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Reversion of metabolic dysfunction-associated steatohepatitis by skeletal muscle-directed FGF21 gene therapy Jimenez, Veronica; Sacristan, Victor; Jambrina, Claudia; Jaen, Maria Luisa; Casana, Estefania; Munoz, Sergio; Marco, Sara; Molas, Maria; Garcia, Miquel; Grass, Ignasi; Leon, Xavier; Elias, Ivet; Ribera, Albert; Elias, Gemma; Sanchez, Victor; Vila, Laia; Casellas, Alba; Ferre, Tura; Rodo, Jordi; Carretero, Ana; Pumarola, Marti; Navarro, Marc; Andaluz, Anna; Moll, Xavier; Anor, Sonia; Franckhauser, Sylvie; Vergara, Mercedes; Caixas, Assumpta; Bosch, Fatima 分享 收藏
AAV-FGF21 Gene Therapy Extends Healthspan in Old Mice Jimenez, Veronica; Sacristan, Victor; Garcia, Miquel; Jambrina, Claudia; Casana, Estefania; Munoz, Sergio A.; Leon, Xavier; Ribera, Albert; Elias, Ivet; Ferre, Tura; Bosch, Fatima 分享 收藏
Gene Therapy for MODY3 Moving from Mice to Large Animals Casana, Estefania; Jimenez, Veronica; Garcia, Miquel; Jaen, Maria Luisa; Casellas, Alba; Morro, Meritxell; Pujol, Anna; Ferre, Tura; Sacristan, Victor; Jambrina, Claudia; Leon, Xavier; Franckhauser, Sylvie; Bosch, Fatima 分享 收藏
Brain-Directed AAV-FGF21 Gene Therapy Reverses Type 2 Diabetes, Obesity, and Cognitive Decline Bosch, Fatima; Sacristan, Victor; Ribera, Albert; Costa, Sara Marco; Jambrina, Claudia; Jimenez, Veronica; Casana, Estefania; Leon, Xavier; Elias, Gemma; Ferre, Tura; Franckhauser, Sylvie; Elias, Ivet 分享 收藏
Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy Munoz, Sergio; Bertolin, Joan; Jimenez, Veronica; Jaen, Maria Luisa; Garcia, Miquel; Pujol, Anna; Vila, Laia; Sacristan, Victor; Barbon, Elena; Ronzitti, Giuseppe; El Andari, Jihad; Tulalamba, Warut; Pham, Quang Hong; Ruberte, Jesus; VandenDriessche, Thierry; Chuah, Marinee K.; Grimm, Dirk; Mingozzi, Federico; Bosch, Fatima 分享 收藏
Reversion of Nonalcoholic Steatohepatitis by Skeletal-Muscle Directed FGF21 Gene Therapy Jimenez, Veronica; Sacristan, Victor; Jambrina, Claudia; Jaen, Maria Luisa; Munoz, Sergio A.; Casana, Estefania; Garcia, Miquel; Grass, Ignasi; Leon, Xavier; Elias, Ivet; Ribera, Albert; Elias, Gemma; Sanchez, Victor; Casellas, Alba; Ferre, Tura; Molas, Maria; Bosch, Fatima 分享 收藏
Evolution of KT-A112, an AAVMediated Gene Therapy for the Treatment of Type 1 Diabetes Smith, Chari; Harrington, William W.; Stone, Michele; Karadge, Uma; Liu, Jiewu; Quinn, William J., III; Bassiri, Ashlyn; Mallory, Jason; Jimenez, Veronica; Bosch, Fatima; Rhodes, Melissa 分享 收藏
Treatment of MODY3 Disease by AAV-Hnf1a-Mediated Gene Therapy Lorente, Estefania Casana; Jimenez, Veronica; Garcia, Miquel; Casellas, Alba; Morro, Meritxell; Pujol, Anna; Ferre, Tura; Sacristan, Victor; Jambrina, Claudia; Leon, Xavier; Franckhauser, Sylvie; Bosch, Fatima 分享 收藏
Integrated gene expression profiles reveal a transcriptomic network underlying the thermogenic response in adipose tissue Rodo, Jordi; Garcia, Miquel; Casana, Estefania; Munoz, Sergio; Jambrina, Claudia; Sacristan, Victor; Franckhauser, Sylvie; Grass, Ignasi; Jimenez, Veronica; Bosch, Fatima 分享 收藏
