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J

Joanne Kurtzberg

duke university

94H指数
672论文数
3.1W被引数
收录论文 136
发表时间
Regulating the Unviable: A Call to FDA for a Rare Biologic Limited Approval (RBLA) Pathway监管不可行性:呼吁FDA设立罕见生物制剂有限批准(RBLA)途径
err2026-08-28
err0
PREAI
errKevin Bosse; Patrick J. Hanley; Joanna Kurtzberg; Olive Sturtevant; Emily Hopewell; Rebecca Gardner; Bambi J. Grilley
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Autologous stem cell transplant for severe, progressive juvenile systemic sclerosis自体干细胞移植治疗严重、进展性青少年系统性硬化症
err2026-04-01
err0
PREAI
errAlqahtani, Shaikha; Cacace, Fabiana; Bauchat, Andrea; DePriest, Brittany Paige; Driscoll, Timothy Alan; Bonfim, Carmem; Kurtzberg, Joanne; Larrier, Nicole; Dvergsten, Jeffery; Mahadeo, Kris Michael
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Reconstitution of thymopoiesis via implantation of cryopreserved cultured thymus tissue into athymic recipients通过将冻存培养的胸腺组织植入无胸腺受者来重建胸腺生成。
err2025-11-13
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PREAI
errLaura P. Hale; Dawn E. Bowles; Jie Li; Andrew N. Macintyre; NiDajah Bolden; Joanne Kurtzberg; Cathlyn K. Medina; Berk Aykut; Elisabeth T. Tracy; Joseph W. Turek
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Defining minimal criteria for peer-reviewed reporting of mesenchymal stromal cell clinical trials for autoimmune diseases定义间充质基质细胞治疗自身免疫性疾病临床试验同行评审报告的最小标准
err2025-07-12
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errOAAI
errLindsay C. Davies; Lucie Biard; Damián García-Olmo; Gary Gilkeson; Massimiliano Gnecchi; Joanne Kurtzberg; Gesine Kogler; Katarina Le Blanc; Mark W. Lowdell; Yves-Marie Pers; Ling-yun Sun; Karin Tarte; Antonio Uccelli; Fermin Sanchez-Guijo; Dominique Farge
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Donor-specific mesenchymal stem cell infusion in human and nonhuman primate kidney transplantation供者特异性间充质干细胞输注在人类和非人灵长类动物肾移植中的应用
err2025-05-12
err0
PREAI
errImran J. Anwar; Shu Li; Michael Mulvihill; Robin Schmitz; Brian Shaw; Qimeng Gao; Sherri Swan-Nesbit; Lynn A. Cheatham; Tam How; Allison Miller; Kyha Williams; Fang-Fang Yin; William Giles; Joanne Kurtzberg; Sindhu Chandran; Nancy Bridges; Lyudmila Lyakh; Cynthia Breeden; Krupa Gandhi; Michelle Sever; Mingqing Song; Xu He; Allan D. Kirk
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Newborn Screening for Hurler Syndrome Facilitates Early Transplant and Good Outcomes
err2025-02-01
err0
PREAI
errBauchat, Andrea; Stokhuyzen, Andre; Driscoll, Timothy A.; Martin, Paul L.; Kurtzberg, Joanne; Mahadeo, Kris M.; Prasad, Vinod K.
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Safety and feasibility of umbilical cord blood transplantation in children with neuronal ceroid lipofuscinosis: a retrospective study
err2024-10-29
err0
errOAAI
errBauchat, Andrea; Polishchuk, Veronika; Fabrizio, Vanessa A.; Brondon, Jennifer E.; Page, Kristin M.; Driscoll, Timothy A.; Martin, Paul L.; Mahadeo, Kris M.; Kurtzberg, Joanne; Prasad, Vinod K.
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Mitigation of supply chain challenges in cell therapy manufacturing: perspectives from the cord blood alliance
err2024-07-29
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errOAAI
errKillela, Patrick; Herrity, Kieran; Frontier, Ludwig; Horton, Roger; Kurtzberg, Joanne; Vant Hof, Wouter
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Newborn Screening for Krabbe Disease and Identification of Minority PatientsKrabbe病的新生儿筛查及少数民族患者的鉴定
err2024-02-01
err3
PREAI
errBonkowsky, Joshua L.; Wilkes, Jacob; Baker, Monika; Grantham, Anna; Kurtzberg, Joanne; Orsini, Joseph
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Mesenchymal stromal cells suppress microglial activation and tumor necrosis factor production
err2024-02-01
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PREAI
errXu, Li; Min, Hyunjung; Saha, Arjun; Gunaratne, Aruni; Schwartzman, Jonathan; Parrott, Roberta; Kurtzberg, Joanne; Filiano, Anthony J.
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Neurodevelopmental outcomes of hematopoietic stem cell transplantation for infantile Krabbe disease diagnosed through newborn screening
