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Franz Hefti

Eli Lilly

90H-index
421Paper Count
3.2WCitation Count
Published Papers 32
Publication Date
Progranulin AAV gene therapy for frontotemporal dementia: translational studies and phase 1/2 trial interim results
err2024-05-14
err2
errOAAI
errSevigny, Jeffrey; Uspenskaya, Olga; Heckman, Laura Dean; Wong, Li Chin; Hatch, Daniel A.; Tewari, Ambika; Vandenberghe, Rik; Irwin, David J.; Saracino, Dario; Le Ber, Isabelle; Ahmed, Rebekah; Rohrer, Jonathan D.; Boxer, Adam L.; Boland, Sebastian; Sheehan, Patricia; Brandes, Alissa; Burstein, Suzanne R.; Shykind, Benjamin M.; Kamalakaran, Sitharthan; Daniels, Carter W.; David Litwack, E.; Mahoney, Erin; Velaga, Jenny; McNamara, Ilan; Sondergaard, Patricia; Sajjad, Syed A.; Kobayashi, Yvonne M.; Abeliovich, Asa; Hefti, Franz
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PR001 gene therapy increased GCase activity and improved Gaucher disease type 1 phenotypes in mouse models
err2022-02-01
err0
PREAI
errSheehan, Patty; Heckman, Laura D.; Wong, Li Chin; Kamalakaran, Sid; Yang, Zhaohui; Lin, Hsuan-Ni; Garimalla, Swetha; Biezonski, Dominik; Hendricks, Jeremiah; Raghunathan, Rekha; Zhao, Zoe; Raut, Priyam; Politi, Jason; Dai, Yong; Abeliovich, Asa; Hefti, Franz
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Gene Therapy for Parkinson's Disease Associated with GBA1 Mutations
err2021-09-22
err47
errOAAI
errAbeliovich, Asa; Hefti, Franz; Sevigny, Jeffrey
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PR001 gene therapy increased GCase activity and improved Gaucher disease type 1 phenotypes in mouse models
err2021-02-01
err0
PREAI
errSheehan, Patty; Heckman, Laura D.; Wong, Li Chin; Yang, Zhaohui; Lin, Hsuan-Ni; Kamalakaran, Sid; Garimalla, Swetha; Politi, Jason; Dai, Yong; Hefti, Franz; Abeliovich, Asa
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PR001 gene therapy increased GCase activity and improved neuronopathic Gaucher disease phenotypes
err2021-02-01
err0
PREAI
errSheehan, Patty; Heckman, Laura D.; Fenn, Tim; Wong, Li Chin; Nelson, Stuart; Garimalla, Swetha; Haller, Jorge; Daily, Jennifer; Politi, Jason; Dai, Yong; Hefti, Franz; Abeliovich, Asa
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Gene therapy PR006 increased progranulin levels and improved lysosomal related phenotypes in model systems
err2020-02-01
err0
PREAI
errBrandes, Alissa; Heckman, Laura D.; Wong, Li Chin; Yang, Zhaohui; Fenn, Tim; Nelson, Stuart; Aziz, Zarah; Kamalakaran, Sid; Garimalla, Swetha; Burstein, Suzanne; Haller, Jorge; Politi, Jason; Dai, Yong; Hefti, Franz; Abeliovich, Asa
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Gene therapy PR001 increased GCase activity and improved neuronopathic Gaucher disease phenotypes in mouse models
err2020-02-01
err0
PREAI
errHeckman, Laura D.; Sheehan, Patty; Fenn, Tim; Wong, Li Chin; Nelson, Stuart; Garimalla, Swetha; Haller, Jorge; Daily, Jennifer; Politi, Jason; Dai, Yong; Hefti, Franz; Abeliovich, Asa
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Randomized, Placebo Controlled Trial of NPT088, A Phage-Derived, Amyloid-Targeted Treatment for Alzheimer's Disease
err2019-10-01
err14
PREAI
errMichelson, D.; Grundman, M.; Magnuson, K.; Fisher, R.; Levenson, J. M.; Aisen, P.; Marek, K.; Gray, M.; Hefti, F.
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An acute functional screen identifies an effective antibody targeting amyloid-β oligomers based on calcium imaging
err2018-03-15
err21
errOAAI
errWang, Xueying; Kastanenka, Ksenia V.; Arbel-Ornath, Michal; Commins, Caitlin; Kuzuya, Akira; Lariviere, Amanda J.; Krafft, Grant A.; Hefti, Franz; Jerecic, Jasna; Bacskai, Brian J.
