Not logged in A xeno-free red blood cell differentiation formula models sickle cell disease from somatically sourced patient iPSCs Conway, Ashlee J.; Rosanwo, Tolulope O.; Williamson, Thomas E.; Landry, Samuel; Kinney, Melissa A.; Clark, Martha A.; Vo, Linda T.; Rowe, R. Grant; Marion, William; Zhang, Yosra; Mullin, Nathaniel K.; Shi, Michael; Archer, Natasha M.; Heeney, Matthew M.; Schlaeger, Thorsten M.; Bauer, Daniel E.; Duraisingh, Manoj T.; Brugnara, Carlo; North, Trista E.; Daley, George Q. Share Save
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Acute Promyelocytic Leukemia With Torque Teno Mini Virus::RARA Fusion: An Approach to Screening and Diagnosis Tsai, Harrison K.; Sabbagh, Mark F.; Montesion, Meagan; Williams, Erik A.; Arbini, Arnaldo; Boue, Daniel R.; Harris, Emily M.; Wachter, Franziska; Grimmett, Leslie; Place, Andrew E.; Lucas, Fabienne; Nardi, Valentina; Kim, Annette S.; Brugnara, Carlo; Degar, Barbara; Pollard, Jessica; Harris, Marian H.; Bledsoe, Jacob R. Share Save
Epeleuton, a novel synthetic ω-3 fatty acid, reduces hypoxia/ reperfusion stress in a mouse model of sickle cell disease Matte, Alessandro; Federti, Enrica; Recchiuti, Antonio; Hamza, Moayed; Ferri, Giulia; Riccardi, Veronica; Ceolan, Jacopo; Passarini, Alice; Mazzi, Filippo; Siciliano, Angela; Bhatt, Deepak L.; Coughlan, David; Climax, John; Gremese, Elisa; Brugnara, Carlo; De Franceschi, Lucia Share Save
Mitapivat reprograms the RBC metabolome and improves anemia in a mouse model of hereditary spherocytosis Matte, Alessandro; Wilson, Anand B.; Gevi, Federica; Federti, Enrica; Recchiuti, Antonio; Ferri, Giulia; Brunati, Anna Maria; Pagano, Mario Angelo; Russo, Roberta; Leboeuf, Christophe; Janin, Anne; Timperio, Anna Maria; Iolascon, Achille; Gremese, Elisa; Dang, Lenny; Mohandas, Narla; Brugnara, Carlo; De Franceschi, Lucia Share Save
In Humanized Sickle Cell Mice, Imatinib Protects Against Sickle Cell-Related Injury Federti, Enrica; Matte, Alessandro; Recchiuti, Antonio; Garello, Francesca; Ghigo, Alessandra; El Nemer, Wassim; Terreno, Enzo; Amoresano, Angela; Mattoscio, Domenico; Turrini, Franco; Lebouef, Christophe; Janin, Anne; Pantaleo, Antonella; Russo, Roberta; Marin, Mickael; Iatcencko, Iana; Riccardi, Veronica; Siciliano, Angela; Iolascon, Achille; Brugnara, Carlo; De Franceschi, Lucia Share Save
Mitapivat, a pyruvate kinase activator, improves transfusion burden and reduces iron overload in β-thalassemic mice Matte, Alessandro; Kosinski, Penelope A.; Federti, Enrica; Dang, Lenny; Recchiuti, Antonio; Russo, Roberta; Siciliano, Angela; Riccardi, Veronica; Janin, Anne; Mucci, Matteo; Leboeuf, Christophe; Iolascon, Achille; Brugnara, Carlo; De Franceschi, Lucia Share Save
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The erythroid K-Cl cotransport inhibitor [(dihydroindenyl)oxy]acetic acid blocks erythroid Ca2+-activated K+ channel KCNN4 Rivera, Alicia; Nasburg, Joshua A.; Shim, Heesung; Shmukler, Boris E.; Kitten, Jason; Wohlgemuth, Jay G.; Dlott, Jeffrey S.; Snyder, L. Michael; Brugnara, Carlo; Wulff, Heike; Alper, Seth L. Share Save
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An artificial intelligence-assisted diagnostic platform for rapid near-patient hematology Bachar, Neta; Benbassat, Dana; Brailovsky, David; Eshel, Yochay; Gluck, Dan; Levner, Daniel; Levy, Sarah; Pecker, Sharon; Yurkovsky, Evgeny; Zait, Amir; Sever, Cordelia; Kratz, Alexander; Brugnara, Carlo Share Save
A Grammastola spatulata mechanotoxin-4 (GsMTx4)-sensitive cation channel mediates increased cation permeability in human hereditary spherocytosis of multiple genetic etiologies Vandorpe, David H.; Shmukler, Boris E.; Ilboudo, Yann; Bhasin, Swati; Thomas, Beena; Rivera, Alicia; Wohlgemuth, Jay G.; Dlott, Jeffrey S.; Snyder, L. Michael; Sieff, Colin; Bhasin, Manoj; Lettre, Guillaume; Brugnara, Carlo; Alper, Seth L. Share Save
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The pyruvate kinase activator mitapivat reduces hemolysis and improves anemia in a β-thalassemia mouse model Matte, Alessandro; Federti, Enrica; Kung, Charles; Kosinski, Penelope A.; Narayanaswamy, Rohini; Russo, Roberta; Federico, Giorgia; Carlomagno, Francesca; Desbats, Maria Andrea; Salviati, Leonardo; Leboeuf, Christophe; Valenti, Maria Teresa; Turrini, Francesco; Janin, Anne; Yu, Shaoxia; Beneduce, Elisabetta; Ronseaux, Sebastien; Iatcenko, Iana; Dang, Lenny; Ganz, Tomas; Jung, Chun-Ling; Iolascon, Achille; Brugnara, Carlo; De Franceschi, Lucia Share Save
Single-cell analysis of FOXP3 deficiencies in humans and mice unmasks intrinsic and extrinsic CD4+ T cell perturbations Zemmour, David; Charbonnier, Louis-Marie; Leon, Juliette; Six, Emmanuelle; Keles, Sevgi; Delville, Marianne; Benamar, Mehdi; Baris, Safa; Zuber, Julien; Chen, Karin; Neven, Benedicte; Garcia-Lloret, Maria I.; Ruemmele, Frank M.; Brugnara, Carlo; Cerf-Bensussan, Nadine; Rieux-Laucat, Frederic; Cavazzana, Marina; Andre, Isabelle; Chatila, Talal A.; Mathis, Diane; Benoist, Christophe Share Save
Plasmodium vivax infection compromises reticulocyte stability Clark, Martha A.; Kanjee, Usheer; Rangel, Gabriel W.; Chery, Laura; Mascarenhas, Anjali; Gomes, Edwin; Rathod, Pradipsinh K.; Brugnara, Carlo; Ferreira, Marcelo U.; Duraisingh, Manoj T. Share Save