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Correction of multiple striated muscles in murine Pompe diseasethrough adeno-associated virus-mediated gene therapy Sun, Baodong; Young, Sarah P.; Li, Ping; Di, Chunhui; Brown, Talmage; Salva, Maja Z.; Li, Songtao; Bird, Andrew; Yan, Zhen; Auten, Richard; Hauschka, Stephen D.; Koeberl, Dwight D. 分享 收藏
AAV vector-mediated reversal of hypoglycemia in canine and murine glycogen storage disease type Ia Koeberl, Dwight D.; Pinto, Carlos; Sun, Baodong; Li, Songtao; Kozink, Daniel M.; Benjamin, Daniel K., Jr.; Demaster, Amanda K.; Kruse, Meghan A.; Vaughn, Valerie; Hillman, Steven; Bird, Andrew; Jackson, Mark; Brown, Talmage; Kishnani, Priya S.; Chen, Yuan-Tsong 分享 收藏
Enhanced efficacy of an AAV vector encoding chimeric, highly secreted acid α-glucosidase in glycogen storage disease type II Sun, Baodong; Zhang, Haoyue; Benjamin, Daniel K., Jr.; Brown, Talmage; Bird, Andrew; Young, Sarah P.; McVie-Wylie, Alison; Chen, Y. -T.; Koeberl, Dwight D. 分享 收藏
Evasion of immune responses to introduced human acid α-glucosidase by liver-restricted expression in glycogen storage disease type II Franco, LM; Sun, BD; Yang, XY; Bird, A; Zhang, HY; Schneider, A; Brown, T; Young, SP; Clay, TM; Amalfitano, A; Chen, YT; Koeberl, DD 分享 收藏
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