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Vertex Pharmaceuticals

学者数1.5K
论文数603
被引数4
关联论文 (599)
发表时间
N-Alkoxysulfurdiimide Reagents for the One-Step Modular Synthesis of Primary SulfonimidamidesN-烷氧基二硫代亚胺试剂用于一步模块化合成初级磺酰基亚胺胺
err2026-07-07
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errOAAI
errSuzanne E. Davison; Jonathan A. Andrews; Agamemnon E. Crumpton; Mireia Sidera Portela; Michael A. Clegg; Damien Valette; Michael C. Willis
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Some Items of Interest to Process R&D Chemists and Engineers对过程研究与开发化学家及工程师感兴趣的一些事项
err2026-06-10
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errOAAI
errJames A. Schwindeman; Timothy Kwok; Annabel Q. Ansel; James M. MacDougall; Jimmy Lauberteaux; Deeksha Jain; Elizabeth M. Dauncey; Augustin Péneau; Carlos Mateos; John Kremers; John Knight
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Developing Predictive Models by Sharing Predictions – An Investigation of a Federated Learning Approach for ADMET Predictions通过共享预测开发预测模型——对用于ADMET预测的联邦学习方法的调查
err2026-05-29
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PREAI
errRajarshi Guha; Wenyi Wang; Edward Price; Barun Bhhatarai; Majdi Hassan; Anthony DiFranzo; Christopher Keefer; Nathaniel Woody; Fabio Broccatelli; Susanne Winiwarter; Ling He; Darren V. S. Green; Christopher D. Edwards; Harutoshi Kato; Yohei Kosugi; Prashant Desai
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Reengineering Protease Inhibitors to Disrupt Hsp70 Chaperone Function重设计蛋白酶抑制剂以破坏Hsp70分子伴侣功能
err2026-05-19
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PREAI
errAweon Richards; Ascensión Ariza-Mateos; Antara Ghosh; Max Kim; Sterling Sandler; Isabelle Yardumian; Gideon Yawson; Jeremy Baryza; Alexander Serganov; Tania J. Lupoli
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Some Items of Interest to Process R&D Chemists and Engineers过程研发化学家和工程师感兴趣的一些事项
err2026-04-30
err0
PREAI
errJames A. Schwindeman; Timothy Kwok; Annabel Q. Ansel; James M. MacDougall; Sylvain Guizzetti; Jimmy Lauberteaux; Deeksha Jain; Chad Ungarean; Thomas James; Augustin Péneau; John Kremers; John Knight
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Uncovering the gene variants in a global cohort of patients with unexplained increased left ventricular wall thickness using next-generation sequencing利用下一代测序技术在全球患者队列中揭示原因不明的左心室壁增厚相关基因变异
err2026-04-17
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PREAI
errArad, Michael; Chaves, Andrea Virginia Ferreira; Antunes, Murillo; Bakhsh, Abeer; Berger, Kenneth I.; Fat, Tse Hung; Alves da Fonseca, Armando; Furtado, Adriana; Maksimova, Irina; Marques e Silva, Sandra; Maski, Manish; Monjes, Enrique; Murillo Benitez, Nelson E.; Ortuno Campos, Eduardo; Ribeiro, Marcia Goncalves; Rodriguez-Gonzalez, Maria Juliana; Yu, Wen-Chung; Onay, Huseyin
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Durable Clinical Benefits With Exa-Cel for SCD With Recurrent Vocs in Participants 5 to 35 Years OldExa-Cel在5至35岁复发性VOCs的SCD患者中表现出持久的临床益处
err2026-04-01
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PREAI
errHobbs, William; Grupp, Stephan; Locatelli, Franco; Sharma, Akshay; de la Fuente, Josu; Bhatia, Monica; Molinari, Lyndsay; Mapara, Markus; Dedeken, Laurence; Liem, Robert; Kuo, Kevin; Meisel, Roland; Shah, Ami; Telfer, Paul; Corbacioglu, Selim; Cavazzana, Marina; Lobitz, Stephan; de Montalembert, Mariane; Rondelli, Damiano; Steinberg, Martin; Walters, Mark; Lux, Chris; Liu, Tina; Boerner, Kevin; Frangoul, Haydar
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Durable Clinical Benefits With Exa-CEL for TDT in Participants 5 To 35 Years Old对于5至35岁TDT参与者的Exa-CEL持久临床益处
err2026-04-01
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PREAI
errHobbs, William; Frangoul, Haydar; Meisel, Roland; de la Fuente, Josu; Corbacioglu, Selim; Algeri, Mattia; Chopra, Yogi; Amrolia, Persis; Rupprecht, Joachim; Kuo, Kevin; Shah, Ami; Lang, Peter; Merkeley, Hayley; Carpenter, Ben; Mapara, Markus; Liem, Robert; Grupp, Steve; Li, Amanda; Kwiatkowski, Janet; Kirby-Allen, Melanie; Cappellini, Maria; Kattamis, Antonis; Sheth, Sujit; Locatelli, Franco; Zairis, Sakellarios; Liu, Tina; Boerner, Kevin
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Advances in Human Mass Balance Studies: An IQ Consortium Perspective on Current Practices and Emerging Trends人类物质平衡研究的进展:IQ联盟关于当前实践和新兴趋势的观点
err2026-03-20
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errOAAI
errJason Boer; Ellen Cannady; Filip Cuyckens; Ulrike Glaenzel; Camille Granvil; Felix Huth; Alexander D. James; Wenying Li; Céline Veau; Graeme Young; Qin Yue; Gregory S. Walker; Upendra A. Argikar; Jonathan N. Bauman; Cathy Cantalloube; Yu-Luan Chen; Ping Kang; Patricia Moliner; Mette L. Pedersen; Isabel Piel; Simone Schadt; Hanno Schieferstein; Julia Suchomel; Shuai Wang; S. Cyrus Khojasteh
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Some Items of Interest to Process R&D Chemists and Engineers对过程研究与开发化学家和工程师感兴趣的一些事项
err2026-02-11
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PREAI
errJames A. Schwindeman; Timothy Kwok; Annabel Q. Ansel; James M MacDougall; Sylvain Guizzetti; Jimmy Lauberteaux; Hannah L. D. Hayes; Christopher B. Kelly; John Knight
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ICD-10 codes for APOL1-mediated kidney disease
err2026-01-21
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PREAI
errBarry I. Freedman; Barbara S. Gillespie; Ogo I. Egbuna
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Lower proteinuria is better for patients with IgA nephropathy: a systematic reviewIgA肾病患者的蛋白尿水平越低越好:一项系统评价
err2026-01-07
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errOAAI
errShah, Ankit; Maski, Manish; Egbuna, Ogo; Longstaff, Whitney; Stricker-Shaver, Janice; Barber, Beth
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Statisticians at the Forefront of Health Technology Assessment: Aligning Regulatory and HTA Evidence Through Transdisciplinary Collaboration统计学家在卫生技术评估前沿:通过跨学科合作协调监管和HTA证据
err2026-01-01
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errOAAI
errJen, Min-Hua; Cai, Zhihong; Chu, Haitao; Becker, Ursula; Cappelleri, Joseph C.; Chen, Liang; Dohring, Orlando; Li, Yinglei; Mt-Isa, Shahrul; Ren, Min; Bridges, Ian
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