err2024-02-01
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PREAI
errKurtzberg, Joanne; Rangarajan, Hemalatha G.; Rubin, Jennifer P.; Arbuckle, Erin; West, Tara; Ream, Margie; Shenoy, Shalini; Gustafson, Katie
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Newborn screening for Krabbe disease: Status quo and recommendations for improvements
err2024-02-01
err0
PREAI
errMatern, Dietrich; Basheeruddin, Khaja; Klug, Tracy; McKee, Gwendolyn; Edge, Patricia; Kurtzberg, Joanne; Hall, Patricia; Orsini, Joseph J.
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Newborn Screening for Krabbe Disease: Status Quo and Recommendations for ImprovementsKrabbe病的新生儿筛查: 现状和改进建议
err2024-01-28
err2
errOAAI
errMatern, Dietrich; Basheeruddin, Khaja; Klug, Tracy L.; McKee, Gwendolyn; Edge, Patricia U.; Hall, Patricia L.; Kurtzberg, Joanne; Orsini, Joseph J.
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Mural cells interact with macrophages in the dura mater to regulate CNS immune surveillance
err2024-01-09
err3
errOAAI
errMin, Hyunjung; O'Neil, Shane M.; Xu, Li; Moseman, E. Ashley; Kurtzberg, Joanne; Filiano, Anthony J.
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Cell-based versus corticosteroid injections for knee pain in osteoarthritis: a randomized phase 3 trial (vol 29, pg 3120, 2023)
err2023-12-22
err1
errOAAI
errMautner, Ken; Gottschalk, Michael; Boden, Scott D.; Akard, Alison; Bae, Won C.; Black, Lora; Boggess, Blake; Chatterjee, Paramita; Chung, Christine B.; Easley, Kirk A.; Gibson, Greg; Hackel, Josh; Jensen, Katie; Kippner, Linda; Kurtenbach, Chad; Kurtzberg, Joanne; Mason, R. Amadeus; Noonan, Benjamin; Roy, Krishnendu; Valentine, Verle; Yeago, Carolyn; Drissi, Hicham
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A Randomized, Placebo-Controlled, Phase II Trial of Intravenous Allogeneic Non-HLA Matched, Unrelated Donor, Cord Blood Infusion for Ischemic Stroke
err2023-12-10
err4
errOAAI
errLaskowitz, Daniel T.; Troy, Jesse; Poehlein, Emily; Bennett, Ellen R.; Shpall, Elizabeth J.; Wingard, John R.; Freed, Brian; Belagaje, Samir R.; Khanna, Anna; Jones, William; Volpi, John J.; Marrotte, Eric; Kurtzberg, Joanne
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Cell-based versus corticosteroid injections for knee pain in osteoarthritis: a randomized phase 3 trial
err2023-11-02
err26
errOAAI
errMautner, Ken; Gottschalk, Michael; Boden, Scott D.; Akard, Alison; Bae, Won C.; Black, Lora; Boggess, Blake; Chatterjee, Paramita; Chung, Christine B.; Easley, Kirk A.; Gibson, Greg; Hackel, Josh; Jensen, Katie; Kippner, Linda; Kurtenbach, Chad; Kurtzberg, Joanne; Mason, R. Amadeus; Noonan, Benjamin; Roy, Krishnendu; Valentine, Verle; Yeago, Carolyn; Drissi, Hicham
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A Pilot Phase I Trial of Allogeneic Umbilical Cord Tissue-Derived Mesenchymal Stromal Cells in Neonates With Hypoxic-Ischemic Encephalopathy
err2023-06-15
err17
errOAAI
errCotten, Charles Michael; Fisher, Kimberley; Malcolm, William; Gustafson, Kathryn E.; Cheatham, Lynn; Marion, Amanda; Greenberg, Rachel; Kurtzberg, Joanne
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Multicenter Long-Term Follow-Up of Allogeneic Hematopoietic Cell Transplantation with Omidubicel: A Pooled Analysis of Five Prospective Clinical Trials异基因造血干细胞移植与omiudubicel的多中心长期随访: 五项前瞻性临床试验的汇总分析
err2023-05-01
err7
errOAAI
errLin, Chenyu; Schwarzbach, Aurelie; Sanz, Jaime; Montesinos, Pau; Stiff, Patrick; Parikha, Suhag; Brunstein, Claudio; Cutler, Corey; Lindemans, Caroline A.; Hanna, Rabi; Koh, Liang Piu; Jagasia, Madan H.; Valcarcel, David; Maziarz, Richard T.; Keating, Amy K.; Hwang, William Y. K.; Rezvani, Andrew R.; Karras, Nicole A.; Fernandes, Juliana F.; Rocha, Vanderson; Badell, Isabel; Ram, Ron; Schiller, Gary J.; Volodin, Leonid; Walters, Mark C.; Hamerschlak, Nelson; Cilloni, Daniela; Frankfurt, Olga; McGuirk, Joseph P.; Kurtzberg, Joanne; Sanz, Guillermo; Simantov, Ronit; Horwitz, Mitchell E.
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