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Design and Mechanistic Analysis of a Potent Bivalent Inhibitor of Transthyretin Amyloid Fibrillogenesis 设计和机制分析:一种强效的双价转甲状腺素蛋白淀粉样纤维形成抑制剂 Mangione, P. Patrizia; Verona, Guglielmo; Cantarutti, Cristina; Nocerino, Paola; Mimmi, Maria Chiara; Swain, Christopher J.; Canetti, Diana; Giorgetti, Sofia; Uings, Iain; Gillmore, Julian D.; Taylor, Graham W.; Pepys, Mark B.; Bellotti, Vittorio; Corazza, Alessandra 分享 收藏
Development of human targeted extracellular vesicles loaded with shRNA minicircles to prevent parkinsonian pathology 开发靶向人类的外泌体,负载shRNA微环以预防帕金森病病理变化 Izco, Maria; Sola, Carlos; Schleef, Martin; Schmeer, Marco; de Toro, Maria; Verona, Guglielmo; Carlos, Estefania; Reinares-Sebastian, Alejandro; Colina, Sandra; Marzo-Sola, Maria Eugenia; Garcia-Sanmartin, Josune; Fernandez-Irigoyen, Joaquin; Santamaria, Enrique; Mugica-Vidal, Rodolfo; Blesa, Javier; Alvarez-Erviti, Lydia 分享 收藏
Oxidative conversion of transthyretin in formalin-fixed clinical amyloid samples results in the formation of the His90Asp and His90Asn variants Raheja, Simran; Verona, Guglielmo; Florent, Paolo; Rendell, Nigel B.; Nocerino, Paola; Ellemerich, Stephan; Fernandes, Raizel; Botcher, Nicola; Rowczenio, Dorota; Gilbertson, Janet A.; Simons, J. Paul; Gillmore, Julian D.; Bellotti, Vittorio; Taylor, Graham W.; Canetti, Diana 分享 收藏
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Truncation of the constant domain drives amyloid formation by immunoglobulin light chains Lavatelli, Francesca; Natalello, Antonino; Marchese, Loredana; Ami, Diletta; Corazza, Alessandra; Raimondi, Sara; Mimmi, Maria Chiara; Malinverni, Silvia; Mangione, P. Patrizia; Palmer, Manel Terrones; Lampis, Alessio; Concardi, Monica; Verona, Guglielmo; Canetti, Diana; Arbustini, Eloisa; Bellotti, Vittorio; Giorgetti, Sofia 分享 收藏
Antibody-Associated Reversal of ATTR Amyloidosis-Related Cardiomyopathy Fontana, Marianna; Gilbertson, Janet; Verona, Guglielmo; Riefolo, Mattia; Slamova, Ivana; Leone, Ornella; Rowczenio, Dorota; Botcher, Nicola; Ioannou, Adam; Patel, Rishi K.; Razvi, Yousuf; Martinez-Naharro, Ana; Whelan, Carol J.; Venneri, Lucia; Duhlin, Amanda; Canetti, Diana; Ellmerich, Stephan; Moon, James C.; Kellman, Peter; Al-Shawi, Raya; Mccoy, Laura; Simons, J. Paul; Hawkins, Philip N.; Gillmore, Julian D. 分享 收藏
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Amyloid Formation by Globular Proteins: The Need to Narrow the Gap Between in Vitro and in Vivo Mechanisms Faravelli, Giulia; Mondani, Valentina; Mangione, P. Patrizia; Raimondi, Sara; Marchese, Loredana; Lavatelli, Francesca; Stoppini, Monica; Corazza, Alessandra; Canetti, Diana; Verona, Guglielmo; Obici, Laura; Taylor, Graham W.; Gillmore, Julian D.; Giorgetti, Sofia; Bellotti, Vittorio 分享 收藏
