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Impact of rAAV-shRNA treatment targeting mechanosensitive Ilk1 and Fermt2 in a mouse model of sepsis-induced muscle weakness 靶向力敏感受体Ilk1和Fermt2的rAAV-shRNA治疗对脓毒症诱导的肌肉无力小鼠模型的影响 Pacolet, Alexander; Derese, Inge; Pauwels, Lies; Perre, Sarah Vander; Smits, Maxime; van den Haute, Chris; Derde, Sarah; Koppo, Katrien; Gijsbers, Rik; Langouche, Lies 分享 收藏
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Prime editing functionally corrects cystic fibrosis-causing CFTR mutations in human organoids and airway epithelial cells Bulcaen, Mattijs; Kortleven, Pheline; Liu, Ronald B.; Maule, Giulia; Dreano, Elise; Kelly, Mairead; Ensinck, Marjolein M.; Thierie, Sam; Smits, Maxime; Ciciani, Matteo; Hatton, Aurelie; Chevalier, Benoit; Ramalho, Anabela S.; Solvas, Xavier Casadevall i; Debyser, Zeger; Vermeulen, Francois; Gijsbers, Rik; Sermet-Gaudelus, Isabelle; Cereseto, Anna; Carlon, Marianne S. 分享 收藏
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Evaluation of the efficacy of cystinosin supplementation through CTNS mRNA delivery in experimental models for cystinosis Bondue, Tjessa; Berlingerio, Sante Princiero; Siegerist, Florian; Sendino-Garvi, Elena; Schindler, Maximilian; Baelde, Hans Jacobus; Cairoli, Sara; Goffredo, Bianca Maria; Arcolino, Fanny Oliveira; Dieker, Jurgen; Janssen, Manoe Jacoba; Endlich, Nicole; Brock, Roland; Gijsbers, Rik; van den Heuvel, Lambertus; Levtchenko, Elena 分享 收藏
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Nanoblades allow high-level genome editing in murine and human organoids Tiroille, Victor; Krug, Adrien; Bokobza, Emma; Kahi, Michel; Bulcaen, Mattijs; Ensinck, Marjolein M.; Geurts, Maarten H.; Hendriks, Delilah; Vermeulen, Francois; Larbret, Frederic; Gutierrez-Guerrero, Alejandra; Chen, Yu; Van Zundert, Indra; Rocha, Susana; Rios, Anne C.; Medaer, Louise; Gijsbers, Rik; Mangeot, Philippe E.; Clevers, Hans; Carlon, Marianne S.; Bost, Frederic; Verhoeyan, Els 分享 收藏
Recombinant Adenoassociated Viral Vector 2/8 Model Of Interleukin 6 Mediated Chronic Inflammation Jacobs, Johanna E.; Maes, Wannes; Caluwe, Ellen; Lox, Marleen; Gillijns, Hilde; Pokreisz, Peter; Roskams, Tania; Van den Haute, Chris; Gijsbers, Rik; Janssens, Stefan P.; Van Aelst, Lucas 分享 收藏
VEGF overexpressed mesoangioblasts enhance urethral and vaginal recovery following simulated vaginal birth in rats da Cunha, Marina G. M. C. Mori; van der Veer, Bernard K.; Giacomazzi, Giorgia; Mackova, Katerina; Cattani, Laura; Koh, Kian Peng; Velde, Greetje Vande; Gijsbers, Rik; Albersen, Maarten; Sampaolesi, Maurilio; Deprest, Jan 分享 收藏
Case report: Myocarditis in congenital STAT1 gain-of function Staels, Frederik; Roosens, Willem; Giovannozzi, Simone; Moens, Leen; Bogaert, Jan; Iglesias-Herrero, Cecilia; Gijsbers, Rik; Bossuyt, Xavier; Frans, Glynis; Liston, Adrian; Humblet-Baron, Stephanie; Meyts, Isabelle; Van Aelst, Lucas; Schrijvers, Rik 分享 收藏
