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RNA editing for the treatment of alpha-1 antitrypsin deficiency RNA编辑用于治疗α-1抗胰蛋白酶缺乏症 Monian, Prashant; Shivalila, Chikdu; Lu, Genliang; Bowman, Keith; Briem, Stearne; Bylsma, Marissa; Byrne, Michael; Cannon, Megan; Chatterjee, Arindom; Dallaire, Morgan; Desai, Jigar; Dufresne, Jason; Faraone, Alyse; Favaloro, Frank; Friend, Stephen; Ghosh, Anamitra; Godfrey, Jack; Hernandez, Nidia; Huth, Olivia; Iwamoto, Naoki; Kawamoto, Tomomi; Lamattina, Anthony; Lemaitre, Muriel; Lindsey, Amber; Liu, Fangjun; Looby, Richard; Luu, Khoa; McGlynn, Andrew; Metterville, Jake; Paik, Ik-Hyeon; Pan, Qianli; Patil, Saurabh; Pu, Tom; Purcell-Estabrook, Erin; Ranade, Ashwini; Rheinhardt, Jeanette; Rossi, Jeff; Shimizu, Mamoru; Singh, Kuldeep; Standley, Stephany; Thomas, Carina; Tripathi, Snehlata; Yang, Hailin; Yordanoff, Ryan; Yin, Yuan; Yu, Hui; Narayanan, Padmakumar; Kandasamy, Pachamuthu; Giangrande, Paloma H.; Vargeese, Chandra 分享 收藏
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Rational design of base, sugar and backbone modifications improves ADAR-mediated RNA editing Lu, Genliang; Shivalila, Chikdu; Monian, Prashant; Yu, Hui; Harding, Ian; Briem, Stearne; Byrne, Michael; Faraone, Alyse; Friend, Stephen; Huth, Olivia; Iwamoto, Naoki; Kawamoto, Tomomi; Kumarasamy, Jayakanthan; Lamattina, Anthony; Longo, Kenneth; McCarthy, Leah; McGlynn, Andrew; Molski, Allison; Pan, Qianli; Pu, Tom; Purcell-Estabrook, Erin; Rossi, Jeff; Standley, Stephany; Thomas, Carina; Walen, Alexandra; Yang, Hailin; Kandasamy, Pachamuthu; Vargeese, Chandra 分享 收藏
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Impact of stereopure chimeric backbone chemistries on the potency and durability of gene silencing by RNA interference Liu, Wei; Iwamoto, Naoki; Marappan, Subramanian; Luu, Khoa; Tripathi, Snehlata; Purcell-Estabrook, Erin; Shelke, Juili Dilip; Shah, Himali; Lamattina, Anthony; Pan, Qianli; Schrand, Brett; Favaloro, Frank; Bedekar, Mugdha; Chatterjee, Arindom; Desai, Jigar; Kawamoto, Tomomi; Lu, Genliang; Metterville, Jake; Samaraweera, Milinda; Prakasha, Priyanka Shiva; Yang, Hailin; Yin, Yuan; Yu, Hui; Giangrande, Paloma H.; Byrne, Michael; Kandasamy, Pachamuthu; Vargeese, Chandra 分享 收藏
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Reliability and validity of the Chinese version of the kiddie-schedule for affective disorders and schizophrenia-present and lifetime version DSM-5 (K-SADS-PL-C DSM-5) Dun, Yue; Li, Qiu-Rong; Yu, Hui; Bai, Yu; Song, Zhao; Lei, Chi; Li, Hong-Hua; Gong, Jun; Mo, Yun; Li, Yan; Pei, Xu-Yao; Yuan, Jing; Li, Na; Xu, Chen-Yang; Lai, Qing-Yuan; Fu, Zhao; Zhang, Kang-Fuxi; Song, Jia-Yao; Kang, Si-Min; Sun, Li; Wang, Yu-Feng; Yang, Li; Cao, Qing-Jiu 分享 收藏
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Endogenous ADAR-mediated RNA editing in non-human primates using stereopure chemically modified oligonucleotides Monian, Prashant; Shivalila, Chikdu; Lu, Genliang; Shimizu, Mamoru; Boulay, David; Bussow, Karley; Byrne, Michael; Bezigian, Adam; Chatterjee, Arindom; Chew, David; Desai, Jigar; Favaloro, Frank; Godfrey, Jack; Hoss, Andrew; Iwamoto, Naoki; Kawamoto, Tomomi; Kumarasamy, Jayakanthan; Lamattina, Anthony; Lindsey, Amber; Liu, Fangjun; Looby, Richard; Marappan, Subramanian; Metterville, Jake; Murphy, Ronelle; Rossi, Jeff; Pu, Tom; Bhattarai, Bijay; Standley, Stephany; Tripathi, Snehlata; Yang, Hailin; Yin, Yuan; Yu, Hui; Zhou, Cong; Apponi, Luciano H.; Kandasamy, Pachamuthu; Vargeese, Chandra 分享 收藏