Ryszard Kole - Publications, H-index & Citations

Ryszard Kole

mahidol university

52H指数

170论文数

1.1W被引数

收录论文 36

发表时间

Enhanced delivery of peptide-morpholino oligonucleotides with a small molecule to correct splicing defects in the lung

NUCLEIC ACIDS RESEARCH

IF13.1

2021-06-09

OAAI

Dang, Yan; van Heusden, Catharina; Nickerson, Veronica; Chung, Felicity; Wang, Yang; Quinney, Nancy L.; Gentzsch, Martina; Randell, Scott H.; Moulton, Hong M.; Kole, Ryszard; Ni, Aiguo; Juliano, Rudolph L.; Kreda, Silvia M.

A targeted antisense therapeutic approach for Hutchinson-Gilford progeria syndrome

NATURE MEDICINE

IF50

2021-03-11

OAAI

Erdos, Michael R.; Cabral, Wayne A.; Tavarez, Urraca L.; Cao, Kan; Gvozdenovic-Jeremic, Jelena; Narisu, Narisu; Zerfas, Patricia M.; Crumley, Stacy; Boku, Yoseph; Hanson, Gunnar; Mourich, Dan V.; Kole, Ryszard; Eckhaus, Michael A.; Gordon, Leslie B.; Collins, Francis S.

Restoration of correct βIVS2-654-globin mRNA splicing and HbA production by engineered U7 snRNA in β-thalassaemia/HbE erythroid cells

SCIENTIFIC REPORTS

IF3.9

2019-05-21

OAAI

Nualkaew, Tiwaporn; Jearawiriyapaisarn, Natee; Hongeng, Suradej; Fucharoen, Suthat; Kole, Ryszard; Svasti, Saovaros

Effects of systemic multiexon skipping with peptide-conjugated morpholinos in the heart of a dog model of Duchenne muscular dystrophy

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

IF9.1

2017-04-03

OAAI

Echigoya, Yusuke; Nakamura, Akinori; Nagata, Tetsuya; Urasawa, Nobuyuki; Lim, Kenji Rowel Q.; Trieu, Nhu; Panesar, Dharminder; Kuraoka, Mutsuki; Moulton, Hong M.; Saito, Takashi; Aoki, Yoshitsugu; Iversen, Patrick; Sazani, Peter; Kole, Ryszard; Maruyama, Rika; Partridge, Terry; Takeda, Shin'ichi; Yokota, Toshifumi

Self-aggregating 1.8 kDa polyethylenimines with dissolution switch at endosomal acidic pH are delivery carriers for plasmid DNA, mRNA, siRNA and exon-skipping oligonucleotides

JOURNAL OF CONTROLLED RELEASE

IF11.5

2017-01-01

OAAI

Chiper, Manuela; Tounsi, Nassera; Kole, Ryszard; Kichler, Antoine; Zuber, Guy

RNA therapeutics: beyond RNA interference and antisense oligonucleotides RNA治疗: 超越RNA干扰和反义寡核苷酸

NATURE REVIEWS DRUG DISCOVERY

IF101.8

2012-01-20

1.1K

OAAI

Kole, Ryszard; Krainer, Adrian R.; Altman, Sidney

Targeted Exon Skipping to Address Leaky Mutations in the Dystrophin Gene

MOLECULAR THERAPY-NUCLEIC ACIDS

IF0

2012-01-01

OAAI

Fletcher, Sue; Adkin, Carl F.; Meloni, Penny; Wong, Brenda; Muntoni, Francesco; Kole, Ryszard; Fragall, Clayton; Greer, Kane; Johnsen, Russell; Wilton, Steve D.

