未登录 Pegcetacoplan for Adolescents with C3 Glomerulopathy or Primary Immune Complex Membranoproliferative GN: Phase 3 VALIANT Subgroup Analysis pegcetacoplan治疗C3肾小球病或原发性免疫复合物膜增生性肾小球肾炎的青少年:III期VALIANT亚组分析 Vivarelli, Marina; Ariceta, Gema; Borovitz, Yael; Dixon, Bradley P.; Greenbaum, Larry A.; Licht, Christoph; Mastrangelo, Antonio; Melhem, Nabil; Fujita, Naoya; van de Kar, Nicole C. A. J.; Wallace, Dean; Khankin, Eli; Wang, Zhongshen; Lopez-Lazaro, Luis; Szamosi, Johan; Nester, Carla M. 分享 收藏
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Pegcetacoplan demonstrates clinically significant responses in C3G and primary (idiopathic) IC-MPGN Patients with or without concomitant immunosuppression in VALIANT Pegcetacoplan在VALIANT研究中显示出在C3G和原发性(特发性)IC-MPGN患者中具有临床显著疗效,无论其是否联用免疫抑制治疗。 Kavanagh, David; Bomback, Andrew S.; Ariceta, Gema; Mastrangelo, Antonio; Nester, Carla M.; Remuzzi, Giuseppe; Vivarelli, Marina; Wang, Zhongshen; Szamosi, Johan; Decker, Dima; Gallardo, Lucia Quintana; Fakhouri, Fadi 分享 收藏
Targeted treatment with pegcetacoplan for adolescents with C3G or primary (idiopathic) IC-MPGN in the VALIANT Phase 3 trial VALIANT III期临床试验中,使用pegcetacoplan针对青少年C3G或原发性(特发性)IC-MPGN的靶向治疗 Mastrangelo, Antonio; Vivarelli, Marina; Ariceta, Gema; Borovitz, Yael; Dixon, Bradley P.; Licht, Christoph; Melhem, Nabil; Van De Kar, Nicole; Wallace, Dean; Li, Li; Lopez-Lazaro, Luis; Nester, Carla M. 分享 收藏
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Identification of modifier gene variants overrepresented in familial hypomagnesemia with hypercalciuria and nephrocalcinosis patients with a more aggressive renal phenotype Vall-Palomar, Monica; Torchia, Julieta; Morata, Jordi; Duran, Monica; Tonda, Raul; Ferrer, Mireia; Sanchez, Alex; Cantero-Recasens, Gerard; Ariceta, Gema; Meseguer, Anna; Martinez, Cristina 分享 收藏
Real-world use of complement inhibitors for haemolytic uraemic syndrome: an analysis of the European Rare Kidney Disease Registry cohort 补体抑制剂在溶血尿毒症综合征中的真实世界应用:欧洲罕见肾脏疾病登记研究队列分析 Vujovic, Aleksandra; Sellier-Leclerc, Anne-Laure; Mancuso, Maria Cristina; Boyer, Olivia; Awan, Atif; Gargiulo, Antonio; Loos, Sebastian; Fila, Marc; Jankauskiene, Augustina; Ariceta, Gema; Kanzelmeyer, Nele; Vidal, Enrico; Van Dyck, Maria; Levart, Tanja Kersnik; Simankova, Nadezda; Decramer, Stephane; Hofstetter, Jonas; Vivarelli, Marina; Sciascia, Savino; van de Kar, Nicole C. A. J.; Schaefer, Franz 分享 收藏
Clinical Practice Recommendations on Kidney Management in Methylmalonic Acidemia: an Expert Consensus Statement From ERKNet and MetabERN Servais, Aude; Zacchia, Miriam; Dehoux, Laurene; Shroff, Rukshana; Brassier, Anais; Taurisano, Roberta; Koelker, Stefan; Oh, Jun; Ariceta, Gema; Stojanovic, Jelena; Hoerster, Friederike; Strologo, Dello; Spada, Marco; Schiff, Manuel; Dionisi-Vici, Carlo 分享 收藏
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International expert consensus statement on the diagnosis and management of congenital nephrogenic diabetes insipidus (arginine vasopressin resistance) Levtchenko, Elena; Ariceta, Gema; Arguedas Flores, Olga; Bichet, Daniel G.; Bockenhauer, Detlef; Emma, Francesco; Hoorn, Ewout J.; Koster-Kamphuis, Linda; Nijenhuis, Tom; Trepiccione, Francesco; Vargas-Poussou, Rosa; Walsh, Stephen B.; Knoers, Nine V. A. M. 分享 收藏
