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收藏Use of 2,6-diaminopurine as a potent suppressor of UGA premature stop codons in cystic fibrosis
Leroy, Catherine; Spelier, Sacha; Essonghe, Nadege Charlene; Poix, Virginie; Kong, Rebekah; Gizzi, Patrick; Bourban, Claire; Amand, Severine; Bailly, Christine; Guilbert, Romain; Hannebique, David; Persoons, Philippe; Arhant, Gwenaelle; Prevotat, Anne; Reix, Philippe; Hubert, Dominique; Gerardin, Michele; Chamaillard, Mathias; Prevarskaya, Natalia; Rebuffat, Sylvie; Shapovalov, George; Beekman, Jeffrey; Lejeune, Fabrice
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收藏Safety and pharmacokinetics of Roscovitine (Seliciclib) in cystic fibrosis patients chronically infected with Pseudomonas aeruginosa, a randomized, placebo-controlled study
Meijer, Laurent; Hery-Arnaud, Genevieve; Leven, Cyril; Nowak, Emmanuel; Hillion, Sophie; Renaudineau, Yves; Durieu, Isabelle; Chiron, Raphael; Prevotat, Anne; Fajac, Isabelle; Hubert, Dominique; Murris-Espin, Marlene; Huge, Sandrine; Danner-Boucher, Isabelle; Ravoninjatovo, Bruno; Leroy, Sylvie; Macey, Julie; Urban, Thierry; Rault, Gilles; Mottier, Dominique; Le Berre, Rozenn
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收藏Il faut continuer a poser des questions patient reported outcome measures in cystic fibrosis: An anthropological perspective
Coucke, Rosa; Chansard, Audrey; Bontemps, Veronique; Grenet, Dominique; Hubert, Dominique; Martin, Clemence; Lammertyn, Elise; Bardin, Emmanuelle; Bulteel, Veerle; Chedevergne, Frederique; Le Bourgeois, Muriel; Burgel, Pierre-Regis; Honore, Isabelle; de Keyser, Hilde; Kirszenbaum, Maya; de Carli, Paola; Sermet-Gaudelus, Isabelle; Hayes, Kate; Bend, Jutta; Bresnihan, Claire; Calvert, Anne; Fonts, Anna; Hager, Andreas; Hautrive, Maxime; Havermans, Trudy; Hofmann, Diana
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收藏Clinical response to lumacaftor-ivacaftor in patients with cystic fibrosis according to baseline lung function
Burgel, Pierre-Regis; Durieu, Isabelle; Chiron, Raphael; Mely, Laurent; Prevotat, Anne; Murris-Espin, Marlene; Porzio, Michele; Abely, Michel; Reix, Philippe; Marguet, Christophe; Macey, Julie; Sermet-Gaudelus, Isabelle; Corvol, Harriet; Bui, Stephanie; Biouhee, Tiphaine; Hubert, Dominique; Munck, Anne; Lemonnier, Lydie; Dehillotte, Clemence; Da Silva, Jennifer; Paillasseur, Jean-Louis; Martin, Clemence
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收藏Real-Life Safety and Effectiveness of Lumacaftor-Ivacaftor in Patients with Cystic Fibrosis
Burgel, Pierre-Regis; Munck, Anne; Durieu, Isabelle; Chiron, Raphael; Mely, Laurent; Prevotat, Anne; Murris-Espin, Marlene; Porzio, Michele; Abely, Michel; Reix, Philippe; Marguet, Christophe; Macey, Julie; Sermet-Gaudelus, Isabelle; Corvol, Harriet; Bui, Stephanie; Lemonnier, Lydie; Dehillotte, Clemence; Da Silva, Jennifer; Paillasseur, Jean-Louis; Hubert, Dominique; Mounard, Julie; Poulet, Claire; Rames, Cinthia; Person, Christine; Troussier, Francoise; Urban, Thierry; Dalphin, Marie-Laure; Dalphin, Jean-Claude; Pernet, Didier; Richaud-Thiriez, Benedicte; Fayon, Mickael; Macey-Caro, Julie; Campbell, Karine; Laurans, Muriel; Borderon, Corinne; Heraud, Marie-Christine; Labbe, Andre; Montcouquiol, Sylvie; Bassinet, Laurence; Remus, Natascha; Fanton, Annlyse; Houzel-Charavel, Anne; Huet, Frederic; Perez-Martin, Stephanie; Boldron-Ghaddar, Amale; Scalbert, Manuela; Camara, Boubou; Llerena, Catherine; Pin, Isabelle; Quetant, Sebastien; Cottereau, Aurelie; Deschildre, Antoine; Gicquello, Alice; Perez, Thierry; Stervinou-Wemeau, Lidwine; Thumerelle, Caroline; Wallaert, Benoit; Wizla, Nathalie; Languepin, Jane; Menetrey, Celine; Dupuy-Grasset, Magalie; Bazus, Lucie; Buchs, Clelia; Jubin, Virginie; Werck-Gallois, Marie-Christine; Mainguy, Catherine; Perrin, Thomas; Toutain-Rigolet, Agnes; Durupt, Stephane; Reynaud, Quitterie; Nove-Josserand, Raphaele; Baravalle-Einaudi, Melisande; Coltey, Berangere; Dufeu, Nadine; Dubus, Jean-Christophe; Stremler, Nathalie; Caimmi, Davide; Billon, Yves; Derelle, Jocelyne; Kieffer, Sebastien; Pichon, Anne-Sophie; Schweitzer, Cyril; Tatopoulos, Aurelie; Abbes, Sarah; Bihouee, Tiphaine; Danner-Boucher, Isabelle; David, Valerie; Haloun, Alain; Tissot, Adrien; Leroy, Sylvie; Bailly-Piccini, Carole; Clement, Annick; Tamalet, Aline; Honore, Isabelle; Kanaan, Reem; Martin, Clemence; Bailly, Cecile; Chedevergne, Frederique; De