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Thomas Gaj

university of illinois urbana-champaign

32H指数
61论文数
8.8K被引数
收录论文 39
发表时间
In vivo CRISPR base editing for treatment of Huntington’s disease体内CRISPR碱基编辑治疗亨廷顿病
err2026-07-29
err0
errOAAI
errShraddha Shirguppe; Michael Gapinske; Devyani Swami; Kyrollos Shenouda; Angelo Miskalis; Nicholas Gosstola; Daniela Del Bosque Siller; Isabelle Guerra; Pankaj Acharya; Dana Joulani; Maddie G. Szkwarek; Ananthan Nambiar; Abhishek Bhattacharjee; Anagha S. Dangi; Norah Odle; Gabrielle E. Nathan; Gianna Elias; Michelle Stilger; Jackson Winter; Wendy S. Woods; Daphine Anand; Colin K. W. Lim; Sergei Maslov; Thomas Gaj; Pablo Perez-Pinera
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Treatment of Huntington’s disease with a pan-HTT-targeting CRISPR nuclease使用泛-HTT靶向CRISPR核酸酶治疗亨廷顿病
err2026-04-24
err0
errOAAI
errKatherine Tan; Daniela Del Bosque Siller; Alisha Y. Xiong; Anna X.A. Wang; Tristan X. McCallister; Sreya Mummadi; Luke A. St John; Tae Kyu Lee; Annika Carrillo; Daniel G. Renshaw; Richard H. Zhou; Colin K.W. Lim; Jack He; Christopher J. Fields; Michael R. Hayden; Thomas Gaj
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A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTD高保真CRISPR-Cas13系统改善了与C9ORF72相关的ALS/FTD相关的异常表现
err2025-01-08
err2
errOAAI
errMccallister, Tristan X.; Lim, Colin K. W.; Singh, Mayuri; Zhang, Sijia; Ahsan, Najah S.; Terpstra, William M.; Xiong, Alisha Y.; Zeballos, C. M. Alejandra; Powell, Jackson E.; Drnevich, Jenny; Kang, Yifei; Gaj, Thomas
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SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skipping
err2024-11-28
err0
errOAAI
errMiskalis, Angelo; Shirguppe, Shraddha; Winter, Jackson; Elias, Gianna; Swami, Devyani; Nambiar, Ananthan; Stilger, Michelle; Woods, Wendy S.; Gosstola, Nicholas; Gapinske, Michael; Zeballos, Alejandra; Moore, Hayden; Maslov, Sergei; Gaj, Thomas; Perez-Pinera, Pablo
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CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genes
err2022-12-01
err8
errOAAI
errLim, Colin K. W.; McCallister, Tristan X.; Saporito-Magrina, Christian; McPheron, Garrett D.; Krishnan, Ramya; Zeballos, M. Alejandra; Powell, Jackson E.; Clark, Lindsay, V; Perez-Pinera, Pablo; Gaj, Thomas
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Targeted gene silencing in the nervous system with CRISPR-Cas13
err2022-01-21
err55
errOAAI
errPowell, Jackson E.; Lim, Colin K. W.; Krishnan, Ramya; McCallister, Tristan X.; Saporito-Magrina, Christian; Zeballos, Maria A.; McPheron, Garrett D.; Gaj, Thomas
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Treatment of a Mouse Model of ALS by In Vivo Base Editing
err2020-04-01
err146
errOAAI
errLim, Colin K. W.; Gapinske, Michael; Brooks, Alexandra K.; Woods, Wendy S.; Powell, Jackson E.; Zeballos, M. Alejandra C.; Winter, Jackson; Perez-Pinera, Pablo; Gaj, Thomas
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CRISPR-Cas9-Mediated Genome Editing Increases Lifespan and Improves Motor Deficits in a Huntington's Disease Mouse Model
err2019-09-01
err115
errOAAI
errEkman, Freja K.; Ojala, David S.; Adil, Maroof M.; Lopez, Paola A.; Schaffer, David, V; Gaj, Thomas
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The continuously evolving CRISPR barcoding toolbox
err2018-09-25
err6
errOAAI
errGaj, Thomas; Perez-Pinera, Pablo
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Innovations in CRISPR technology
err2018-08-01
err17
PREAI
errBrooks, Alexandra K.; Gaj, Thomas
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hPSC-Derived Striatal Cells Generated Using a Scalable 3D Hydrogel Promote Recovery in a Huntington Disease Mouse Model
err2018-05-01
err45
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errAdil, Maroof M.; Gaj, Thomas; Rao, Antara T.; Kulkarni, Rishikesh U.; Fuentes, Christina M.; Ramadoss, Gokul N.; Ekman, Freja K.; Miller, Evan W.; Schaffer, David V.
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A Hypothalamic Switch for REM and Non-REM Sleep
errNEURON
IF15
err2018-03-01
err109
errOAAI
errChen, Kai-Siang; Xu, Min; Zhang, Zhe; Chang, Wei-Cheng; Gaj, Thomas; Schaffer, David V.; Dan, Yang
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In vivo genome editing improves motor function and extends survival in a mouse model of ALS
err2017-12-01
err147
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errGaj, Thomas; Ojala, David S.; Ekman, Freja K.; Byrne, Leah C.; Limsirichai, Prajit; Schaffer, David V.
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Defined and Scalable Differentiation of Human Oligodendrocyte Precursors from Pluripotent Stem Cells in a 3D Culture System
err2017-06-01
err61
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errRodrigues, Goncalo M. C.; Gaj, Thomas; Adil, Maroof M.; Wahba, Joyce; Rao, Antara T.; Lorbeer, Franziska K.; Kulkarni, Rishi U.; Diogo, Maria Margarida; Cabral, Joaquim M. S.; Miller, Evan W.; Hockemeyer, Dirk; Schaffer, David V.
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Targeted gene knock-in by homology-directed genome editing using Cas9 ribonucleoprotein and AAV donor delivery
err2017-03-02
err71
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errGaj, Thomas; Staahl, Brett T.; Rodrigues, Goncalo M. C.; Limsirichai, Prajit; Ekman, Freja K.; Doudna, Jennifer A.; Schaffer, David V.
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A Designer AAV Variant Permits Efficient Retrograde Access to Projection Neurons
errNEURON
IF15
err2016-10-01
err968
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errTervo, D. Gowanlock R.; Hwang, Bum-Yeol; Viswanathan, Sarada; Gaj, Thomas; Lavzin, Maria; Ritola, Kimberly D.; Lindo, Sarah; Michael, Susan; Kuleshova, Elena; Ojala, David; Huang, Cheng-Chiu; Gerfen, Charles R.; Schiller, Jackie; Dudman, Joshua T.; Hantman, Adam W.; Looger, Loren L.; Schaffer, David V.; Karpova, Alla Y.
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Purging Latent HIV Infection by CRISPR-Mediated Viral Reactivation
err2016-05-01
err0
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errLimsirichai, Prajit; Gaj, Thomas; Schaffer, David V.
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CRISPR-mediated Activation of Latent HIV-1 Expression
err2016-03-01
err102
errOAAI
errLimsirichai, Prajit; Gaj, Thomas; Schaffer, David V.
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