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Lipid nanoparticles and transcranial focused ultrasound enhance the delivery of SOD1 antisense oligonucleotides to the murine brain for ALS therapy 脂质纳米颗粒和经颅聚焦超声增强SOD1反义寡核苷酸在ALS治疗中对小鼠脑部的递送 Ediriweera, Gayathri R.; Sivaram, Amal J.; Cowin, Gary; Brown, Mikayla L.; Mcalary, Luke; Lum, Jeremy S.; Fletcher, Nicholas L.; Robinson, Liam; Simpson, Joshua D.; Chen, Liyu; Wasielewska, Joanna M.; Byrne, Ella; Finnie, John W.; Manavis, Jim; White, Anthony R.; Yerbury, Justin J.; Thurecht, Kristofer J.; Vine, Kara L. 分享 收藏
RNA-binding properties orchestrate TDP-43 homeostasis through condensate formation in vivo Scherer, Natalie M.; Maurel, Cindy; Graus, Matthew S.; Mcalary, Luke; Richter, Grant; Radford, Rowan A. W.; Hogan, Alison; Don, Emily K.; Lee, Albert; Yerbury, Justin; Francois, Mathias; Chung, Roger S.; Morsch, Marco 分享 收藏
ALS-linked CCNF variant disrupts motor neuron ubiquitin homeostasis Farrawell, Natalie E.; Bax, Monique; McAlary, Luke; McKenna, Jessie; Maksour, Simon; Do-Ha, Dzung; Rayner, Stephanie L.; Blair, Ian P.; Chung, Roger S.; Yerbury, Justin J.; Ooi, Lezanne; Saunders, Darren N. 分享 收藏
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TDP-43 is a ubiquitylation substrate of the SCFcyclin F complex Rayner, Stephanie L.; Yang, Shu; Farrawell, Natalie E.; Jagaraj, Cyril J.; Cheng, Flora; Davidson, Jennilee M.; Luu, Luan; Redondo, Alberto G.; Rabano, Alberto; Borrego-Hernandez, Daniel; Atkin, Julie D.; Morsch, Marco; Blair, Ian P.; Yerbury, Justin J.; Chung, Roger; Lee, Albert 分享 收藏
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CuATSM improves motor function and extends survival but is not tolerated at a high dose in SOD1G93A mice with a C57BL/6 background Lum, Jeremy S.; Brown, Mikayla L.; Farrawell, Natalie E.; McAlary, Luke; Ly, Diane; Chisholm, Christen G.; Snow, Josh; Vine, Kara L.; Karl, Tim; Kreilaus, Fabian; McInnes, Lachlan E.; Nikseresht, Sara; Donnelly, Paul S.; Crouch, Peter J.; Yerbury, Justin J. 分享 收藏
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p62 overexpression induces TDP-43 cytoplasmic mislocalisation, aggregation and cleavage and neuronal death Foster, A. D.; Flynn, L. L.; Cluning, C.; Cheng, F.; Davidson, J. M.; Lee, A.; Polain, N.; Mejzini, R.; Farrawell, N.; Yerbury, J. J.; Layfield, R.; Akkari, P. A.; Rea, S. L. 分享 收藏
Unbiased Label-Free Quantitative Proteomics of Cells Expressing Amyotrophic Lateral Sclerosis (ALS) Mutations in CCNF Reveals Activation of the Apoptosis Pathway: A Workflow to Screen Pathogenic Gene Mutations Cheng, Flora; De Luca, Alana; Hogan, Alison L.; Rayner, Stephanie L.; Davidson, Jennilee M.; Watchon, Maxinne; Stevens, Claire H.; Munoz, Sonia Sanz; Ooi, Lezanne; Yerbury, Justin J.; Don, Emily K.; Fifita, Jennifer A.; Villalva, Maria D.; Suddull, Hannah; Chapman, Tyler R.; Hedl, Thomas J.; Walker, Adam K.; Yang, Shu; Morsch, Marco; Shi, Bingyang; Blair, Ian P.; Laird, Angela S.; Chung, Roger S.; Lee, Albert 分享 收藏
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