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Pablo Pérez‐Piñera

university of illinois urbana-champaign

38H指数
114论文数
5.9K被引数
收录论文 50
发表时间
In vivo CRISPR base editing for treatment of Huntington’s disease体内CRISPR碱基编辑治疗亨廷顿病
err2026-07-29
err0
errOAAI
errShraddha Shirguppe; Michael Gapinske; Devyani Swami; Kyrollos Shenouda; Angelo Miskalis; Nicholas Gosstola; Daniela Del Bosque Siller; Isabelle Guerra; Pankaj Acharya; Dana Joulani; Maddie G. Szkwarek; Ananthan Nambiar; Abhishek Bhattacharjee; Anagha S. Dangi; Norah Odle; Gabrielle E. Nathan; Gianna Elias; Michelle Stilger; Jackson Winter; Wendy S. Woods; Daphine Anand; Colin K. W. Lim; Sergei Maslov; Thomas Gaj; Pablo Perez-Pinera
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Systemic administration of an RNA binding and cell-penetrating antibody targets therapeutic RNA to multiple mouse models of cancer系统性给予一种具有RNA结合能力和细胞穿透作用的抗体,可将治疗性RNA靶向递送至多种癌症小鼠模型。
err2025-07-16
err0
PREAI
errElias Quijano; Diana Martinez-Saucedo; Zaira Ianniello; Natasha Pinto-Medici; Madison Rackear; Haoting Chen; Luiz Lola-Pereira; Yanfeng Liu; Denise Hegan; Xinning Shan; Robert Tseng; Deanne Yugawa; Sumedha Chowdhury; Minsoo Khang; Jay P. Singh; Rashed Abdullah; Perisa Azhir; Soki Kashima; Wendy S. Woods; Nicholas Gosstola; Bruce C. Turner; Stephen Squinto; Dale L. Ludwig; Ranjit S. Bindra; Marie E. Robert; David A. Braun; Pablo Perez Pinera; W. Mark Saltzman; Luisa F. Escobar-Hoyos; Peter M. Glazer
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SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skipping
err2024-11-28
err0
errOAAI
errMiskalis, Angelo; Shirguppe, Shraddha; Winter, Jackson; Elias, Gianna; Swami, Devyani; Nambiar, Ananthan; Stilger, Michelle; Woods, Wendy S.; Gosstola, Nicholas; Gapinske, Michael; Zeballos, Alejandra; Moore, Hayden; Maslov, Sergei; Gaj, Thomas; Perez-Pinera, Pablo
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Altered RNA splicing causes pancreatic cancer and exposes a therapeutic vulnerability
err2024-01-16
err0
PREAI
errMedici, Natasha Pinto; Saucedo, Diana Martinez; Lee, Danny; Ku, Li-Ting; Tseng, Robert; Shan, Xinning; Chu, Tianyi; Perez-Pinera, Pablo; Cannataro, Vincent; Townsend, Jeffrey; Iacobuzio-Donahue, Christine; Robert, Marie; Abdel-Wahab, Omar; Leach, Steven D.; Escobar-Hoyos, Luisa
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Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors
err2023-09-01
err3
errOAAI
errGapinske, Michael; Winter, Jackson; Swami, Devyani; Gapinske, Lauren; Woods, Wendy S.; Shirguppe, Shraddha; Miskalis, Angelo; Busza, Anna; Joulani, Dana; Kao, Collin J.; Kostan, Kurt; Bigot, Anne; Bashir, Rashid; Perez-Pinera, Pablo
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CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genes
err2022-12-01
err8
errOAAI
errLim, Colin K. W.; McCallister, Tristan X.; Saporito-Magrina, Christian; McPheron, Garrett D.; Krishnan, Ramya; Zeballos, M. Alejandra; Powell, Jackson E.; Clark, Lindsay, V; Perez-Pinera, Pablo; Gaj, Thomas
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Delineating cooperative effects of Notch and biomechanical signals on patterned liver differentiation
err2022-10-07
err4
errOAAI
errJain, Ishita; Berg, Ian C.; Acharya, Ayusha; Blaauw, Maddie; Gosstola, Nicholas; Perez-Pinera, Pablo; Underhill, Gregory H.
