Not logged in Safe and durable immune responses to a single dose DNA COVID-19 vaccine in previously vaccinated or SARS-CoV-2-infected adults: A phase 1 study Anwer, Khursheed; Musso, Lauren; Lasrado, Ninaad; Barouch, Dan H.; Ai-Ris-Collier; Sood, Subeena; Sparks, Jeff; Blume, Danielle; Boyer, Jean D.; Faller, Douglas, V; Lindborg, Stacy R. Share Save
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Sky-1214, a Small Molecule Splicing Modulator Targeting FANCL and Fanci, Provides a New Mechanism of Action Targeting Multiple Myeloma and Non-Hodgkin's Lymphoma Rauch, Simone; Reber, Stefan; Perez-Salvia, Montserrat; Pregnolato, Marco; Liu, Botao; Berry, Loren; Buiakova, Olesia; Ratni, Hasane; Gudenas, Brian; Cusulin, Carlo; Shanahan, Lauren; Faller, Douglas, V; Costa, Veronica; Paushkin, Sergey Share Save
Iadademstat in combination with azacitidine in patients with newly diagnosed acute myeloid leukaemia (ALICE) :an open-label, phase 2a dose-finding study Salamero, Olga; Molero, Antonieta; Perez-Simon, Jose Antonio; Arnan, Montserrat; Coll, Rosa; Garcia-Avila, Sara; Acuna-Cruz, Evelyn; Cano, Isabel; Somervaille, Tim C. P.; Gutierrez, Sonia; Arevalo, Maria Isabel; Xaus, Jordi; Buesa, Carlos; Limon, Ana; Faller, Douglas, V; Bosch, Francesc; Montesinos, Pau Share Save
Targeted therapy with nanatinostat and valganciclovir in recurrent EBV-positive lymphoid malignancies: a phase 1b/2 study Haverkos, Bradley; Alpdogan, Onder; Baiocchi, Robert; Brammer, Jonathan E.; Feldman, Tatyana A.; Capra, Marcelo; Brem, Elizabeth A.; Nair, Santosh; Scheinberg, Phillip; Pereira, Juliana; Shune, Leyla; Joffe, Erel; Young, Patricia; Spruill, Susan; Katkov, Afton; McRae, Robert; Royston, Ivor; V. Faller, Douglas; Rojkjaer, Lisa; Porcu, Pierluigi Share Save
Iadademstat in combination with paclitaxel in relapsed/ refractory small cell lung carcinoma (SCLC) and extrapulmonary high grade neuroendocrine carcinoma (NEC) Belani, N.; Ghatalia, P.; Cohen, T.; Ehrlichman, P.; Faller, D.; Iyer, R.; Limon, A.; Soares, H.; Whetstine, J.; Borghaei, H.; Vijayvergia, N. Share Save
Epilepsy: Mitochondrial connections to the 'Sacred' disease Moos, Walter H.; Faller, Douglas V.; Glavas, Ioannis P.; Kanara, Iphigenia; Kodukula, Krishna; Pernokas, Julie; Pernokas, Mark; Pinkerth, Carl A.; Powers, Whitney R.; Sampani, Konstantina; Steliou, Kosta; Vavvas, Demetrios G. Share Save
Quality of life and symptoms among patients with relapsed/refractory AL amyloidosis treated with ixazomib-dexamethasone versus physician's choice Sanchorawala, Vaishali; Wechalekar, Ashutosh D.; Kim, Kihyun; Schonland, Stefan O.; Landau, Heather J.; Kwok, Fiona; Suzuki, Kenshi; Dispenzieri, Angela; Merlini, Giampaolo; Comenzo, Raymond L.; Cherepanov, Dasha; Hayden, Vanessa C.; Kumar, Arun; Labotka, Richard; Faller, Douglas V.; Kastritis, Efstathios Share Save
Time without transfusion reliance: a novel patient-centric metric for new therapies in myelodysplastic syndromes Zeidner, Joshua F.; Mazerolle, Flora; Norton, Jonathan; Regnault, Antoine; Kristo, Fjoralba; Romero, Heather; Fram, Robert J.; V. Faller, Douglas; Dalal, Mehul; Ades, Lionel; Sekeres, Mikkael A. Share Save
