未登录 Supporting development of novel brain tumour therapies through global collaboration: early insights from a novel therapeutics accelerator 通过全球合作支持新型脑瘤疗法的开发:来自新型疗法加速器的早期见解 Aitken, Charlotte; Bushby, Katie; Goetz, Camille; Huskens, Nicky; Noble, Karen; Hamerlik, Petra; Kaye, Edward; Kobayashi, Dione; Matthew, Ryan; Nazarian, Javad; Plummer, Ruth; Rahman, Ruman; Romero, Artie; Lopez, Juanita; Nagaraju, Kanneboyina 分享 收藏
Exposure-response of serum biomarkers to vamorolone, a dissociative corticosteroidal anti-inflammatory drug, in 4-to <7-year children vamorolone(一种解离性皮质类固醇抗炎药)对4至<7岁儿童血清生物标志物的暴露-反应关系 Mummidivarpu, Swati; Dang, Utkarsh J.; Ziemba, Michael; Hathout, Yetrib; Clemens, Paula R.; Damsker, Jesse; Hagerty, Laura; Jusko, William J.; Smith, Edward C.; Mah, Jean K.; Guglieri, Michela; Nevo, Yoram; Kuntz, Nancy; Mcdonald, Craig M.; Ryan, Monique M.; Castro, Diana; Finkel, Richard S.; Conklin, Laurie S.; Mccall, John M.; Nagaraju, Kanneboyina; Van Den Anker, John; Hoffman, Eric P. 分享 收藏
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Enhancing AAV-microdystrophin gene therapy after repeat dosing by blocking phagocytosis (vol 16, 1527840, 2025) 通过阻断吞噬作用增强AAV-microdystrophin基因疗法在重复给药后的效果(vol 16, 1527840, 2025) Spathis, Rita; Kuriplach, Deeva Robles; Narvesen, Sabrina; Eybs, Matthew; Huang, Karen; Torres, Steven; King, Madison; Bagley, Elizabeth; Elustondo, Pia; Lawlor, Michael W.; Nagaraju, Kanneboyina; Morales, Melissa 分享 收藏
The effect of IL-1β inhibitor canakinumab (Ilaris®) on IL-6 production in human skeletal muscle cells IL-1β抑制剂canakinumab (Ilaris®) 对人骨骼肌细胞中IL-6产生的影响 Cordeiro-Santanach, Anna; Morales, Fiorella; Parquet, Maria del Carmen; Uaesoontrachoon, Kitipong; Rowsell, Joyce; Warford, Jordan; Wu, Wilson; Elustondo, Pia; Hoffman, Eric P.; Nagaraju, Kanneboyina 分享 收藏
Enhancing AAV-microdystrophin gene therapy after repeat dosing by blocking phagocytosis Spathis, Rita; Kuriplach, Deeva Robles; Narvesen, Sabrina; Eybs, Matthew; Huang, Karen; Torres, Steven; King, Madison; Bagley, Elizabeth; Elustondo, Pia; Lawlor, Michael W.; Nagaraju, Kanneboyina; Morales, Melissa 分享 收藏
AN INTERNATIONAL ACCELERATOR PROGRAMME FOR RESEARCHERS DEVELOPING NOVEL THERAPIES FOR BRAIN TUMOURS Aitken, Charlotte; Huskens, Nicky; Bushby, Katie; Noble, Karen; Hamerlik, Petra; Kaye, Edward; Kobayashi, Dione; Mathew, Ryan; Mccall, John; Nazarian, Javad; Plummer, Ruth; Rahman, Ruman; Lopez, Juanita; Nagaraju, Kanneboyina 分享 收藏
A NEW INTERNATIONAL, MULTIDISCIPLINARY ACCELERATOR PROGRAMME FOR NOVEL BRAIN TUMOUR THERAPIES Aitken, Charlotte; Huskens, Nicky; Bushby, Katie; Noble, Karen; Hamerlik, Petra; Kaye, Edward; Kobayashi, Dione; Matthew, Ryan; McCall, John; Nazarian, Javad; Plummer, Ruth; Rahman, Ruman; Lopez, Juanita; Nagaraju, Kanneboyina 分享 收藏
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Mechanism of action and therapeutic route for a muscular dystrophy caused by a genetic defect in lipid metabolism Tavasoli, Mahtab; Lahire, Sarah; Sokolenko, Stanislav; Novorolsky, Robyn; Reid, Sarah Anne; Lefsay, Abir; Otley, Meredith O. C.; Uaesoontrachoon, Kitipong; Rowsell, Joyce; Srinivassane, Sadish; Praest, Molly; MacKinnon, Alexandra; Mammoliti, Melissa Stella; Maloney, Ashley Alyssa; Moraca, Marina; Fernandez-Murray, J. Pedro; McKenna, Meagan; Sinal, Christopher J.; Nagaraju, Kanneboyina; Robertson, George S.; Hoffman, Eric P.; McMaster, Christopher R. 分享 收藏
A mouse model of inherited choline kinase β-deficiency presents with specific cardiac abnormalities and a predisposition to arrhythmia Tavasoli, Mahtab; Feridooni, Tiam; Feridooni, Hirad; Sokolenko, Stanislav; Mishra, Abhishek; Lefsay, Abir; Srinivassane, Sadish; Reid, Sarah Anne; Rowell, Joyce; Praest, Molly; MacKinnon, Alexandra; Mammoliti, Melissa; Maloney, Ashley Alyssa; Moraca, Marina; Uaesoontrachoon, Kitipong P.; Nagaraju, Kanneboyina R.; Hoffman, Eric; Pasumarthi, Kishore B. S.; McMaster, Christopher 分享 收藏
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Effects of Chronic, Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy Klimek, Margaret E. Benny; Vila, Maria Candida; Edwards, Katie; Boehler, Jessica; Novak, James; Zhang, Aiping; Van der Meulen, Jack; Tatum, Kathleen; Quinn, James; Fiorillo, Alyson; Burki, Umar; Straub, Volker; Lu, Qi Long; Hathout, Yetrib; van Den Anker, John; Partridge, Terence A.; Morales, Melissa; Hoffman, Eric; Nagaraju, Kanneboyina 分享 收藏
The Effect of Immunomodulatory Treatments on Anti-Dystrophin Immune Response After AAV Gene Therapy in Dystrophin Deficient mdx Mice Li, Ning; Parkes, Joanna E.; Spathis, Rita; Morales, Melissa; Mcdonald, John; Kendra, Ryan M.; Ott, Emily M.; Brown, Kristy J.; Lawlor, Michael W.; Nagaraju, Kanneboyina 分享 收藏
Interrogation of Dystrophin and Dystroglycan Complex Protein Turnover After Exon Skipping Therapy Novak, James S.; Spathis, Rita; Dang, Utkarsh J.; Fiorillo, Alyson A.; Hindupur, Ravi; Tully, Christopher B.; Mazala, Davi A. G.; Canessa, Emily; Brown, Kristy J.; Partridgea, Terence A.; Hathout, Yetrib; Nagaraju, Kanneboyina 分享 收藏
Validation of Chemokine Biomarkers in Duchenne Muscular Dystrophy Ogundele, Michael; Zhang, Jesslyn S.; Goswami, Mansi, V; Barbieri, Marissa L.; Dang, Utkarsh J.; Novak, James S.; Hoffman, Eric P.; Nagaraju, Kanneboyina; Hathout, Yetrib 分享 收藏
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