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Optimizing Quantum Dot Probe Size for Single-Receptor Imaging
err2020-06-11
err16
errOAAI
errLe, Phuong; Vaidya, Rohit; Smith, Lucas D.; Han, Zhiyuan; Zahid, Mohammad U.; Winter, Jackson; Sarkar, Suresh; Chung, Hee Jung; Perez-Pinera, Pablo; Selvin, Paul R.; Smith, Andrew M.
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Treatment of a Mouse Model of ALS by In Vivo Base Editing
err2020-04-01
err146
errOAAI
errLim, Colin K. W.; Gapinske, Michael; Brooks, Alexandra K.; Woods, Wendy S.; Powell, Jackson E.; Zeballos, M. Alejandra C.; Winter, Jackson; Perez-Pinera, Pablo; Gaj, Thomas
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Epigenetic engineering of yeast reveals dynamic molecular adaptation to methylation stress and genetic modulators of specific DNMT3 family members
err2020-03-18
err15
errOAAI
errFinnegan, Alex, I; Kim, Somang; Jin, Hu; Gapinske, Michael; Woods, Wendy S.; Perez-Pinera, Pablo; Song, Jun S.
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Directed Evolution of CRISPR-Cas9 Base Editors
err2019-11-01
err0
PREAI
errWinter, Jackson; Perez-Pinera, Pablo
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Targeted exon skipping with AAV-mediated split adenine base editors (vol 5, 41, 2019)
err2019-10-15
err2
errOAAI
errWinter, Jackson; Luu, Alan; Gapinske, Michael; Manandhar, Sony; Shirguppe, Shraddha; Woods, Wendy S.; Song, Jun S.; Perez-Pinera, Pablo
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Targeted exon skipping with AAV-mediated split adenine base editors
err2019-08-20
err35
errOAAI
errWinter, Jackson; Luu, Alan; Gapinske, Michael; Manandhar, Sony; Shirguppe, Shraddha; Woods, Wendy S.; Song, Jun S.; Perez-Pinera, Pablo
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Multiplexed and tunable transcriptional activation by promoter insertion using nuclease-assisted vector integration
err2019-04-01
err12
errOAAI
errBrown, Alexander; Winter, Jackson; Gapinske, Michael; Tague, Nathan; Woods, Wendy S.; Perez-Pinera, Pablo
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The continuously evolving CRISPR barcoding toolbox
err2018-09-25
err6
errOAAI
errGaj, Thomas; Perez-Pinera, Pablo
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CRISPR-SKIP: programmable gene splicing with single base editors
err2018-08-15
err148
errOAAI
errGapinske, Michael; Luu, Alan; Winter, Jackson; Woods, Wendy S.; Kostan, Kurt A.; Shiva, Nikhil; Song, Jun S.; Perez-Pinera, Pablo
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Versatile and on-demand biologics co-production in yeast
err2018-01-08
err31
errOAAI
errCao, Jicong; Perez-Pinera, Pablo; Lowenhaupt, Ky; Wu, Ming-Ru; Purcell, Oliver; de la Fuente-Nunez, Cesar; Lu, Timothy K.
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Production of Functional Anti-Ebola Antibodies in Pichia pastoris
err2017-08-17
err14
PREAI
errPurcell, Oliver; Opdensteinen, Patrick; Chen, William; Lowenhaupt, Ky; Brown, Alexander; Hermann, Mario; Cao, Jicong; Tenhaef, Niklas; Kallweit, Eric; Kastilan, Robin; Sinskey, Anthony J.; Perez-Pinera, Pablo; Buyel, Johannes F.; Lu, Timothy K.
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Mammalian Synthetic Biology: Engineering Biological Systems
err2017-06-21
err48
errOAAI
errBlack, Joshua B.; Perez-Pinera, Pablo; Gersbach, Charles A.
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