Pevonedistat plus azacitidine vs azacitidine alone in higher-risk MDS/chronic myelomonocytic leukemia or low-blast-percentage AML Ades, Lionel; Girshova, Larisa; Doronin, Vadim A.; Diez-Campelo, Maria; Valcarcel, David; Kambhampati, Suman; Viniou, Nora-Athina; Woszczyk, Dariusz; De Paz Arias, Raquel; Symeonidis, Argiris; Anagnostopoulos, Achilles; Ciliao Munhoz, Eduardo; Platzbecker, Uwe; Santini, Valeria; Fram, Robert J.; Yuan, Ying; Friedlander, Sharon; Faller, Douglas, V; Sekeres, Mikkael A. Share Save
Treatment and prevention of pathological mitochondrial dysfunction in retinal degeneration and in photoreceptor injury Moos, Walter H.; V. Faller, Douglas; Glavas, Ioannis P.; Harpp, David N.; Kamperi, Natalia; Kanara, Iphigenia; Kodukula, Krishna; Mavrakis, Anastasios N.; Pernokas, Julie; Pernokas, Mark; Pinkert, Carl A.; Powers, Whitney R.; Sampani, Konstantina; Steliou, Kosta; Tamvakopoulos, Constantin; Vavvas, Demetrios G.; Zamboni, Robert J.; Chen, Xiaohong Share Save
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Phase 1 study to evaluate the effects of rifampin on pharmacokinetics of pevonedistat, a NEDD8-activating enzyme inhibitor in patients with advanced solid tumors Zhou, Xiaofei; Vaishampayan, Ulka; Mahalingam, Devalingam; Harvey, R. Donald; Chung, Ki Young; Sedarati, Farhad; Dong, Cassie; Faller, Douglas, V; Venkatakrishnan, Karthik; Gupta, Neeraj Share Save
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Pevonedistat in East Asian patients with acute myeloid leukemia or myelodysplastic syndromes: a phase 1/1b study to evaluate safety, pharmacokinetics and activity as a single agent and in combination with azacitidine Handa, Hiroshi; Cheong, June-Won; Onishi, Yasushi; Iida, Hiroatsu; Kobayashi, Yukio; Kim, Hyeoung-Joon; Chiou, Tzeon-Jye; Izutsu, Koji; Tsukurov, Olga; Zhou, Xiaofei; Faessel, Helene; Yuan, Ying; Sedarati, Farhad; Faller, Douglas V.; Kimura, Akiko; Wu, Shang-Ju Share Save
A Phase 1 Study of Sapanisertib (TAK-228) in East Asian Patients with Advanced Nonhematological Malignancies (vol 17, pg 15, 2022) Shimizu, Toshio; Kuboki, Yasutoshi; Lin, Chia-Chi; Yonemori, Kan; Yanai, Tomoko; Faller, Douglas V.; Dobler, Lwona; Gupta, Neeraj; Sedarati, Farhad; Kim, Kyu-pyo Share Save
A Phase 1 Study of Sapanisertib (TAK-228) in East Asian Patients with Advanced Nonhematological Malignancies Shimizu, Toshio; Kuboki, Yasutoshi; Lin, Chia-Chi; Yonemori, Kan; Yanai, Tomoko; Faller, Douglas, V; Dobler, Lwona; Gupta, Neeraj; Sedarati, Farhad; Kim, Kyu-pyo Share Save
Randomized phase 2 trial of pevonedistat plus azacitidine versus azacitidine for higher-risk MDS/CMML or low-blast AML (vol 35, pg 2119, 2021) Sekeres, Mikkael A.; Watts, Justin; Radinoff, Atanas; Sangerman, Montserrat Arnan; Cerrano, Marco; Lopez, Patricia Font; Zeidner, Joshua F.; Campelo, Maria Diez; Graux, Carlos; Liesveld, Jane; Selleslag, Dominik; Tzvetkov, Nikolay; Fram, Robert J.; Zhao, Dan; Bell, Jill; Friedlander, Sharon; Faller, Douglas V.; Ades, Lionel Share Save
Pathogenic mitochondrial dysfunction and metabolic abnormalities Moos, Walter H.; Faller, Douglas V.; Glavas, Ioannis P.; Harpp, David N.; Kamperi, Natalia; Kanara, Iphigenia; Kodukula, Krishna; Mavrakis, Anastasios N.; Pernokas, Julie; Pernokas, Mark; Pinkert, Carl A.; Powers, Whitney R.; Steliou, Kosta; Tamvakopoulos, Constantin; Vavvas, Demetrios G.; Zamboni, Robert J.; Sampani, Konstantina Share Save