Extracellular vesicle-derived miRNAs improve stem cell-based therapeutic approaches in muscle wasting conditions Yedigaryan, Laura; Martinez-Sarra, Ester; Giacomazzi, Giorgia; Giarratana, Nefele; van der Veer, Bernard K.; Rotini, Alessio; Querceto, Silvia; Grosemans, Hanne; Cortes-Calabuig, Alvaro; Salucci, Sara; Battistelli, Michela; Falcieri, Elisabetta; Gijsbers, Rik; Quattrocelli, Mattia; Koh, Kian Peng; De Waele, Liesbeth; Buyse, Gunnar M.; Derua, Rita; Sampaolesi, Maurilio 分享 收藏
BET-Independent Murine Leukemia Virus Integration Is Retargeted In Vivo and Selects Distinct Genomic Elements for Lymphomagenesis Nombela, Ivan; Michiels, Martine; Van Looveren, Dominique; Marcelis, Lukas; El Ashkar, Sara; Van Belle, Siska; Bruggemans, Anne; Tousseyn, Thomas; Schwaller, Jurg; Christ, Frauke; Gijsbers, Rik; De Rijck, Jan; Debyser, Zeger 分享 收藏
A Novel Homozygous Stop Mutation in IL23R Causes Mendelian Susceptibility to Mycobacterial Disease Staels, Frederik; Lorenzetti, Flaminia; De Keukeleere, Kerstin; Willemsen, Mathijs; Gerbaux, Margaux; Neumann, Julika; Tousseyn, Thomas; Pasciuto, Emanuela; De Munter, Paul; Bossuyt, Xavier; Gijsbers, Rik; Liston, Adrian; Humblet-Baron, Stephanie; Schrijvers, Rik 分享 收藏
Luminescent Human iPSC-Derived Neurospheroids Enable Modeling of Neurotoxicity After Oxygen-glucose Deprivation (vol 19, pg 550, 2022) 发光的人iPSC衍生的神经球体能够模拟氧糖剥夺后的神经毒性 (第19卷,550页,2022) Van Breedam, Elise; Nijak, Aleksandra; Buyle-Huybrecht, Tamariche; Di Stefano, Julia; Boeren, Marlies; Govaerts, Jonas; Quarta, Alessandra; Swartenbroekx, Tine; Z. Jacobs, Eva; Menten, Bjorn; Gijsbers, Rik; Delputte, Peter; Alaerts, Maaike; Hassannia, Behrouz; Loeys, Bart; Berneman, Zwi; Timmermans, Jean-Pierre; G. Jorens, Philippe; Vanden Berghe, Tom; Fransen, Erik; Wouters, An; H. De Vos, Winnok; Ponsaerts, Peter 分享 收藏
Urine-Derived Kidney Progenitor Cells in Cystinosis Veys, Koenraad; Berlingerio, Sante Princiero; David, Dries; Bondue, Tjessa; Held, Katharina; Reda, Ahmed; van den Broek, Martijn; Theunis, Koen; Janssen, Mirian; Cornelissen, Elisabeth; Vriens, Joris; Diomedi-Camassei, Francesca; Gijsbers, Rik; van den Heuvel, Lambertus; Arcolino, Fanny O.; Levtchenko, Elena 分享 收藏
Luminescent Human iPSC-Derived Neurospheroids Enable Modeling of Neurotoxicity After Oxygen-glucose Deprivation 发光的人iPSC衍生的神经球体可以模拟氧糖剥夺后的神经毒性 Van Breedam, Elise; Nijak, Aleksandra; Buyle-Huybrecht, Tamariche; Di Stefano, Julia; Boeren, Marlies; Govaerts, Jonas; Quarta, Alessandra; Swartenbroekx, Tine; Jacobs, Eva Z.; Menten, Bjorn; Gijsbers, Rik; Delputte, Peter; Alaerts, Maaike; Hassannia, Behrouz; Loeys, Bart; Berneman, Zwi; Timmermans, Jean-Pierre; Jorens, Philippe G.; Vanden Berghe, Tom; Fransen, Erik; Wouters, An; De Vos, Winnok H.; Ponsaerts, Peter 分享 收藏
Predicting genotoxicity of viral vectors for stem cell gene therapy using gene expression-based machine learning 使用基于基因表达的机器学习预测用于干细胞基因治疗的病毒载体的遗传毒性 Schwarzer, Adrian; Talbot, Steven R.; Selich, Anton; Morgan, Michael; Schott, Juliane W.; Dittrich-Breiholz, Oliver; Bastone, Antonella L.; Weigel, Bettina; Ha, Teng Cheong; Dziadek, Violetta; Gijsbers, Rik; Thrasher, Adrian J.; Staal, Frank J. T.; Gaspar, Hubert B.; Modlich, Ute; Schambach, Axel; Rothe, Michael 分享 收藏