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Switching from inotersen to eplontersen in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: analysis from NEURO-TTRansform (vol 271, pg 6655, 2024) 从伊托塞森切换到艾普隆特塞森治疗遗传性甲状腺素转运蛋白介导的淀粉样变性伴多发性神经病变:NEURO-TTRansform(第271卷,第6655页,2024年)的分析 Conceicao, Isabel; Berk, John L.; Weiler, Markus; Kowacs, Pedro A.; Dasgupta, Noel R.; Khella, Sami; Chao, Chi-Chao; Attarian, Shahram; Kwoh, T. Jesse; Jung, Shiangtung W.; Chen, Jersey; Viney, Nicholas J.; Yu, Rosie Z.; Gertz, Morie; Masri, Ahmad; Cruz, Marcia Waddington; Coelho, Teresa 分享 收藏
Effects of eplontersen on symptoms of autonomic neuropathy in hereditary transthyretin-mediated amyloidosis: secondary analysis from the NEURO-TTRansform trial Wixner, Jonas; Berk, John L.; Adams, David; Polydefkis, Michael; Conceicao, Isabel; Attarian, Shahram; Gillmore, Julian D.; Dyck, P. James B.; Folkvaljon, Folke; Zhou, Wunan; Chen, Jersey; Viney, Nicholas J.; Kwoh, T. Jesse; Coelho, Teresa; Waddington-Cruz, Marcia 分享 收藏
Brain MRI in patients with V30M hereditary transthyretin amyloidosis Sousa, Luisa; Pinto, Catarina; Azevedo, Ana; Igreja, Liliana; Marta, Ana; Fernandes, Joana; Oliveira, Pedro; Cardoso, Marcio; Alves, Cristina; da Silva, Ana Martins; Pinto, Miguel Mendonca; Sousa, Ana Paula; Coelho, Teresa; Taipa, Ricardo 分享 收藏
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Clinical and Genotype Characteristics and Symptom Migration in Patients With Mixed Phenotype Transthyretin Amyloidosis from the Transthyretin Amyloidosis Outcomes Survey Gonzalez-Moreno, Juan; Dispenzieri, Angela; Grogan, Martha; Coelho, Teresa; Tournev, Ivailo; Waddington-Cruz, Marcia; Wixner, Jonas; Diemberger, Igor; Garcia-Pavia, Pablo; Chapman, Doug; Gupta, Pritam; Glass, Oliver 分享 收藏
A 15-year consolidated overview of data in over 6000 patients from the Transthyretin Amyloidosis Outcomes Survey (THAOS) Gentile, Luca; Coelho, Teresa; Dispenzieri, Angela; Conceicao, Isabel; Waddington-Cruz, Marcia; Kristen, Arnt; Wixner, Jonas; Diemberger, Igor; Gonzalez-Moreno, Juan; Cariou, Eve; Maurer, Mathew S.; Plante-Bordeneuve, Violaine; Garcia-Pavia, Pablo; Tournev, Ivailo; Gonzalez-Costello, Jose; Duarte, Alejandra Gonzalez; Grogan, Martha; Mazzeo, Anna; Chapman, Doug; Gupta, Pritam; Glass, Oliver; Amass, Leslie; THAOS Investigators 分享 收藏
Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy Eplontersen用于遗传性甲状腺素蛋白淀粉样变性伴多发性神经病 Coelho, Teresa; Marques, Wilson, Jr.; Dasgupta, Noel R.; Chao, Chi-Chao; Parman, Yesim; Franca, Marcondes Cavalcante, Jr.; Guo, Yuh-Cherng; Wixner, Jonas; Ro, Long-Sun; Calandra, Cristian R.; Kowacs, Pedro A.; Berk, John L.; Obici, Laura; Barroso, Fabio A.; Weiler, Markus; Conceicao, Isabel; Jung, Shiangtung W.; Buchele, Gustavo; Brambatti, Michela; Chen, Jersey; Hughes, Steven G.; Schneider, Eugene; Viney, Nicholas J.; Masri, Ahmad; Gertz, Morie R.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Dyck, P. James B.; Cruz, Marcia Waddington 分享 收藏
Optimal practices for the management of hereditary transthyretin amyloidosis: real-world experience from Japan, Brazil, and Portugal Ando, Yukio; Waddington-Cruz, Marcia; Sekijima, Yoshiki; Koike, Haruki; Ueda, Mitsuharu; Konishi, Hiroaki; Ishii, Tomonori; Coelho, Teresa 分享 收藏
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Patients with transthyretin amyloidosis enrolled in THAOS between 2018 and 2021 continue to experience substantial diagnostic delay Coelho, Teresa; Dispenzieri, Angela; Grogan, Martha; Conceicao, Isabel; Waddington-Cruz, Marcia V.; Kristen, Arnt; Wixner, Jonas; Diemberger, Igor; Gonzalez-Moreno, Juan S.; Maurer, Mathew; Plante-Bordeneuve, Violaine; Garcia-Pavia, Pablo; Tournev, Ivailo; Gonzalez-Costello, Jose; Cariou, Eve; Gonzalez-Duarte, Alejandra; Glass, Oliver; Chapman, Doug; Amass, Leslie 分享 收藏
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Characteristics of Patients with Hereditary Transthyretin Amyloidosis-Polyneuropathy (ATTRv-PN) in NEURO-TTRansform, an Open-label Phase 3 Study of Eplontersen Eplontersen的开放标签3期研究neuro-ttransform中遗传性甲状腺素蛋白淀粉样变性多发性神经病 (attrv-pn) 患者的特征 Coelho, Teresa; Cruz, Marcia Waddington; Chao, Chi-Chao; Parman, Yesim; Wixner, Jonas; Weiler, Markus; Barroso, Fabio A.; Dasgupta, Noel R.; Jung, Shiangtung W.; Schneider, Eugene; Viney, Nicholas J.; Dyck, P. James B.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Gertz, Morie A.; Obici, Laura; Berk, John L. 分享 收藏
Liver-directed drugs for transthyretin-mediated amyloidosis 转甲状腺素蛋白介导的淀粉样变性的肝导向药物 Brannagan, Thomas H.; Berk, John L.; Gillmore, Julian D.; Maurer, Mathew S.; Waddington-Cruz, Marcia; Fontana, Marianna; Masri, Ahmad; Obici, Laura; Brambatti, Michela; Baker, Brenda F.; Hannan, Lisa A.; Buchele, Gustavo; Viney, Nick J.; Coelho, Teresa; Nativi-Nicolau, Jose 分享 收藏
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Tafamidis polyneuropathy amelioration requires modest increases in transthyretin stability even though increases in plasma native TTR and decreases in non-native TTR do not predict response Monteiro, Cecilia; Mesgarzadeh, Jaleh S.; Anselmo, Joao; Fernandes, Joana; Novais, Marta; Rodrigues, Carla; Powers, David L.; Powers, Evan T.; Coelho, Teresa; Kelly, Jeffery W. 分享 收藏
Efficacy and safety of vutrisiran for patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: a randomized clinical trial Adams, David; Tournev, Ivailo L.; Taylor, Mark S.; Coelho, Teresa; Plante-Bordeneuve, Violaine; Berk, John L.; Gonzalez-Duarte, Alejandra; Gillmore, Julian D.; Low, Soon-Chai; Sekijima, Yoshiki; Obici, Laura; Chen, Chongshu; Badri, Prajakta; Arum, Seth M.; Vest, John; Polydefkis, Michael 分享 收藏
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