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收藏Late-onset metachromatic leukodystrophy - Genotype strongly influences phenotype
Rauschka, H.; Colsch, B.; Baumann, N.; Wevers, R.; Schmidbauer, M.; Krammer, M.; Turpin, J. -C.; Lefevre, M.; Olivier, C.; Tardieu, S.; Krivit, W.; Moser, H.; Moser, A.; Gieselmann, V.; Zalc, B.; Cox, T.; Reuner, U.; Tylki-Szymanska, A.; Aboul-Enein, F.; LeGuern, E.; Bernheimer, H.; Berger, J.
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收藏Transplantation of umbilical-cord blood in babies with infantile Krabbe's disease
Escolar, ML; Poe, MD; Provenzale, JM; Richards, KC; Allison, J; Wood, S; Wenger, DA; Pietryga, D; Wall, D; Champagne, M; Morse, R; Krivit, W; Kurtzberg, J
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收藏Cord-blood transplants from unrelated donors in patients with Hurler's syndrome
Staba, SL; Escolar, ML; Poe, M; Kim, Y; Martin, PL; Szabolcs, P; Allison-Thacker, J; Wood, S; Wenger, DA; Rubinstein, P; Hopwood, JJ; Krivit, W; Kurtzberg, J
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收藏Effective treatment of α-mannosidosis by allogeneic hematopoietic stem cell transplantation
Grewal, SS; Shapiro, EG; Krivit, W; Charnas, L; Lockman, LA; Delaney, KA; Davies, SM; Wenger, DA; Rimell, FL; Abel, S; Grovas, AC; Orchard, PJ; Wagner, JE; Peters, C
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收藏Long-term effect of bone-marrow transplantation for childhood-onset cerebral X-linked adrenoleukodystrophy
Shapiro, E; Krivit, W; Lockman, L; Jambaqué, I; Peters, C; Cowan, M; Harris, R; Blanche, S; Bordigoni, P; Loes, D; Ziegler, R; Crittenden, M; Ris, D; Berg, B; Cox, C; Moser, H; Fischer, A; Aubourg, P
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