Plasmin activity promotes amyloid deposition in a transgenic model of human transthyretin amyloidosis Slamova, Ivana; Adib, Rozita; Ellmerich, Stephan; Golos, Michal R.; Gilbertson, Janet A.; Botcher, Nicola; Canetti, Diana; Taylor, Graham W.; Rendell, Nigel; Tennent, Glenys A.; Verona, Guglielmo; Porcari, Riccardo; Mangione, P. Patrizia; Gillmore, Julian D.; Pepys, Mark B.; Bellotti, Vittorio; Hawkins, Philip N.; Al-Shawi, Raya; Simons, J. Paul 分享 收藏
Clinical ApoA-IV amyloid is associated with fibrillogenic signal sequence Canetti, Diana; Nocerino, Paola; Rendell, Nigel B.; Botcher, Nicola; Gilbertson, Janet A.; Blanco, Angel; Rowczenio, Dorota; Morelli, Alessandra; Mangione, P. Patrizia; Corazza, Alessandra; Verona, Guglielmo; Giorgetti, Sofia; Marchese, Loredana; Westermark, Per; Hawkins, Philip N.; Gillmore, Julian D.; Bellotti, Vittorio; Taylor, Graham W. 分享 收藏
Comparative study of the stabilities of syntheticin vitroand naturalex vivotransthyretin amyloid fibrils Raimondi, Sara; Mangione, P. Patrizia; Verona, Guglielmo; Canetti, Diana; Nocerino, Paola; Marchese, Loredana; Piccarducci, Rebecca; Mondani, Valentina; Faravelli, Giulia; Taylor, Graham W.; Gillmore, Julian D.; Corazza, Alessandra; Pepys, Mark B.; Giorgetti, Sofia; Bellotti, Vittorio 分享 收藏
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Lysozyme amyloid: evidence for the W64R variant by proteomics in the absence of the wild type protein Moura, Alexandra; Nocerino, Paola; Gilbertson, Janet A.; Rendell, Nigel B.; Mangione, P. Patrizia; Verona, Guglielmo; Rowczenio, Dorota; Gillmore, Julian D.; Taylor, Graham W.; Bellotti, Vittorio; Canetti, Diana 分享 收藏
Binding of Monovalent and Bivalent Ligands by Transthyretin Causes Different Short-and Long-Distance Conformational Changes Corazza, Alessandra; Verona, Guglielmo; Waudby, Christopher A.; Mangione, Patrizia; Bingham, Ryan; Uings, Iain; Canetti, Diana; Nocerino, Paola; Taylor, Graham W.; Pepys, Mark B.; Christodoulou, John; Bellotti, Vittorio 分享 收藏
Innovative measurements for improved diagnosis and management of neurodegenerative diseases Quaglia, M.; Cano, S.; Delatour, V.; Divieto, C.; Fillmer, A.; Goeschel, L.; Lehmann, S.; Melin, J.; Pang, S.; Verona, G. 分享 收藏
Plasminogen activation triggers transthyretin amyloidogenesis in vitro Mangione, P. Patrizia; Verona, Guglielmo; Corazza, Alessandra; Marcoux, Julien; Canetti, Diana; Giorgetti, Sofia; Raimondi, Sara; Stoppini, Monica; Esposito, Marilena; Relini, Annalisa; Canale, Claudio; Valli, Maurizia; Marchese, Loredana; Faravelli, Giulia; Obici, Laura; Hawkins, Philip N.; Taylor, Graham W.; Gillmore, Julian D.; Pepys, Mark B.; Bellotti, Vittorio 分享 收藏
Misidentification of transthyretin and immunoglobulin variants by proteomics due to methyl lysine formation in formalin-fixed paraffin-embedded amyloid tissue Canetti, Diana; Rendell, Nigel Brian; Di Vagno, Lucia; Gilbertson, Janet A.; Rowczenio, Dorota; Rezk, Tamar; Gillmore, Julian D.; Hawkins, Phillip N.; Verona, Guglielmo; Mangione, Palma Patrizia; Giorgetti, Sofia; Mauri, Pierluigi; Motta, Sara; De Palma, Antonella; Bellotti, Vittorio; Taylor, Graham W. 分享 收藏