Role of SARS-CoV-2-specific memory B cells promoting immune protection after booster vaccination in solid organ transplantation Donadeu, Laura; Gomez-Olles, Susana; Casanova, Franc; Torija, Alba; Lopez-Meseguer, Manuel; Boada-Perez, Meritxell; Kervella, Delphine; Crespo, Elena; Carrera-Munoz, Claudia; Campos-Varela, Isabel; Castells, Lluis; Cortese, Maria F.; Esperalba, Juliana; Fernandez-Naval, Candela; Quintero, Jesus; Munoz, Marina; Aguero, Fernando; Gonzalez-Costello, Jose; Llado, Laura; Fava, Alexandre; Canas, Laura; del Mar de la Hoz-caballero, Maria; Meneghini, Maria; Torres, Irina B.; Juve, Mariona; Hafkamp, Fmj; Vila, Marta; Robles, Alba G.; Buzon, Maria Jose; Toapanta, Nestor; Zuniga, Jose Miguel; Monforte, Victor; Saez-Gimenez, Berta; Len, Oscar; Arcos, Ibai Los; Miret, Enric; Ariceta, Gema; Pardo, Emma; Martinez, Xavier; Moreso, Francesc; Bestard, Oriol 分享 收藏
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Favorable Outcome After Single-kidney Transplantation From Small Donors in Children: A Match-controlled CERTAIN Registry Study Schild, Raphael; Abreu, Karla Carvajal; Buescher, Anja; Kanzelmeyer, Nele; Lezius, Susanne; Krupka, Kai; Weitz, Marcus; Prytula, Agnieszka; Printza, Nikoleta; Berta, Laszlo; Saygili, Seha Kamil; Sellier-Leclerc, Anne-Laure; Sparta, Giuseppina; Marks, Stephen D.; Kemper, Markus J.; Koenig, Sabine; Topaloglu, Rezan; Mueller, Dominik; Klaus, Guenter; Weber, Stefanie; Oh, Jun; Herden, Uta; Carraro, Andrea; Dello Strologo, Luca; Ariceta, Gema; Hoyer, Peter; Toenshoff, Burkhard; Pape, Lars 分享 收藏
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Ex vivo C5b-9 Deposition Test to Monitor Complement Activity in Clinical and Subclinical Atypical Hemolytic Uremic Syndrome and in Transplantation-Associated Thrombotic Microangiopathy Martin, Maria; Llorens-Cebria, Carmen; Leon-Roman, Juan; Perurena-Prieto, Janire; Perez-Beltran, Victor; Saumell, Silvia; Torres, Irina B.; Agraz, Irene; Sellares, Joana; Ramos, Natalia; Bestard, Oriol; Lopez, Mercedes; Moreso, Francesc; Ariceta, Gema; Soler, Maria Jose; Hernandez-Gonzalez, Manuel; Jacobs-Cacha, Conxita 分享 收藏
Real-world non-interventional post-authorization safety study of long-term use of burosumab in children and adolescents with X-linked hypophosphatemia: first interim analysis Boot, Annemieke M.; Ariceta, Gema; Beck-Nielsen, Signe Sparre; Brandi, Maria Luisa; Briot, Karine; Collantes, Carmen de Lucas; Giannini, Sandro; Haffner, Dieter; Keen, Richard; Levtchenko, Elena; Mughal, M. Zulf; Makitie, Outi; Nilsson, Ola; Schnabel, Dirk; Tripto-Shkolnik, Liana; Zillikens, M. Carola; Liu, Jonathan; Tudor, Alina; Emma, Francesco 分享 收藏
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Dilated Cardiomyopathy With Concomitant Salt-Losing Renal Tubulopathy Caused by Heterozygous RRAGD Gene Variant de Frutos, Fernando; Diez-Lopez, Carles; Garcia-Romero, Elena; Gondra, Leire; Madariaga, Leire; Ariceta, Gema; Garcia-Castano, Alejandro; Melilli, Edoardo; Herrador, Lorena; Triguero-Llonch, Laura; Gran, Ferran; Rosenfeld, Laia; Llatjos, Roger; Comin-Colet, Josep; Gonzalez-Costello, Jose 分享 收藏
Switching from immediate- to extended-release cysteamine in patients with nephropathic cystinosis: from clinical trials to clinical practice Ariceta, Gema; Santos, Fernando; Muniz, Andres Lopez; Hermida, Alvaro; Matoses, Maria Luisa; Ventura, Ana; Martin-Moreno, Paloma Leticia; Gonzalez, Esther; Acuna, Laura; Giner, Elisa; Vara, Julia 分享 收藏