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

LANCET

IF88.5

2011-08-01

810

OAAI

Cirak, Sebahattin; Arechavala-Gomeza, Virginia; Guglieri, Michela; Feng, Lucy; Torelli, Silvia; Anthony, Karen; Abbs, Stephen; Garralda, Maria Elena; Bourke, John; Wells, Dominic J.; Dickson, George; Wood, Matthew J. A.; Wilton, Steve D.; Straub, Volker; Kole, Ryszard; Shrewsbury, Stephen B.; Sewry, Caroline; Morgan, Jennifer E.; Bushby, Kate; Muntoni, Francesco

Anti-tumor activity of splice-switching oligonucleotides

NUCLEIC ACIDS RESEARCH

IF13.1

2010-08-18

123

OAAI

Bauman, John A.; Li, Shyh-Dar; Yang, Angela; Huang, Leaf; Kole, Ryszard

Prevention of Dystrophic Pathology in Severely Affected Dystrophin/Utrophin-deficient Mice by Morpholino-oligomer-mediated Exon-skipping

MOLECULAR THERAPY

IF12

2010-01-01

OAAI

Goyenvalle, Aurelie; Babbs, Arran; Powell, Dave; Kole, Ryszard; Fletcher, Sue; Wilton, Steve D.; Davies, Kay E.

Long-term improvement in mdx cardiomyopathy after therapy with peptide-conjugated morpholino oligomers

CARDIOVASCULAR RESEARCH

IF13.3

2009-10-08

OAAI

Jearawiriyapaisarn, Natee; Moulton, Hong M.; Sazani, Peter; Kole, Ryszard; Willis, Monte S.

Peptide-Morpholino Conjugate: A Promising Therapeutic for Duchenne Muscular Dystrophy

OLIGONUCLEOTIDE THERAPEUTICS

IF0

2009-09-24

PREAI

Moulton, Hong M.; Wu, Bo; Jearawiriyapaisarn, Natee; Sazani, Peter; Lu, Qi Long; Kole, Ryszard

RNA repair restores hemoglobin expression in IVS2-654 thalassemic mice RNA修复恢复IVS2-654地中海贫血小鼠的血红蛋白表达

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

IF9.1

2009-01-27

OAAI

Svasti, Saovaros; Suwanmanee, Thipparat; Fucharoen, Suthat; Moulton, Hong M.; Nelson, Michelle H.; Maeda, Nobuyo; Smithies, Oliver; Kole, Ryszard

Correction of a splice-site mutation in the beta-globin gene stimulated by triplex-forming peptide nucleic acids

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

IF9.1

2008-09-09

OAAI

Chin, Joanna Y.; Kuan, Jean Y.; Lonkar, Pallavi S.; Krause, Diane S.; Seidman, Michael M.; Peterson, Kenneth R.; Nielsen, Peter E.; Kole, Ryszard; Glazer, Peter M.

Sustained dystrophin expression induced by peptide-conjugated morpholino oligomers in the muscles of mdx mice

MOLECULAR THERAPY

IF12

2008-09-01

304

OAAI

Jearawiriyapaisarn, Natee; Moulton, Hong M.; Buckley, Brian; Roberts, Jennifer; Sazani, Peter; Fucharoen, Suthat; Iversen, Patrick L.; Kole, Ryszard

An endogenous TNF-α antagonist induced by splice-switching oligonucleotides reduces inflammation in hepatitis and arthritis mouse models

MOLECULAR THERAPY

IF12

2008-07-01

OAAI

Graziewicz, Maria A.; Tarrant, Teresa K.; Buckley, Brian; Roberts, Jennifer; Fulton, LeShara; Hansen, Henrik; Orum, Henrik; Kole, Ryszard; Sazani, Peter

The importance of Bcl-XL in the survival of human RPE cells

INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE

IF4.7

2007-08-01

PREAI

Zhang, Nanfei; Peairs, James J.; Yang, Ping; Tyrrell, Jillian; Roberts, Jennifer; Kole, Ryszard; Jaffe, Glenn J.

Switching on transgene expression by correcting aberrant splicing using multi-targeting steric-btocking oligonucleotides 通过使用多靶向空间位阻寡核苷酸纠正异常剪接来切换转基因表达

JOURNAL OF GENE MEDICINE

IF2.2

2007-05-01

PREAI

Resina, Sarah; Kole, Ryszard; Travo, Adrian; Lebleul, Bernard; Thierry, Alain R.