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收藏New blood-based biomarkers for Sanfilippo syndrome
Bitan, Gal; Taha, Hash Brown; Siddique, Ibrar; Chamoun, Lea M.; Mohseni, Kimia; Morris, Alanna J.; Luzzi, Anna; Acevedo, Jonathan; Morales, Adolfo; de la Garza, Giselle Perez; Nour, Elabed; Khijniak, Marie; Fenwick, Leony; Chen, Agnes; Iacovino, Michelina; O'Neill, Cara; Eisengart, Julie B.; Polgreen, Lynda
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收藏Impact of anakinra on disordered movement in Sanfilippo syndrome
Acevedo, Jonathan; Chen, Agnes; Youngju, Pak; Luzzi, Anna; Morales, Adolfo; Bitan, Gal; Iacovino, Michelina; O'Neill, Cara; Eisengart, Julie B.; Polgreen, Lynda
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收藏Immune response to intrathecal enzyme replacement therapy in mucopolysaccharidosis I patients
Vera, Moin; Le, Steven; Kan, Shih-hsin; Garban, Hermes; Naylor, David; Mlikotic, Anton; Kaitila, Ilkka; Harmatz, Paul; Chen, Agnes; Dickson, Patricia
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收藏Brain response to intrathecal or high dose enzyme replacementtherapy in the MPS I dog
Ellinwood, N.; Dickson, Patricia; Dierenfeld, Ashley; Kline, Karen; Parkes, Jennifer; Hanson, Steven; Vite, Charles; Mlikotic, Anton; Chen, Agnes; Gross, William; Haskins, Mark; Ponder, Katherine; Le, Steven
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