Blic, Jacques; Fauroux, Brigitte; Le Bourgeois, Murielle; Delaisi, Bertrand; Gerardin, Michele; Ravoninjatovo, Bruno; Belleguic, Chantal; Desrues, Benoit; Brinchault, Graziella; Dagorne, Michel; Deneuville, Eric; Lefeuvre, Sylvaine; Dirou, Anne; Le Bihan, Jean; Ramel, Sophie; Dominique, Stephane; Payet, Annabelle; Kessler, Romain; Rosner, Vincent; Weiss, Laurence; de Miranda, Sandra; Grenet, Dominique; Hamid, Abdoul; Picard, Clement; Bremont, Francois; Didier, Alain; Labouret, Geraldine; Mittaine, Marie; Tetu, Laurent; Cosson, Laure; Giraut, Charlotte; Henriet, Anne-Cecile; Mankikian, Julie; Marchand, Sophie; Huge, Sandrine; Storni, Veronique; CoMer-Duet, Emmanuelle
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收藏AN OBSERVATIONAL STUDY OF IVACAFTOR IN PATIENTS WITH CYSTIC FIBROSIS IN FRANCE: FIRST INTERIM ANALYSIS OF HEALTH CARE RESOURCE UTILIZATION FROM THE BRIO STUDY
Hubert, D.; Fajac, I; Munck, A.; Marguet, C.; Benichou, J.; Payen-Champenois, C.; Jha, L.; Hassan, M.; DeSouza, C.; Kinnman, N.
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收藏Retrospective observational study of French patients with cystic fibrosis and a G1y551Asp-CFTR mutation after 1 and 2 years of treatment with ivacaftor in a real-world setting
Hubert, Dominique; Dehillotte, Clemence; Munck, Anne; David, Valerie; Baek, Jinmi; Mely, Laurent; Dominique, Stephane; Ramel, Sophie; Boucher, Isabelle Danner; Lefeuvre, Sylvaine; Reynaud, Quitterie; Colomb-Jung, Virginie; Bakouboula, Prissile; Lemonnier, Lydie
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收藏Real-life initiation of lumacaftor/ivacaftor combination in adults with cystic fibrosis homozygous for the Phe508del CFTR mutation and severe lung disease
Hubert, Dominique; Chiron, Raphael; Camara, Boubou; Grenet, Dominique; Prevotat, Anne; Bassinet, Laurence; Dominique, Stephane; Rault, Gilles; Macey, Julie; Honore, Isabelle; Kanaan, Reem; Leroy, Sylvie; Dufeu, Nadine Desmazes; Burgel, Pierre-Regis
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收藏Causes of death in French cystic fibrosis patients: The need for improvement in transplantation referral strategies!
Martin, Clemence; Hamard, Cecile; Kanaan, Reem; Boussaud, Veronique; Grenet, Dominique; Abely, Michel; Hubert, Dominique; Munck, Anne; Lemonnier, Lydie; Burgel, Pierre-Regis
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收藏Lessons from a French collaborative case-control study in cystic fibrosis patients during the 2009 A/H1N1 influenza pandemy
Bucher, Julie; Boelle, Pierre-Yves; Hubert, Dominique; Lebourgeois, Muriel; Stremler, Nathalie; Durieu, Isabelle; Bremont, Francois; Deneuville, Eric; Delaisi, Bertrand; Corvol, Harriet; Bassinet, Laurence; Grenet, Dominique; Remus, Natacha; Vodoff, Marie Veronique; Boussaud, Veronique; Troussier, Francoise; Leruez-Ville, Marianne; Treluyer, Jean-Marc; Launay, Odile; Sermet-Gaudelus, Isabelle
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收藏Reduced risk of nontuberculous mycobacteria in cystic fibrosis adults receiving long-term azithromycin
Coolen, Nathalie; Morand, Philippe; Martin, Clemence; Hubert, Dominique; Kanaan, Reem; Chapron, Jeanne; Honore, Isabelle; Dusser, Daniel; Audureau, Etienne; Veziris, Nicolas; Burgel, Pierre-Regis
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收藏Pregnancies After Lung Transplantation: A Retrospective Multicenter French Study About 39 Pregnancies
Bry, C.; Hubert, D.; Reynaud-Gaubert, M.; Dromer, C.; Mal, H.; Grenet, D.; Boussaud, V.; Claustre, J.; Le Pavec, J.; Murris-Espin, M.; Danner-Boucher, I.
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收藏Central venous thrombosis and thrombophilia in cystic fibrosis: A prospective study
Munck, Anne; Kheniche, Ahmed; Alberti, Corinne; Hubert, Dominique; Reynaud-Gaubert, Martine; Nove-Josserand, Raphaele; Pin, Isabelle; Bremont, Francois; Chiron, Raphael; Couderc, Laure; Dalphin, Marie Laure; Darviot, Estelle; Delaisi, Bertrand; Dominique, Stephane; Durieu, Isabelle; Fanton, Annelyse; Fayon, Michael; Gerardin, Michele; Ginies, Jean-Louis; Giraut, Charlotte; Grenet, Dominique; Guillot, Marcel; Huet, Frederic; Le Bourgeois, Muriel; Murris-Epin, Marlene; Ramel, Sophie; Sardet, Anne; Sermet-Gaudelus, Isabelle; Varaigne, Francoise; Wanin, Stephanie; Weiss, Laurence; Hurtaud, Marie-Francoise
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