未登录Transcriptional reprogramming restores UBE3A brain-wide and rescues behavioral phenotypes in an Angelman syndrome mouse model转录重编程在Angelman综合征小鼠模型中恢复UBE3A全脑范围并挽救行为表型
O'Geen, Henriette; Beitnere, Ulrika; Garcia, Miranda S.; Adhikari, Anna; Cameron, David L.; Fenton, Timothy A.; Copping, Nycole A.; Deng, Peter; Lock, Samantha; Halmai, Julian A. N. M.; Villegas, Isaac J.; Liu, Jiajian; Wang, Danhui; Fink, Kyle D.; Silverman, Jill L.; Segal, David J.
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收藏An in vivo Cell-Based Delivery Platform for Zinc Finger Artificial Transcription Factors in Pre-clinical Animal Models
Deng, Peter; Halmai, Julian A. N. M.; Beitnere, Ulrika; Cameron, David; Martinez, Michele L.; Lee, Charles C.; Waldo, Jennifer J.; Thongphanh, Krista; Adhikari, Anna; Copping, Nycole; Petkova, Stela P.; Lee, Ruth D.; Lock, Samantha; Palomares, Miranda; O'Geen, Henriette; Carter, Jasmine; Gonzalez, Casiana E.; Buchanan, Fiona K. B.; Anderson, Johnathan D.; Fierro, Fernando A.; Nolta, Jan A.; Tarantal, Alice F.; Silverman, Jill L.; Segal, David J.; Fink, Kyle D.
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收藏Artificial escape from XCI by DNA methylation editing of the CDKL5 gene
Halmai, Julian A. N. M.; Deng, Peter; Gonzalez, Casiana E.; Coggins, Nicole B.; Cameron, David; Carter, Jasmine L.; Buchanan, Fiona K. B.; Waldo, Jennifer J.; Lock, Samantha R.; Anderson, Johnathon D.; O'Geen, Henriette; Segal, David J.; Nolta, Jan; Fink, Kyle D.
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