未登录 Humoral and cellular responses to a tetravalent dengue vaccine (TAK-003) in adults from a dengue non-endemic region: An open-label phase 2 trial 对来自非登革热流行区的成人接种四价登革热疫苗(TAK-003)后的体液和细胞免疫反应:一项开放标签二期临床试验 Mandaric, Sanja; Friberg, Heather; Gottardo, Raphael; Messer, William; Tricou, Vianney; Faccin, Alice; Roubinis, Nicholas; Nadeem, Iqra; Gray, Lauren; Sharma, Mayuri; Currier, Jeffrey R.; Biswal, Shibadas 分享 收藏
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Exome sequencing and analysis of 44,028 British South Asians enriched for high autozygosity 44,028名高近交度富集的英国南亚裔外显子测序与分析 Kim, Hye In; Deboever, Christopher; Walter, Klaudia; Kalantzis, Georgios; Li, Chen; Mozaffari, Sahar V.; Kundu, Kousik; Jacobs, Benjamin M.; Mohammadi-Shemirani, Pedrum; Musolf, Anthony M.; Davitte, Jonathan M.; Aksit, Melis A.; Gafton, Joseph; Catalano, Katrina A.; Dawed, Adem Y.; Graham, Robert R.; Guo, Bin; Gupta, Namrata; Heng, Teng Hiang; Hunt, Karen A.; Iyer, Vivek; Langenberg, Claudia; Lassen, Frederik H.; MacArthur, Daniel G.; Maher, Eamonn R.; Maroteau, Cyrielle; Newman, William G.; O'rahilly, Stephen; Palmer, Duncan S.; Popov, Iaroslav; Siddiqui, Moneeza K.; Simpson, Michael A.; Spreckley, Marie; Wright, John; Del Angel, Guillermo; Petrovski, Slave; Holzinger, Emily R.; Maranville, Joseph C.; Addis, Laura; Turner, Richard M.; Estrada, Karol; Longerich, Simone; Howson, Joanna M. M.; Jamshidi, Yalda; Fauman, Eric B.; Miller, Melissa R.; Diogo, Dorothee; Trembath, Richard C.; Finer, Sarah; Martin, Hilary C.; van Heel, David A. 分享 收藏
Progress and promise of pharmacodynamic biomarkers: novel strategies and assay considerations in drug development 药效学生物标志物的进展与前景:药物开发中的新策略与检测考虑 Fernandez-Metzler, Carmen; Quadrini, Karen J.; Amaravadi, Lakshmi; Cape, Stephanie; Green, Jennifer; Hays, Amanda; Kamphorst, Jurre J.; Laxmanan, Sreenivas; Pandey, Alok; Qiu, Xiazi; Rajapaksha, Ruwini D.; Hassanein, Mohamed 分享 收藏
Pharmacokinetics, safety and tolerability, and efficacy of hyaluronidase-facilitated subcutaneous immunoglobulin 10% (HyQvia®) in Japanese patients with primary immunodeficiency diseases 玻璃酸酶促进的10%皮下免疫球蛋白(HyQvia®)在日本原发性免疫缺陷病患者中的药代动力学、安全性与耐受性及疗效 Kanegane, Hirokazu; Ishimura, Masataka; Suganuma, Eisuke; Imagawa, Tomoyuki; Hoshina, Takayuki; Kawai, Tomoki; Ohnishi, Hidenori; Okada, Satoshi; Suzuki, Chihiro; Kudou, Kentarou; Russo-Schwarzbaum, Sharon; Freedman, Immanuel; Mccoy, Barbara; Li, Zhaoyang; Kuga, Atsushi 分享 收藏
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Matching-adjusted indirect treatment comparison of A plus AVD vs PET-guided ABVD in newly diagnosed advanced Hodgkin lymphoma A plus AVD与PET指导下的ABVD在 newly diagnosed advanced Hodgkin lymphoma中的匹配调整间接治疗比较 Kristo, Fjoralba; Molinari, Alexa; Lan, Zhiyi; Paly, Victoria; Khan, Ramsha; Poirier, Abbey; Moradian, Hoora; Savani, Bipin N.; Zomas, Athanasios; Ashaye, Ajibade 分享 收藏
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Treatment Patterns, Perceptions, Barriers, and Costs in Patients With Chronic Idiopathic Constipation in the United States 美国慢性特发性便秘患者的治疗模式、认知、障碍及成本 Brenner, Darren M.; Moshiree, Baharak; de Courcy, Joanna; Reynolds, Neil; Taylor-Whiteley, Teresa; Jiang, Jeanne; Lu, Mei; Terreri, Brian; Shah, Eric D. 分享 收藏
The prevalence and incidence of narcolepsy in the United States: a real-world observational study using a validated narcolepsy case definition 美国发作性睡病的患病率和发病率:一项使用验证的发作性睡病病例定义的真实世界观察性研究 Ghosh, Somraj; Hoffman, Veena; Calingaert, Brian; Plante, David T.; Krahn, Lois E.; Cai, Alice; Anthony, Mary S.; Dave, Shreya; Rao, Satish; Crawford, Stephen 分享 收藏
A Phase 1/2, Open-Label, Single-Dose, Multicenter Study to Evaluate the Pharmacokinetics and Safety of Human Plasma-Derived Protein C Concentrate in Japanese Patients with Severe Congenital Protein C Deficiency (SCPCD) I期/II期、开放标签、单剂量、多中心研究,旨在评估人血浆衍生蛋白C浓缩物在日本严重先天性蛋白C缺乏症患者(SCPCD)中的药代动力学和安全性 Koh, Katsuyoshi; Nogami, Keiji; Kakuda, Harumi; Okimoto, Yuri; Hino, Moeko; Tanigawara, Yusuke; Li, Zhaoyang; Suzuki, Chihiro; Terashio, Souhei; Ueda, Hitoshi; Ohga, Shouichi 分享 收藏
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Intravenous Delivery of a Gene Therapy Vector that Expresses an Antitransferrin Receptor 1 Nanobody-I2S Fusion Protein Rescued Central Nervous System Lysosomal Burden in Mucopolysaccharidosis II Mice Ruangsiriluk, Wanida; Jacobo, Sarah Melissa P.; Iskenderian, Andrea; Modi, Meera; Chen, Nancy; Felice, Brian; Yuan, Shipeng; Mukherji, Shreya T.; Hernandez, Melody Rivera; Sunkara, Shashank; Macdonald, Amanda; Rajarshi, Girija; Palmieri, Kathleen; Crooker, Robert; Wu, Rui; Dalrymple, Margaret; Chheda, Mihir; Megahid, Donia; Arce, Camila; Shen, Mingfang; Dasari, Bhanu; Zhao, Xiaohui; Yalavarthi, Maneesha; Rompikuntal, Pramod; Ayyadurai, Saravanan; Fang, Josephine; Hozanovic, Alen; Pescatore, Brian; Bassous, Dany; Romashko, Alla; Galbreath, Elizabeth; Maccani, Andreas; Steinkellner, Julia; Ehmann, David E.; Choi, Vivian W.; Islam, Rizwana 分享 收藏
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