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Cystic Fibrosis Foundation

学者数280
论文数209
被引数408
关联论文 (207)
发表时间
In Vitro Responsiveness of 417 CFTR Variants to Vanzacaftor/Tezacaftor/Ivacaftor体外417种CFTR变体对Vanzacaftor/Tezacaftor/Ivacaftor的应答性
err2026-09-11
err0
errOAAI
errHermann Bihler; Andrey Sivachenko; Priyanka Bhatt; Ashley Baldwin; Jan Harrington; Violaine Bailey; Alexi Panagiotou; Divesh Patel; Michael J. Mulligan; Rachel Valdez Misiolek; Kylie Arnold; Yi Cheng; Kevin Coote; Normand E. Allaire; Joshua Conte; Karen S. Raraigh; Garry R. Cutting; Martin Mense
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Association between the childhood opportunity index and healthcare utilization in cystic fibrosis儿童机会指数与囊性纤维化患者医疗利用之间的关联
err2026-09-04
err0
PREAI
errAshley Han; Matt Hall; Elizabeth Cromwell; Ronald L. Gibson; Thida Ong; A. Jay Freeman; Clement L. Ren; Don B. Sanders; Jonathan D. Cogen
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Incidence, prevalence, and survival of persons living with advanced cystic fibrosis lung disease in the United States美国晚期囊性纤维化肺病患者的发生率、患病率和生存率
err2026-08-22
err0
PREAI
errJonathan V Todd; Kathleen J. Ramos; Erin Tallarico; Abigail Thaxton; Chris Beres; Whitney Brown; Albert Faro; Elizabeth A. Cromwell
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SPL84 and Trikafta® exhibit comparable and additive effects in patient-derived HBE cells carrying the 3849+10kb C→T/F508del CFTR variantsSPL84和Trikafta®在携带3849+10kb C→T/F508del CFTR变异的患者来源HBE细胞中表现出相似且相加的效果
err2026-06-26
err0
PREAI
errYi Cheng; Yifat S. Oren; Jan Harrington; Aurélie Hatton; Efrat Ozeri-Galai; Chava D. Stampfer; Tamar Mordechai; Ofra Barchad-Avitzur; Gili Hart; Kevin Coote; Hermann Bihler; Isabelle Sermet-Gaudelus; Martin Mense; Batsheva Kerem
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Obesity in adults with cystic fibrosis following prescription of elexacaftor/tezacaftor/ivacaftor囊性纤维化患者服用elexacaftor/tezacaftor/ivacaftor后的肥胖情况
err2026-06-20
err0
PREAI
errJoshua S. Ostrenga; Christina M. Mingora; Sylvia Szentpetery; Raksha Jain; Michael S. Schechter; Elizabeth Cromwell; Patrick A. Flume
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Global Collaboration in Cystic Fibrosis: Lessons From the COVID-19 Pandemic for Low- and Middle-Income Countries全球囊性纤维化合作:COVID-19大流行对中低收入国家的启示
err2026-03-18
err0
PREAI
errCheng, Stephanie Y.; Zampoli, Marco; Elbert, Alex; Bakkeheim, Egil; Carr, Siobhan B.; Charman, Susan C.; Stephenson, Anne L.
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The Human Cost of Respiratory Care: Professional Quality of Life and Burnout across Multidisciplinary Cystic Fibrosis Teams呼吸护理中的人本代价:囊性纤维化多学科团队的专业生活质量与职业倦怠
errCHEST
IF8.6
err2026-03-14
err0
PREAI
errAlexandra L. Quittner; Elizabeth Seng; Beth A. Smith; Sonia Graziano; Nivedita Chaudhary; Paula Lomas; Emily Muther; Michael S. Schechter; Laura Tillman; Chelsea Toth; Marieke Verkleij; Ruobin Wei; Anna M. Georgiopoulos
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Stakeholder Priorities for Cystic Fibrosis Mental Health Research: A Community and Provider Survey囊性纤维化心理健康研究的利益相关者优先事项:一项社区和提供者调查
err2026-01-20
err0
PREAI
errGeorgiopoulos, Anna M.; Smith, Beth A.; Aliaj, Enid; Riva, Dara; Davis, Kayli; Lomas, Paula; Kirby, Katie; Nowakowski, Alexandra (xan) C. H.; Shiffman, Melissa; Tillman, Laura; Chaudhary, Nivedita; Wei, Ruobin; Schechter, Michael S.; Quittner, Alexandra L.
