未登录 Real-world evidence for coverage determination of treatments for rare diseases Dayer, Victoria W.; Drummond, Michael F.; Dabbous, Omar; Toumi, Mondher; Neumann, Peter; Tunis, Sean; Teich, Nelson; Saleh, Shadi; Persson, Ulf; von der Schulenburg, Johann-Matthias Graf; Malone, Daniel C.; Salimullah, Tay; Sullivan, Sean D. 分享 收藏
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Variation in market access decisions for cell and gene therapies across the United States, Canada, and Europe Tunis, Sean; Hanna, Eve; Neumann, Peter J.; Toumi, Mondher; Dabbous, Omar; Drummond, Michael; Fricke, Frank-Ulrich; Sullivan, Sean D.; Malone, Daniel C.; Persson, Ulf; Chambers, James D. 分享 收藏
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Social/economic costs and health-related quality of life in patients with epidermolysis bullosa in Europe Angelis, Aris; Kanavos, Panos; Lopez-Bastida, Julio; Linertova, Renata; Oliva-Moreno, Juan; Serrano-Aguilar, Pedro; Posada-de-la-Paz, Manuel; Taruscio, Domenica; Schieppati, Arrigo; Iskrov, Georgi; Brodszky, Valentin; von der Schulenburg, Johann Matthias Graf; Chevreul, Karine; Persson, Ulf; Fattore, Giovanni 分享 收藏
Social/economic costs and health-related quality of life in patients with juvenile idiopathic arthritis in Europe Kuhlmann, A.; Schmidt, T.; Treskova, M.; Lopez-Bastida, J.; Linertova, R.; Oliva-Moreno, J.; Serrano-Aguilar, P.; Posada-de-la-Paz, M.; Kanavos, P.; Taruscio, D.; Schieppati, A.; Iskrov, G.; Pentek, M.; Delgado, C.; von der Schulenburg, J. M.; Persson, U.; Chevreul, K.; Fattore, G. 分享 收藏
Social/economic costs and health-related quality of life in patients with fragile X syndrome in Europe Chevreul, Karine; Gandre, Coralie; Brigham, Karen Berg; Lopez-Bastida, Julio; Linertova, Renata; Oliva-Moreno, Juan; Serrano-Aguilar, Pedro; Posada-de-la-Paz, Manuel; Taruscio, Domenica; Schieppati, Arrigo; Iskrov, Georgi; Gulacsi, Laszlo; von der Schulenburg, Johann Matthias Graf; Kanavos, Panos; Persson, Ulf; Fattore, Giovani 分享 收藏
Social/economic costs and health-related quality of life of mucopolysaccharidosis patients and their caregivers in Europe 欧洲粘多糖贮积症患者及其护理人员的社会/经济成本和与健康相关的生活质量 Pentek, Marta; Gulacsi, Laszlo; Brodszky, Valentin; Baji, Petra; Boncz, Imre; Pogany, Gabor; Lopez-Bastida, Julio; Linertova, Renata; Oliva-Moreno, Juan; Serrano-Aguilar, Pedro; Posada-de-la-Paz, Manuel; Taruscio, Domenica; Iskrov, Georgi; Schieppati, Arrigo; von der Schulenburg, Johann Matthias Graf; Kanavos, Panos; Chevreul, Karine; Persson, Ulf; Fattore, Giovanni 分享 收藏
Social/economic costs and health-related quality of life in patients with cystic fibrosis in Europe Chevreul, Karine; Michel, Morgane; Brigham, Karen Berg; Lopez-Bastida, Julio; Linertova, Renata; Oliva-Moreno, Juan; Serrano-Aguilar, Pedro; Posada-de-la-Paz, Manuel; Taruscio, Domenica; Schieppati, Arrigo; Iskrov, Georgi; Pentek, Marta; von der Schulenburg, Johann Matthias Graf; Kanavos, Panos; Persson, Ulf; Fattore, Giovani 分享 收藏
Social/economic costs and quality of life in patients with haemophilia in Europe Cavazza, Marianna; Kodra, Yllka; Armeni, Patrizio; De Santis, Marta; Lopez-Bastida, Julio; Linertova, Renata; Oliva-Moreno, Juan; Serrano-Aguilar, Pedro; Posada-de-la-Paz, Manuel; Taruscio, Domenica; Schieppati, Arrigo; Iskrov, Georgi; Gulacsi, Laszlo; Schulenburg, Johann Matthias Graf von der; Kanavos, Panos; Chevreul, Karine; Persson, Ulf; Fattore, Giovanni 分享 收藏