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The case for soluble Aβ oligomers as a drug target in Alzheimer's disease
err2013-05-01
err106
PREAI
errHefti, Franz; Goure, William F.; Jerecic, Jasna; Iverson, Kent S.; Walicke, Patricia A.; Krafft, Grant A.
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Advancing Alzheimer's disease diagnosis, treatment, and care: Recommendations from the Ware Invitational Summit
err2012-09-01
err55
errOAAI
errNaylor, Mary D.; Karlawish, Jason H.; Arnold, Steven E.; Khachaturian, Ara S.; Khachaturian, Zaven S.; Lee, Virginia M. -Y.; Baumgart, Matthew; Banerjee, Sube; Beck, Cornelia; Blennow, Kaj; Brookmeyer, Ron; Brunden, Kurt R.; Buckwalter, Kathleen C.; Comer, Meryl; Covinsky, Kenneth; Feinberg, Lynn Friss; Frisoni, Giovanni; Green, Colin; Guimaraes, Renato Maia; Gwyther, Lisa P.; Hefti, Franz F.; Hutton, Michael; Kawas, Claudia; Kent, David M.; Kuller, Lewis; Langa, Kenneth M.; Mahley, Robert W.; Maslow, Katie; Masters, Colin L.; Meier, Diane E.; Neumann, Peter J.; Paul, Steven M.; Petersen, Ronald C.; Sager, Mark A.; Sano, Mary; Schenk, Dale; Soares, Holly; Sperling, Reisa A.; Stahl, Sidney M.; van Deerlin, Vivianna; Stern, Yaakov; Weir, David; Wolk, David A.; Trojanowski, John Q.
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Multimodal image coregistration and inducible selective cell ablation to evaluate imaging ligands
err2011-12-05
err30
errOAAI
errVirostko, John; Henske, Joseph; Vinet, Laurent; Lamprianou, Smaragda; Dai, Chunhua; Radhika, Aramandla; Baldwin, Ronald M.; Ansari, Mohammad S.; Hefti, Franz; Skovronsky, Daniel; Kung, Hank F.; Herrera, Pedro L.; Peterson, Todd E.; Meda, Paolo; Powers, Alvin C.
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Multidentate 18F-Polypegylated Styrylpyridines As Imaging Agents for Aβ Plaques in Cerebral Amyloid Angiopathy (CAA)
err2011-11-09
err46
errOAAI
errZha, Zhihao; Choi, Seok Rye; Ploessl, Karl; Lieberman, Brian P.; Qu, Wenchao; Hefti, Franz; Mintun, Mark; Skovronsky, Daniel; Kung, Hank F.
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Synovial sarcomas usually metastasize after >5 years: a multicenter retrospective analysis with minimum follow-up of 10 years for survivors
err2011-02-01
err162
errOAAI
errKrieg, A. H.; Hefti, F.; Speth, B. M.; Jundt, G.; Guillou, L.; Exner, U. G.; von Hochstetter, A. R.; Cserhati, M. D.; Fuchs, B.; Mouhsine, E.; Kaelin, A.; Klenke, F. M.; Siebenrock, K. A.
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Use of Florbetapir-PET for Imaging β-Amyloid Pathology
err2011-01-19
err906
errOAAI
errClark, Christopher M.; Schneider, Julie A.; Bedell, Barry J.; Beach, Thomas G.; Bilker, Warren B.; Mintun, Mark A.; Pontecorvo, Michael J.; Hefti, Franz; Carpenter, Alan P.; Flitter, Matthew L.; Krautkramer, Michael J.; Kung, Hank F.; Coleman, R. Edward; Doraiswamy, P. Murali; Fleisher, Adam S.; Sabbagh, Marwan N.; Sadowsky, Carl H.; Reiman, P. Eric M.; Zehntner, Simone P.; Skovronsky, Daniel M.
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Preclinical Properties of 18F-AV-45: A PET Agent for Aβ Plaques in the Brain
err2009-10-16
err394
errOAAI
errChoi, Seok Rye; Golding, Geoff; Zhuang, Zhiping; Zhang, Wei; Lim, Nathaniel; Hefti, Franz; Benedum, Tyler E.; Kilbourn, Michael R.; Skovronsky, Daniel; Kung, Hank F.
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