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Upregulation of a CI-TR mRNA isoform has therapeutic potential for the treatment of 3′ CI-TR PTC variants上调一种CI-TR mRNA剪接异构体对治疗3′端CI-TR移码突变体具有治疗潜力
err2026-01-01
err0
PREAI
errAllaire, Normand E.; Armstrong, Matthew S.; Yoon, Jae Seok; Walker, Mercy C.; Bhatt, Priyanka; Harrington, Jan M.; Cheng, Yi; Wong, Eric I.; Mahoney, John E.; Valley, Hillary C.; Macadino, Caitlin M.; Bihler, Hermann J.; Sivachenko, Andrey Y.; Cotton, Calvin U.; Carulli, John P.; Mense, Martin
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Response响应
errCHEST
IF8.6
err2025-12-09
err0
errOAAI
errA. Whitney Brown; Erin Tallarico; Virginia Steen
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Differences in pulmonary exacerbation risks among CF subpopulationsCF亚群间肺部恶化的风险差异
err2025-11-29
err0
errOAAI
errD.R. VanDevanter; C. O'Rourke; M.W. Konstan; J.P. Clancy; N. Mayer Hamblett
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Global prevalence of CFTR variants with respect to their responsiveness to elexacaftor-tezacaftor-ivacaftorCFTR变异体对伊莱克萨福特-替扎卡福特-伊卡福特的全球流行率
err2025-10-17
err0
errOAAI
errP-R Burgel; A. Orenti; E. Cromwell; M. Macek; H.H. Gutierrez; B. Karadag; A. Faro; J.G. van Rens; L. Naehrlich; E. Bakkeheim; S.B. Carr; A. Lindblad; A. Zolin; E. Lammertyn; R. Ruseckaite; M. Zampoli; C.A. Byrnes; LVRF da Silva-Filho; A. Elbert; S.Y. Cheng; A.L. Stephenson
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Cystic Fibrosis Newborn Screening: A Systematic Review-Driven Consensus Guideline from the United States Cystic Fibrosis Foundation囊性纤维化新生儿筛查:一项基于系统评价的共识指南——来自美国囊性纤维化基金会
err2025-09-29
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errOAAI
errMeghan E. McGarry; Karen S. Raraigh; Philip Farrell; Faith Shropshire; Karey Padding; Cambrey White; M. Christine Dorley; Steven Hicks; Clement L. Ren; Kathryn Tullis; Debra Freedenberg; Q. Eileen Wafford; Sarah E. Hempstead; Marissa A. Taylor; Albert Faro; Marci K. Sontag; Susanna A. McColley
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Cystic Fibrosis Newborn Screening: A Systematic Review-Driven Consensus Guideline from the United States Cystic Fibrosis Foundation囊性纤维化新生儿筛查:一项由美国囊性纤维化基金会推动的系统评价共识指南
err2025-08-21
err0
PREAI
errMeghan E. McGarry; Karen S. Raraigh; Philip Farrell; Faith Shropshire; Karey Padding; Cambrey White; M. Christine Dorley; Steven Hicks; Clement L. Ren; Kathryn Tullis; Debra Freedenberg; Q. Eileen Wafford; Sarah E. Hempstead; Marissa A. Taylor; Albert Faro; Marci K. Sontag; Susanna A. McColley
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PRenatal mOdulator treatment to PrEvent CF complicaTions (PROTECT) workshop reportPRenatal mOdulator治疗以预防CF并发症 (PROTECT) 工作坊报告
err2025-08-05
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errOAAI
errSylvia Szentpetery; Dara Riva; Yair J. Blumenfeld; John F. Engelhardt; Carmen Luna-Paredes; Carlos Milla; Elena K. Schneider-Futschik; Jeanne S Sheffield; Rebecca Darrah; Jane C. Davies; Patrick A Flume; Kimberly E Foil; Christopher N. Fortner; Jennifer S. Guimbellot; Anne D. Lyerly; Nicole Mayer-Hamblett; Clement L. Ren; Jacquelyn Spano; Emma M. Tillman; Aaron Trimble; Benjamin S. Wilfond; Jennifer L. Taylor-Cousar
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Pseudomonas infections persisting after CFTR modulators are widespread throughout the lungs and drive lung inflammationCFTR调节剂治疗后持续存在的铜绿假单胞菌感染遍布整个肺部,并驱动肺部炎症。
err2025-08-05
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errOAAI
errSamantha L. Durfey; Siddhartha G. Kapnadak; Tahuanty Pena; Matthew M. Willmering; J. David Godwin; Mary E. Teresi; Sonya L. Heltshe; Anh T. Vo; Raul A. Villacreses; Ieva Aliukonyte; Linda Boyken; Mal R. Stroik; Sarah J. Morgan; Grace M. Wang; Hannah L. Betts; Shide Zhang; Christopher H. Goss; John P. Clancy; Moira L. Aitken; Chad Steele; Alison F. Feder; Charles R. Esther; Harm A.W.M. Tiddens; Jason C. Woods; David A. Stoltz; Pradeep K. Singh
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