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Healthcare Resource Use Associated With Tumor-Induced Osteomalacia: A Literature Review Jan de Beur, Suzanne M.; Dahir, Kathryn M.; Imel, Erik A.; Zanchetta, Maria Belen; Williams, Angela; Li, Zhiyi; Webb, Neil; Crowe, Victoria; Johnson, Ben; Carpenter, Thomas O. 分享 收藏
Burosumab Improves Patient-Reported Outcomes in Adults With Tumor-Induced Osteomalacia: Mixed-Methods Analysis Burosumab改善患有肿瘤诱发性骨软化症的成人患者报告的结局: 混合方法分析 de Beur, Suzanne M. Jan; Cimms, Tricia; Nixon, Annabel; Theodore-Oklota, Christina; Luca, Diana; Roberts, Mary Scott; Egan, Shayna; Graham, Christina A.; Hribal, Elizabeth; Evans, Christopher J.; Wood, Sue; Williams, Angela 分享 收藏
The International X-Linked Hypophosphatemia (XLH) Registry: first interim analysis of baseline demographic, genetic and clinical data Ariceta, Gema; Beck-Nielsen, Signe Sparre; Boot, Annemieke M.; Brandi, Maria Luisa; Briot, Karine; Collantes, Carmen de Lucas; Emma, Francesco; Giannini, Sandro; Haffner, Dieter; Keen, Richard; Levtchenko, Elena; Makitie, Outi; Mughal, M. Zulf; Nilsson, Ola; Schnabel, Dirk; Tripto-Shkolnik, Liana; Liu, Jonathan; Williams, Angela; Wood, Sue; Zillikens, M. Carola 分享 收藏
Health-related quality of life (HRQL) in cutaneous T-cell lymphoma: burden of disease and patient characteristics from a post-hoc analysis of a phase 3 trial in mycosis fungoides and Sezary syndrome Romero, Pablo; Nixon, Annabel; Kim, Youn H.; Molloy, Kevin; Quaglino, Pietro; Scarisbrick, Julia; Thornton, Susan; Sandilands, Kerry; Liu, Jennifer; Nixon, Annabel; Williams, Angela; Shinohara, Michi 分享 收藏
A real-world international observational study of mogamulizumab in adult patients with mycosis fungoides and Sezary syndrome (PROSPER study NCT05455931) Scarisbrick, Julia; Williams, Angela; Ardigo, Marco; Arumainathan, Arvind; Cowan, Richard; DeSimone, Jennifer; Geskin, Larisa; Goldaniga, Maria; Hashmi, Shahrukh; James, Eleanor; Musiek, Amy; Muniesa, Cristina; Nassi, Luca; Pileri, Alessandro; Pujol Vallverdu, Ramon; Quint, Koen; Rozati, Sima; Rupoli, Serena; Shinohara, Michi; Pagano, Livio 分享 收藏
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Efficacy of Burosumab in Adults with X-linked Hypophosphatemia (XLH): A Post Hoc Subgroup Analysis of a Randomized Double-Blind Placebo-Controlled Phase 3 Study Brandi, Maria Luisa; Jan de Beur, Suzanne; Briot, Karine; Carpenter, Thomas; Cheong, Hae Il; Cohen-Solal, Martine; Crowley, Rachel K.; Eastell, Richard; Imanishi, Yasuo; Imel, Erik A.; Ing, Steven W.; Insogna, Karl; Ito, Nobuaki; Javaid, Kassim; Kamenicky, Peter; Keen, Richard; Kubota, Takuo; Lachmann, Robin H.; Perwad, Farzana; Pitukcheewanont, Pisit; Portale, Anthony; Ralston, Stuart H.; Tanaka, Hiroyuki; Weber, Thomas J.; Yoo, Han-Wook; Sun, Wei; Williams, Angela; Nixon, Annabel; Takeuchi, Yasuhiro 分享 收藏
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Patient-Reported Outcomes from a Randomized, Active-Controlled, Open-Label, Phase 3 Trial of Burosumab Versus Conventional Therapy in Children with X-Linked Hypophosphatemia Padidela, Raja; Whyte, Michael P.; Glorieux, Francis H.; Munns, Craig F.; Ward, Leanne M.; Nilsson, Ola; Portale, Anthony A.; Simmons, Jill H.; Namba, Noriyuki; Cheong, Hae Il; Pitukcheewanont, Pisit; Sochett, Etienne; Hogler, Wolfgang; Muroya, Koji; Tanaka, Hiroyuki; Gottesman, Gary S.; Biggin, Andrew; Perwad, Farzana; Williams, Angela; Nixon, Annabel; Sun, Wei; Chen, Angel; Skrinar, Alison; Imel, Erik A. 分享 收藏
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