Not logged in A clinically relevant retrograde intraductal injection (RIDI) for lipid nanoparticles-mediated base editing in the pancreas Sahel, Deepak; Tiyaboonchai, Amita; Wakefield, Leslie; Renner, Jonas; Jozic, Antony; Dorrell, Craig; Vlasova, Kseniia; Murthy, Namratha Turuvekere Vittala; Grompe, Markus; Sahay, Gaurav Share Save
A porcine model of Fanconi anemia Hergert, Brandon; Whitworth, Kristin M.; Goldman, Devorah C.; Moreau, Lisa; McQueen, Kelsey; Parmar, Kalindi; D'andrea, Alan; Samuel, Melissa S.; Wells, Kevin D.; Prather, Randall S.; Dorell, Craig; Grompe, Markus; Fleming, William H. Share Save
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Enhancing the potency of in vivo lentiviral vector mediated gene therapy to hepatocytes Canepari, Cesare; Milani, Michela; Simoni, Chiara; Starinieri, Francesco; Volpin, Monica; Fabiano, Anna; Biffi, Mauro; Russo, Fabio; Norata, Rossana; Rocchi, Martina; Brombin, Chiara; Cugnata, Federica; Montini, Eugenio; Sanvito, Francesca; Grompe, Markus Share Save
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The DNA methylome of human vascular endothelium and its use in liquid biopsies Peretz, Ayelet; Loyfer, Netanel; Piyanzin, Sheina; Ochana, Bracha Lea; Neiman, Daniel; Magenheim, Judith; Klochendler, Agnes; Drawshy, Zeina; Fox-Fisher, Ilana; Fridlich, Ori; Moss, Joshua; Cohen, Daniel; Zemmour, Hai; Cann, Gordon; Bredno, Joerg; Venn, Oliver; Avni, Batia; Alekberli, Tural; Samet, Yaacov; Korach, Amit; Wald, Ori; Yutkin, Vladimir; Izhar, Uzi; Pillar, Nir; Grompe, Markus; Fridlender, Zvi; Rokach, Ariel; Planer, David; Landesberg, Giora; Glaser, Benjamin; Shemer, Ruth; Kaplan, Tommy; Dor, Yuval Share Save
Fanconi anemia-isogenic head and neck cancer cell line pairs: A basic and translational science resource Nguyen, Hiep Tai; Tang, Weiliang; Webster, Andrew L. H.; Whiteaker, Jeffrey R. R.; Chandler, Christopher M. M.; Errazquin, Ricardo; Roohollahi, Khashayar; Fritzke, Madeline; Hoskins, Elizabeth E. E.; Jonlin, Erica; Wakefield, Leslie; Sullivan, Lucas B. B.; Chen, Eleanor Y. Y.; Dorsman, Josephine; Brakenhoff, Ruud; Paulovich, Amanda G. G.; Grompe, Markus; Garcia-Escudero, Ramon; Wells, Susanne I. I.; Smogorzewska, Agata; Monnat Jr, Raymond J. J. Share Save
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Human hepatocyte PNPLA3-148M exacerbates rapid non-alcoholic fatty liver disease development in chimeric mice Kabbani, Mohammad; Michailidis, Eleftherios; Steensels, Sandra; Fulmer, Clifton G.; Luna, Joseph M.; Le Pen, Jeremie; Tardelli, Matteo; Razooky, Brandon; Ricardo-Lax, Inna; Zou, Chenhui; Zeck, Briana; Stenzel, Ansgar F.; Quirk, Corrine; Foquet, Lander; Ashbrook, Alison W.; Schneider, William M.; Belkaya, Serkan; Lalazar, Gadi; Liang, Yupu; Pittman, Meredith; Devisscher, Lindsey; Suemizu, Hirosh; Theise, Neil D.; Chiriboga, Luis; Cohen, David E.; Copenhaver, Robert; Grompe, Markus; Meuleman, Philip; Ersoy, Baran A.; Rice, Charles M.; Jong, Ype P. de Share Save
Metformin for treatment of cytopenias in children and young adults with Fanconi anemia Pollard, Jessica A.; Furutani, Elissa; Liu, Shanshan; Esrick, Erica; Cohen, Laurie E.; Bledsoe, Jacob; Liu, Chih-Wei; Lu, Kun; de Haro, Maria Jose Ramirez; Sumalles, Jordi; Malsch, Maggie; Kuniholm, Ashley; Galvin, Ashley; Armant, Myriam; Kim, Annette S.; Ballotti, Kaitlyn; Moreau, Lisa; Zhou, Yu; Babushok, Daria; Boulad, Farid; Carroll, Clint; Hartung, Helge; Hont, Amy; Nakano, Taizo; Olson, Tim; Sze, Sei-Gyung; Thompson, Alexis A.; Wlodarski, Marcin W.; Gu, Xuesong; Libermann, Towia A.; D'Andrea, Alan; Grompe, Markus; Weller, Edie; Shimamura, Akiko Share Save
Cancer stem cells: advances in biology and clinical translation-a Keystone Symposia report Cable, Jennifer; Pei, Duanqing; Reid, Lola M.; Wang, Xin Wei; Bhatia, Sonam; Karras, Panagiotis; Melenhorst, Jan Joseph; Grompe, Markus; Lathia, Justin D.; Song, Erwei; Kuo, Calvin J.; Zhang, Ning; White, Richard M.; Ma, Stephanie Ky; Ma, Lichun; Chin, Y. Rebecca; Shen, Michael M.; Ng, Irene Oi Lin; Kaestner, Klaus H.; Zhou, Lei; Sikandar, Shaheen; Schmitt, Clemens A.; Guo, Wei; Wong, Carmen Chak-Lui; Ji, Junfang; Tang, Dean G.; Dubrovska, Anna; Yang, Chunzhang; Wiedemeyer, Wolf R.; Weissman, Irving L. Share Save
Generation of functional ciliated cholangiocytes from human pluripotent stem cells Ogawa, Mina; Jiang, Jia-Xin; Xia, Sunny; Yang, Donghe; Ding, Avrilynn; Laselva, Onofrio; Hernandez, Marcela; Cui, Changyi; Higuchi, Yuichiro; Suemizu, Hiroshi; Dorrell, Craig; Grompe, Markus; Bear, Christine E.; Ogawa, Shinichiro Share Save
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