbo, Mikael; Herber, Mathilde; Hubiche, Thomas; Mallet, Stephanie; Tauber, Marie; Beziat, Vivien; Castelle, Martin; Du Thanh, Aurlie; Farhi, Johathan; Fieschi, Claire; Fournier, Benjamin; Gourguechon, Clement; Guiddir, Tamazoust; Lipsker, Dan; Raison-Peyron, Nadia; Garcelon, Nicolas; Cheminant, Morgane; Suarez, Felipe; Hermine, Olivier; Blanche, Stephane; Moshous, Despina; Mahlaoui, Nizar; Neven, Benedicte; Bodemer, Christine; Levy, Romain; Polivka, Laura Share Save
Iron Deficiency in Familial Mediterranean Fever: A Study on 211 Adult Patients From the JIR Cohort Di Cola, Ilenia; Savey, Lea; Delplanque, Marion; Bourguiba, Rim; Bartoli, Alessandra; Aknouche, Zohra; Bensalek, Fatima; Kone-Paut, Isabelle; Rossi-Semerano, Linda; Melki, Isabelle; Bader-Meunier, Brigitte; Ruscitti, Piero; Neven, Benedicte; Quartier, Pierre; Boursier, Guilaine; Giurgea, Irina; Cuisset, Laurence; Grateau, Gilles; Hentgen, Veronique; Georgin-Lavialle, Sophie Share Save
Performance of serum IL-18 levels for the follow-up of patients with familial Mediterranean fever Elhani, Ines; Calas, Laure; Bejar, Farah; Pieroni, Laurence; Kone-Paut, Isabelle; Rossi-Semerano, Linda; Melki, Isabelle; Bader-Meunier, Brigitte; Neven, Benedicte; Quartier, Pierre; Boursier, Guilaine; Giurgea, Irina; Cuisset, Laurence; Grateau, Gilles; Hentgen, Veronique; Mertz, Philippe; Delplanque, Marion; Savey, Lea; Georgin-Lavialle, Sophie Share Save
Hematopoietic stem cell transplantation for CTLA-4 insufficiency across Europe: A European Society for Blood and Marrow Transplantation Inborn Errors Working Party study Tsilifis, Christo; Speckmann, Carsten; Lum, Su Han; Fox, Thomas A.; Soler, Adriana Margarit; Mozo, Yasmina; Corral, Dolores; Ewins, Anna-Maria; Hague, Rosie; Oikonomopoulou, Christina; Kalwak, Krzysztof; Drabko, Katarzyna; Wynn, Robert; Morris, Emma C.; Elcombe, Suzanne; Bigley, Venetia; Lougaris, Vassilios; Malagola, Michele; Hauck, Fabian; Sedlacek, Petr; Laberko, Alexandra; Tjon, Jennifer M. L.; Buddingh, Emilie P.; Wehr, Claudia; Grimbacher, Bodo; Gennery, Andrew R.; Lankester, Arjan C.; Albert, Michael H.; Neven, Benedicte; Slatter, Mary A. Share Save
Outcome of Cerebral Vasculopathy and Cognitive Performances 10 Years Post-Enrollment in the Drepagreffe Trial Comparing Allogeneic Stem Cell Transplantation to Standard-Care in Children with Sickle Cell Anemia and History of Abnormal Cerebral Velocities Bernaudin, Francoise; Verlhac, Suzanne; Ducros-Miralles, Elisabeth; Arnaud, Cecile; Genty, Isabelle; Petras, Marie; Paillard, Catherine; Isabelle, Thuret; Kamdem, Annie; Pondarre, Corinne; Cannas, Giovanna; Chantalat-Auger, Christelle; De Luna, Gonzalo; Meunier, Benoit; Firah, Nadia; Pertuisel, Sophie; Guitton, Corinne; Joseph, Laure; Missud, Florence; Pluchart, Claire; Elmaleh, Monique; Neven, Benedicte; Angoso, Marie; Frange, Pierre; Yakouben, Karima; Bruno, Benedicte; Dhedin, Nathalie; Dalle, Jean-Hugues; de Latour, Regis Peffault; Belozertseva, Catherine; Jung, Camille Share Save
