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SavePPDPF preserves integrity of proximal tubule by modulating NMNAT activity in chronic kidney diseases
Fang, Xiaoliang; Zhong, Yi; Zheng, Rui; Wu, Qihui; Liu, Yu; Zhang, Dexin; Wang, Yuwei; Ding, Wubing; Wang, Kaiyuan; Zhong, Fengbo; Lin, Kai; Yao, Xiaohui; Hu, Qingxun; Li, Xiaofei; Xu, Guofeng; Liu, Na; Nie, Jing; Li, Dali
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SaveAmelioration of metabolic and behavioral defects through base editing in the PahR408W phenylketonuria mouse model
Yin, Shuming; Gao, Liangcai; Sun, Xiaoyue; Zhang, Mei; Gao, Hongyi; Chen, Xiaoqing; Zhang, Dan; Ming, Xinyu; Yang, Lei; Hu, Yaqiang; Chen, Xi; Liu, Meizhen; Zhan, Xia; Guan, Yuting; Wang, Liren; Han, Lianshu; Zhu, Ping; Li, Dali
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SaveLuteinizing Hormone Receptor Mutation (LHRN316S) Causes Abnormal Follicular Development Revealed by Follicle Single-Cell Analysis and CRISPR/Cas9
Zhang, Chen; Nie, Yongqiang; Xu, Bufang; Mu, Chunlan; Tian, Geng G.; Li, Xiaoyong; Cheng, Weiwei; Zhang, Aijun; Li, Dali; Wu, Ji
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SaveEngineering IscB to develop highly efficient miniature editing tools in mammalian cells and embryos
Xue, Niannian; Hong, Dishan; Zhang, Dan; Wang, Qian; Zhang, Shun; Yang, Lei; Chen, Xi; Li, Yongmei; Han, Honghui; Hu, Chunyi; Liu, Mingyao; Song, Gaojie; Guan, Yuting; Wang, Liren; Zhu, Yifan; Li, Dali
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SaveEfficient expansion and CRISPR-Cas9-mediated gene correction of patient-derived hepatocytes for treatment of inherited liver diseases
Zhang, Kun; Wan, Ping; Wang, Liren; Wang, Zhen; Tan, Fangzhi; Li, Jie; Ma, Xiaolong; Cen, Jin; Yuan, Xiang; Liu, Yang; Sun, Zhen; Cheng, Xi; Liu, Yuanhua; Liu, Xuhao; Hu, Jiazhi; Zhong, Guisheng; Li, Dali; Xia, Qiang; Hui, Lijian
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SaveAllele-Specific Suppression of Variant MHC With High-Precision RNA Nuclease CRISPR-Cas13d Prevents Hypertrophic Cardiomyopathy
Yang, Ping; Lou, Yingmei; Geng, Zilong; Guo, Zhizhao; Wu, Shuo; Li, Yige; Song, Kaiyuan; Shi, Ting; Zhang, Shasha; Xiong, Junhao; Chen, Alex F.; Li, Dali; Pu, William T.; Da, Lintai; Zhang, Yan; Sun, Kun; Zhang, Bing
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SaveRe-engineering the adenine deaminase TadA-8e for efficient and specific CRISPR-based cytosine base editing (vol 41, pg 663, 2023)
Chen, Liang; Zhu, Biyun; Ru, Gaomeng; Meng, Haowei; Yan, Yongchang; Hong, Mengjia; Zhang, Dan; Luan, Changming; Zhang, Shun; Wu, Hao; Gao, Hongyi; Bai, Sijia; Li, Changqing; Ding, Ruoyi; Xue, Niannian; Lei, Zhixin; Chen, Yuting; Guan, Yuting; Siwko, Stefan; Cheng, Yiyun; Song, Gaojie; Wang, Liren; Yi, Chengqi; Liu, Mingyao; Li, Dali
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SaveAdenine transversion editors enable precise, efficient A•T-to-C•G base editing in mammalian cells and embryos (vol 42, pg pages638, 2024)
Chen, Liang; Hong, Mengjia; Luan, Changming; Gao, Hongyi; Ru, Gaomeng; Guo, Xinyuan; Zhang, Dujuan; Zhang, Shun; Li, Changwei; Wu, Jun; Randolph, Peyton B.; Sousa, Alexander A.; Qu, Chao; Zhu, Yifan; Guan, Yuting; Wang, Liren; Liu, Mingyao; Feng, Bo; Song, Gaojie; Liu, David R.; Li, Dali
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SaveAuthor Correction: Engineering a precise adenine base editor with minimal bystander editing(vol 19, pg 101, 2024)
Chen, Liang; Zhang, Shun; Xue, Niannian; Hong, Mengjia; Zhang, Xiaohui; Zhang, Dan; Yang, Jing; Bai, Sijia; Huang, Yifan; Meng, Haowei; Wu, Hao; Luan, Changming; Zhu, Biyun; Ru, Gaomeng; Gao, Hongyi; Zhong, Liping; Liu, Meizhen; Liu, Mingyao; Cheng, Yiyun; Yi, Chengqi; Wang, Liren; Zhao, Yongxiang; Song, Gaojie; Li, Dali
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SaveDual-responsive nanocarriers for efficient cytosolic protein delivery and CRISPR-Cas9 gene therapy of inflammatory skin disorders
Tan, Echuan; Wan, Tao; Pan, Qi; Duan, Jianan; Zhang, Song; Wang, Ruijue; Gao, Peng; Lv, Jia; Wang, Hui; Li, Dali; Ping, Yuan; Cheng, Yiyun
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SaveEngineering APOBEC3A deaminase for highly accurate and efficient base editing
Yang, Lei; Huo, Yanan; Wang, Man; Zhang, Dan; Zhang, Tianai; Wu, Hao; Rao, Xichen; Meng, Haowei; Yin, Shuming; Mei, Jiale; Zhang, Dexin; Chen, Xi; Lv, Jia; Liu, Meizhen; Cheng, Yiyun; Guan, Yuting; Feng, Bo; Song, Gaojie; Yi, Chengqi; Liu, Mingyao; Zeng, Fanyi; Wang, Liren; Li, Dali
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