Overexpressing high levels of human vaspin limits high fat diet-induced obesity and enhances energy expenditure in a transgenic mouse Rapoehn, Inka; Elias, Ivet; Weiner, Juliane; Pujol, Anna; Kehr, Stephanie; Chadt, Alexandra; Al-Hasani, Hadi; Burkhardt, Ralph; Kloeting, Nora; Stumvoll, Michael; Bosch, Fatima; Kovacs, Peter; Heiker, John T.; Breitfeld, Jana 分享 收藏
Analysis of genome-wide knockout mouse database identifies candidate ciliopathy genes Higgins, Kendall; Moore, Bret A.; Berberovic, Zorana; Adissu, Hibret A.; Eskandarian, Mohammad; Flenniken, Ann M.; Shao, Andy; Imai, Denise M.; Clary, Dave; Lanoue, Louise; Newbigging, Susan; Nutter, Lauryl M. J.; Adams, David J.; Bosch, Fatima; Braun, Robert E.; Brown, Steve D. M.; Dickinson, Mary E.; Dobbie, Michael; Flicek, Paul; Gao, Xiang; Galande, Sanjeev; Grobler, Anne; Heaney, Jason D.; Herault, Yann; de Angelis, Martin Hrabe; Chin, Hsian-Jean Genie; Mammano, Fabio; Qin, Chuan; Shiroishi, Toshihiko; Sedlacek, Radislav; Seong, J-K; Xu, Ying; Lloyd, K. C. Kent; McKerlie, Colin; Moshiri, Ala 分享 收藏
Interaction of a viral insulin-like peptide with the IGF-1 receptor produces a natural antagonist Moreau, Francois; Kirk, Nicholas S.; Zhang, Fa; Gelfanov, Vasily; List, Edward O.; Chrudinova, Martina; Venugopal, Hari; Lawrence, Michael C.; Jimenez, Veronica; Bosch, Fatima; Kopchick, John J.; DiMarchi, Richard D.; Altindis, Emrah; Kahn, C. Ronald 分享 收藏
CDK4 is an essential insulin effector in adipocytes (vol 126, pg 335, 2016) Lagarrigue, Sylviane; Lopez-Mejia, Isabel C.; Denechaud, Pierre-Damien; Escote, Xavier; Castillo-Armengol, Judit; Jimenez, Veronica; Chavey, Carine; Giralt, Albert; Lai, Qiuwen; Zhang, Lianjun; Martinez-Carreres, Laia; Delacuisine, Brigitte; Annicotte, Jean-Sebastien; Blanchet, Emilie; Hure, Sebastien; Abella, Anna; Tinahones, Francisco J.; Vendrell, Joan; Dubus, Pierre; Bosch, Fatima; Kahn, C. Ronald; Fajas, Lluis 分享 收藏
Insulin receptor activation by proinsulin preserves synapses and vision in retinitis pigmentosa Sanchez-Cruz, Alonso; Hernandez-Pinto, Alberto; Lillo, Concepcion; Isiegas, Carolina; Marchena, Miguel; Lizasoain, Ignacio; Bosch, Fatima; de la Villa, Pedro; Hernandez-Sanchez, Catalina; de la Rosa, Enrique J. 分享 收藏
Treatment of skeletal and non-skeletal alterations of Mucopolysaccharidosis type IVA by AAV-mediated gene therapy Bertolin, Joan; Sanchez, Victor; Ribera, Albert; Jaen, Maria Luisa; Garcia, Miquel; Pujol, Anna; Sanchez, Xavier; Munoz, Sergio; Marco, Sara; Perez, Jennifer; Elias, Gemma; Leon, Xavier; Roca, Carles; Jimenez, Veronica; Otaegui, Pedro; Mulero, Francisca; Navarro, Marc; Ruberte, Jesus; Bosch, Fatima 分享 收藏
Adipose tissue is a key organ for the beneficial effects of GLP-2 metabolic function Ejarque, Miriam; Sabadell-Basallote, Joan; Beiroa, Daniel; Calvo, Enrique; Keiran, Noelia; Nunez-Roa, Catalina; Rodriguez, Maria del Mar; Sabench, Fatima; del Castillo, Daniel; Jimenez, Veronica; Bosch, Fatima; Nogueiras, Ruben; Vendrell, Joan; Fernandez-Veledo, Sonia 分享 收藏