2q33 Deletions Underlying Syndromic and Non-syndromic CTLA4 Deficiency Brakta, Charlyne; Tabet, Anne-Claude; Puel, Mathilde; Pacault, Mathilde; Stolzenberg, Marie-Claude; Goudet, Claire; Merger, Marguerite; Reumaux, Heloise; Lambert, Nathalie; Alioua, Najiba; Malan, Valerie; Hanein, Sylvain; Dupin-Deguine, Delphine; Treiner, Emmanuel; Lefevre, Guillaume; Farhat, Meryem-Maud; Luca, Luminita Elena; Hureaux, Marguerite; Li, Hailun; Chelloug, Nora; Dehak, Rabha; Boussion, Simon; Ouachee-Chardin, Marie; Schleinitz, Nicolas; Abou Chahla, Wadih; Barlogis, Vincent; Vely, Frederic; Oksenhendler, Eric; Quartier, Pierre; Pasquet, Marlene; Suarez, Felipe; Bustamante, Jacinta; Neven, Benedicte; Picard, Capucine; Rieux-Laucat, Frederic; Levy, Jonathan; Rosain, Jeremie Share Save
Allogeneic Hematopoietic Stem Cell Transplantation (allo-HSCT) Outcomes in Leukocyte Adhesion Deficiency Type-I Booth, Claire; Gilbert, Patrick; Gras, Luuk; Alsaedi, Hawazen; Hamidieh, Amir Ali; Gueye, Mor Seny; Slatter, Mary; Mousavi, Ashrafsadat; Toren, Amos; Karakukcu, Musa; Tbakhi, Abdelghani; Stepensky, Polina; Ozturk, Gulyuz; Bader, Peter; Sengeloev, Henrik; Guengoer, Tayfun; Wynn, R. F.; Locatelli, Franco; Chitty-Lopez, Maria; Matos, Joana E.; Turner, Stuart; Rao, Gayatri R.; Schwartz, Jonathan; Albert, Michael H.; Neven, Benedicte Share Save
Impact of hydroxyurea on follicle density in patients with sickle cell disease Diesch-Furlanetto, Tamara; Sanchez, Carlos; Atkinson, Andrew; Pondarre, Corinne; Dhedin, Nathalie; Neven, Benedicte; Arnaud, Cecile; Kamdem, Annie; Pirenne, France; Lenaour, Gilles; Brocheriou, Isabelle; Terris, Benoit; Bernaudin, Francoise; Dalle, Jean-Hugues; Poirot, Catherine Share Save
IL-7-dependent and -independent lineages of IL-7R-dependent human T cells Arango-Franco, Carlos A.; Ogishi, Masato; Unger, Susanne; Delmonte, Ottavia M.; Orrego, Julio Cesar; Yatim, Ahmad; Velasquez-Lopera, Margarita M.; Zea-Vera, Andres F.; Bohlen, Jonathan; Chbihi, Marwa; Fayand, Antoine; Sanchez, Juan Pablo; Rojas, Julian; Seeleuthner, Yoann; Le Voyer, Tom; Philippot, Quentin; Payne, Kathryn J.; Gervais, Adrian; Erazo-Borras, Lucia, V; Correa-Londono, Luis A.; Cederholm, Axel; Gallon-Duque, Alejandro; Goncalves, Pedro; Doisne, Jean-Marc; Horev, Liran; Charmeteau-de Muylder, Benedicte; Alvarez, Jesus A.; Arboleda, Diana M.; Perez-Zapata, Lizet; Vasquez-Echeverri, Estefania; Moncada-Velez, Marcela; Lopez, Juan A.; Caicedo, Yolanda; Palterer, Boaz; Patino, Pablo J.; Montoya, Carlos J.; Chaldebas, Matthieu; Zhang, Peng; Nguyen, Tina; Ma, Cindy S.; Jeljeli, Mohamed; Alzate, Juan F.; Cabarcas, Felipe; Khan, Taushif; Rinchai, Darawan; Pretet, Jean-Luc; Boisson, Bertrand; Marr, Nico; Ibrahim, Ruba; Molho-Pessach, Vered; Boisson-Dupuis, Stephanie; Kiritsi, Dimitra; Barata, Joao T.; Landegren, Nils; Neven, Benedicte; Abe, Laurent; Lisco, Andrea; Beziat, Vivien; Jouanguy, Emmanuelle; Bustamante, Jacinta; Di Santo, James P.; Tangye, Stuart G.; Notarangelo, Luigi D.; Cheynier, Remi; Natsuga, Ken; Arias, Andres A.; Franco, Jose Luis; Warnatz, Klaus; Casanova, Jean-Laurent; Puel, Anne Share Save
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