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收藏RNA-Based Therapy Utilizing Oculopharyngeal Muscular Dystrophy Transcript Knockdown and Replacement
Abu-Baker, Aida; Kharma, Nawwaf; Perreault, Jonathan; Grant, Alanna; Shekarabi, Masoud; Maios, Claudia; Dona, Michele; Neri, Christian; Dion, Patrick A.; Parker, Alex; Varin, Luc; Rouleau, Guy A.
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收藏Automated design of hammerhead ribozymes and validation by targeting the PABPN1 gene transcript
Kharma, Nawwaf; Varin, Luc; Abu-Baker, Aida; Ouellet, Jonathan; Najeh, Sabrine; Ehdaeivand, Mohammad-Reza; Belmonte, Gabriel; Ambri, Anas; Rouleau, Guy; Perreault, Jonathan
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